Recombinant AAV2-mediated β-globin expression in human fetal hematopoietic cells from the aborted fetuses with β-thalassemia major

International Journal of Hematology

Volumn 93, Issue 6, 2011, Pages 691-699

  Tian, Jing ^a,b   Wang, Feng ^a,b   Xue, Jin Feng ^a,b   Zhao, Fei ^a,b   Song, Liu Jiang ^a,b   Tan, Meng Qun ^a,b  

^a Central South University   (China)

^b Xiangya Biological Medicine Institute   (China)

Author keywords

Globin; Adeno associated virus; Gene expression; Genetic modification; Hematopoietic cells; Transplantation

Indexed keywords

ALPHA GLOBIN; BETA GLOBIN; PARVOVIRUS VECTOR; PLASMID VECTOR;

ABORTION; ADENO ASSOCIATED VIRUS; ALLELE; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CELL ISOLATION; CONTROLLED STUDY; FEMALE; FETUS; FETUS CELL; GENE EXPRESSION; GENE SYNTHESIS; GENETIC TRANSDUCTION; HEMATOPOIETIC CELL; HIGH PERFORMANCE LIQUID CHROMATOGRAPHY; HUMAN; HUMAN CELL; LIVER CELL; MOUSE; NONHUMAN; STEM CELL TRANSPLANTATION; THALASSEMIA MAJOR; TRANSGENE; VIRAL GENE THERAPY;

ABORTED FETUS; ANIMALS; BETA-GLOBINS; BETA-THALASSEMIA; DEPENDOVIRUS; ERYTHROCYTES; FEMALE; GENE EXPRESSION REGULATION; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HEK293 CELLS; HEMATOPOIETIC STEM CELLS; HUMANS; MICE; MICE, INBRED BALB C; MICE, NUDE; RECOMBINANT PROTEINS; RNA, MESSENGER;

EID: 80955180060     PISSN: 09255710     EISSN: 18653774     Source Type: Journal    
DOI: 10.1007/s12185-011-0823-x     Document Type: Article

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