Sustained hepatic and renal glucose-6-phosphatase expression corrects glycogen storage disease type Ia in mice

Human Molecular Genetics

Volumn 11, Issue 18, 2002, Pages 2155-2164

  Sun, Mao Sen ^a   Pan, Chi Jiunn ^a   Shieh, Jeng Jer ^a   Ghosh, Abhijit ^a   Chen, Li Yuan ^a   Mansfield, Brian C ^a   Ward, Jerrold M ^b   Byrne, Barry J ^c   Chou, Janice Yang ^a,d  

^a EUNICE KENNEDY SHRIVER NATIONAL INSTITUTE OF CHILD HEALTH AND HUMAN DEVELOPMENT   (United States)

^b NATIONAL CANCER INSTITUTE   (United States)

^c UNIVERSITY OF FLORIDA   (United States)

^d NATIONAL INSTITUTES OF HEALTH   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; GLUCOSE 6 PHOSPHATASE; KIDNEY ENZYME; LIVER ENZYME; MEMBRANE PROTEIN;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; AUTOSOMAL RECESSIVE DISORDER; CONTROLLED STUDY; ENDOPLASMIC RETICULUM; ENZYME DEFICIENCY; ENZYME REPLACEMENT; FEASIBILITY STUDY; GLUCOSE HOMEOSTASIS; GLYCOGEN STORAGE DISEASE TYPE 1; GROWTH RETARDATION; HEPATOMEGALY; HYPERLIPIDEMIA; HYPERURICEMIA; HYPOGLYCEMIA; KIDNEY DISEASE; LACTIC ACIDEMIA; MOUSE; NEWBORN; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY;

ADENO-ASSOCIATED VIRUS; ADENOVIRIDAE; ANIMALIA; MURINAE;

EID: 0036712798     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/11.18.2155     Document Type: Article

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