Hepatorenal correction in murine glycogen storage disease type i with a double-stranded adeno-associated virus vector

Molecular Therapy

Volumn 19, Issue 11, 2011, Pages 1961-1970

  Luo, Xiaoyan ^a   Hall, Gentzon ^b   Li, Songtao ^a   Bird, Andrew ^a   Lavin, Peter J ^b   Winn, Michelle P ^b   Kemper, Alex R ^a   Brown, Talmage T ^c   Koeberl, Dwight D ^a  

^a DUKE UNIVERSITY MEDICAL CENTER   (United States)

^b Division of Nephrology   (United States)

^c NORTH CAROLINA STATE UNIVERSITY   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

GLUCOSE; GLUCOSE 6 PHOSPHATASE; GLYCOGEN; PARVOVIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ADENO ASSOCIATED VIRUS 2; ADENO ASSOCIATED VIRUS 7; ADENO ASSOCIATED VIRUS 8; ADENO ASSOCIATED VIRUS 9; ALBUMINURIA; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DIET RESTRICTION; DRUG MEGADOSE; EPITHELIUM CELL; FEMALE; GLUCOSE BLOOD LEVEL; GLYCOGEN STORAGE DISEASE TYPE 1; HEPATORENAL SYNDROME; HYPOGLYCEMIA; KIDNEY CELL; KIDNEY FIBROSIS; LOW DRUG DOSE; MALE; MOUSE; NONHUMAN; PROTEIN EXPRESSION; SEROTYPE; TREATMENT RESPONSE;

ADENO-ASSOCIATED VIRUS; MURINAE; MUS;

EID: 80455174006     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2011.126     Document Type: Article

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