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Volumn 44, Issue 5, 2011, Pages 720-726

Enzyme replacement therapy induces T-cell responses in late-onset Pompe disease

Author keywords

A glucosidase; Enzyme replacement therapy; Inherited muscle diseases; Late onset glycogenosis ii; Myozyme; Pompe disease; T cell response

Indexed keywords

FAS LIGAND; GAMMA INTERFERON; INTERLEUKIN 17; INTERLEUKIN 4; INTERLEUKIN 6; PERFORIN; RECOMBINANT GLUCAN 1,4 ALPHA GLUCOSIDASE; TUMOR NECROSIS FACTOR ALPHA;

EID: 80053377114     PISSN: 0148639X     EISSN: 10974598     Source Type: Journal    
DOI: 10.1002/mus.22136     Document Type: Article
Times cited : (13)

References (24)
  • 2
    • 7244236586 scopus 로고    scopus 로고
    • Improved efficacy of gene therapy approaches for Pompe disease using a new, immune-deficient GSD-II mouse model
    • Xu F, Ding E, Liao SX, Migone F, Dai J, Schneider A, et al. Improved efficacy of gene therapy approaches for Pompe disease using a new, immune-deficient GSD-II mouse model. Gene Ther 2004;11:1590-1598
    • (2004) Gene Ther , vol.11 , pp. 1590-1598
    • Xu, F.1    Ding, E.2    Liao, S.X.3    Migone, F.4    Dai, J.5    Schneider, A.6
  • 3
    • 35348926853 scopus 로고    scopus 로고
    • Enhanced response to enzyme replacement therapy in Pompe disease after the induction of immune tolerance
    • Sun B, Bird A, Young SP, Kishnani PS, Chen YT, Koeberl DD. Enhanced response to enzyme replacement therapy in Pompe disease after the induction of immune tolerance. Am J Hum Genet 2007;81:1042-1049
    • (2007) Am J Hum Genet , vol.81 , pp. 1042-1049
    • Sun, B.1    Bird, A.2    Young, S.P.3    Kishnani, P.S.4    Chen, Y.T.5    Koeberl, D.D.6
  • 5
    • 0030908645 scopus 로고    scopus 로고
    • Enzyme therapy in Gaucher disease type I: Effect of neutralizing antibodies to acid b-glucosidase
    • Ponce E, Moskovitz J, Grabowski G. Enzyme therapy in Gaucher disease type I: effect of neutralizing antibodies to acid b-glucosidase. Blood 1997;90:43-48
    • (1997) Blood , vol.90 , pp. 43-48
    • Ponce, E.1    Moskovitz, J.2    Grabowski, G.3
  • 6
    • 0035746540 scopus 로고    scopus 로고
    • Recombinant human acid alpha-glucosidase enzyme therapy for infantile glycogen storage disease type II: Results of a phase I/II clinical trial
    • Amalfitano A, Bengur AR, Morse RP, Majure JM, Case LE, Veerling DL, et al. Recombinant human acid alpha-glucosidase enzyme therapy for infantile glycogen storage disease type II: results of a phase I/II clinical trial. Gen Med 2001;3:132-138
    • (2001) Gen Med , vol.3 , pp. 132-138
    • Amalfitano, A.1    Bengur, A.R.2    Morse, R.P.3    Majure, J.M.4    Case, L.E.5    Veerling, D.L.6
  • 7
    • 33746151202 scopus 로고    scopus 로고
    • Chinese hamster ovary cell-derived recombinant human acid alpha-glucosidase in infantile-onset Pompe disease
    • Kishnani PS, Nicolino M, Voit T, Rogers RC, Tsai AC, Waterson J, et al. Chinese hamster ovary cell-derived recombinant human acid alpha-glucosidase in infantile-onset Pompe disease. J Pediatr 2006; 149:89-97
    • (2006) J Pediatr , vol.149 , pp. 89-97
    • Kishnani, P.S.1    Nicolino, M.2    Voit, T.3    Rogers, R.C.4    Tsai, A.C.5    Waterson, J.6
  • 8
    • 15044345490 scopus 로고    scopus 로고
    • Safety and efficacy of recombinant acid alpha-glucosidase (rhGAA) in patients with classical infantile Pompe disease: Results of a phase II clinical trial
    • Klinge L, Straub V, Neudorf U, Schaper J, Bosbach T, Görlinger K, et al. Safety and efficacy of recombinant acid alpha-glucosidase (rhGAA) in patients with classical infantile Pompe disease: results of a phase II clinical trial. Neuromuscul Disord 2005;15:24-31
    • (2005) Neuromuscul Disord , vol.15 , pp. 24-31
    • Klinge, L.1    Straub, V.2    Neudorf, U.3    Schaper, J.4    Bosbach, T.5    Görlinger, K.6
  • 10
    • 0037906571 scopus 로고    scopus 로고
    • Immune tolerance after long-term enzyme-replacement therapy among patients who have mucopolysaccharidosis I
    • Kakavanos R, Turner CT, Hopwood JJ, Kakkis ED, Brooks DA. Immune tolerance after long-term enzyme-replacement therapy among patients who have mucopolysaccharidosis I. Lancet 2003;361:1608-1613
    • (2003) Lancet , vol.361 , pp. 1608-1613
    • Kakavanos, R.1    Turner, C.T.2    Hopwood, J.J.3    Kakkis, E.D.4    Brooks, D.A.5
  • 11
    • 70049095101 scopus 로고    scopus 로고
    • How do regulatory T cells work?
    • Corthay A. How do regulatory T cells work? Scand J Immunol 2009; 70:326-336
    • (2009) Scand J Immunol , vol.70 , pp. 326-336
    • Corthay, A.1
  • 12
    • 52649167708 scopus 로고    scopus 로고
    • CD4 T cells: Fates, functions and faults
    • Zhu J, Paul WE. CD4 T cells: fates, functions and faults. Blood 2008; 112:1557-1569
    • (2008) Blood , vol.112 , pp. 1557-1569
    • Zhu, J.1    Paul, W.E.2
  • 14
    • 0028110928 scopus 로고
    • Fas and perforin pathways as major mechanisms of T cell-mediated cytotoxicity
    • Kägi D, Vignaux F, Ledermann B, Bürki K, Depraetere V, Nagata S, et al. Fas and perforin pathways as major mechanisms of T cell-mediated cytotoxicity. Science 1994;265:528-530
    • (1994) Science , vol.265 , pp. 528-530
    • Kägi, D.1    Vignaux, F.2    Ledermann, B.3    Bürki, K.4    Depraetere, V.5    Nagata, S.6
  • 15
    • 0027937745 scopus 로고
    • Cytolytic T-cell cytotoxicity is mediated through perforin and Fas lytic pathways
    • Lowin B, Hahne M, Mattmann C, Tschopp J. Cytolytic T-cell cytotoxicity is mediated through perforin and Fas lytic pathways. Nature 1994;370:650-652
    • (1994) Nature , vol.370 , pp. 650-652
    • Lowin, B.1    Hahne, M.2    Mattmann, C.3    Tschopp, J.4
  • 16
  • 17
    • 0038171458 scopus 로고    scopus 로고
    • Activation-induced cell death in T cells
    • Green DR, Droin N, Pinkoski M. Activation-induced cell death in T cells. Immunol Rev 2003;193:70-81
    • (2003) Immunol Rev , vol.193 , pp. 70-81
    • Green, D.R.1    Droin, N.2    Pinkoski, M.3
  • 19
    • 44649172457 scopus 로고    scopus 로고
    • Reduced alpha-Gal A enzyme activity in Fabry fibroblast cells and Fabry mice tissues induced by serum from antibody positive patients with Fabry disease
    • Ohashi T, Iizuka S, Ida H, Eto Y. Reduced alpha-Gal A enzyme activity in Fabry fibroblast cells and Fabry mice tissues induced by serum from antibody positive patients with Fabry disease. Mol Genet Metab 2008;94:313-318
    • (2008) Mol Genet Metab , vol.94 , pp. 313-318
    • Ohashi, T.1    Iizuka, S.2    Ida, H.3    Eto, Y.4
  • 20
    • 34447121276 scopus 로고    scopus 로고
    • Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: Results of a multinational study of recombinant human alpha-L-iduronidase (laronidase)
    • Wraith JE, Beck M, Lane R, van der Ploeg A, Shapiro E, Xue Y, et al. Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: results of a multinational study of recombinant human alpha-L-iduronidase (laronidase). Pediatrics 2007;120:e37-e46.
    • (2007) Pediatrics , vol.120
    • Wraith, J.E.1    Beck, M.2    Lane, R.3    van der Ploeg, A.4    Shapiro, E.5    Xue, Y.6
  • 21
    • 77950876430 scopus 로고    scopus 로고
    • Clinical effect of neutralizing antibodies to interferon beta that persist long after cessation of therapy for multiple sclerosis
    • van der Voort LF, Gilli F, Bertolotto A, Knol DL, Ulitdehaag DM, Polman CH, et al. Clinical effect of neutralizing antibodies to interferon beta that persist long after cessation of therapy for multiple sclerosis. Arch Neurol 2010;67:402-407
    • (2010) Arch Neurol , vol.67 , pp. 402-407
    • van der Voort, L.F.1    Gilli, F.2    Bertolotto, A.3    Knol, D.L.4    Ulitdehaag, D.M.5    Polman, C.H.6
  • 23
    • 79952467499 scopus 로고    scopus 로고
    • A shift towards a T cell cytokine deficiency along with an anti-inflammatory/regulatory microenvironment may enable the synthesis of anti-FVIII inhibitors in haemophilia A patients
    • Chaves DG, Velloso-Rodrigues C, Oliveira CA, Teixeira-Carvalho A, Santoro MM, Martins-Filho OA. A shift towards a T cell cytokine deficiency along with an anti-inflammatory/regulatory microenvironment may enable the synthesis of anti-FVIII inhibitors in haemophilia A patients. Clin Exp Immunol 2010;162:425-437
    • (2010) Clin Exp Immunol , vol.162 , pp. 425-437
    • Chaves, D.G.1    Velloso-Rodrigues, C.2    Oliveira, C.A.3    Teixeira-Carvalho, A.4    Santoro, M.M.5    Martins-Filho, O.A.6
  • 24
    • 34249003669 scopus 로고    scopus 로고
    • Cytokine production by CD4{thorn} T cells specific for coagulation factor VIII in healthy subjects and haemophilia A patients
    • Hu G, Guo D, Key NS, Conti-Fine BM. Cytokine production by CD4{thorn} T cells specific for coagulation factor VIII in healthy subjects and haemophilia A patients. Thromb Haemost 2007;97:788-794.
    • (2007) Thromb Haemost , vol.97 , pp. 788-794
    • Hu, G.1    Guo, D.2    Key, N.S.3    Conti-Fine, B.M.4


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.