Informed reasoning: Repositioning of nitisinone to treat oculocutaneous albinism

Journal of Clinical Investigation

Volumn 121, Issue 10, 2011, Pages 3828-3831

  Manga, Prashiela ^a   Orlow, Seth J ^a  

^a NEW YORK UNIVERSITY SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

MELANIN; MONOPHENOL MONOOXYGENASE; NITISINONE; TYROSINE;

DRUG MECHANISM; HUMAN; MELANOGENESIS; MORBIDITY; NONHUMAN; NOTE; OCULOCUTANEOUS ALBINISM; OFF LABEL DRUG USE; PATHOGENESIS; PIGMENT EPITHELIUM; PREVALENCE; PRIORITY JOURNAL; PROTEIN FOLDING; TYROSINEMIA;

ALBINISM, OCULOCUTANEOUS; ANIMALS; CYCLOHEXANONES; EYE COLOR; FEMALE; HUMANS; NITROBENZOATES; PREGNANCY; SKIN PIGMENTATION;

EID: 80053434968     PISSN: 00219738     EISSN: 15588238     Source Type: Journal    
DOI: 10.1172/JCI59763     Document Type: Note

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