Successful cord blood transplantation using a reduced-intensity conditioning regimen for advanced childhood-onset cerebral adrenoleukodystrophy

Pediatric Transplantation

Volumn 15, Issue 6, 2011, Pages

  Awaya, Tomonari ^a   Kato, Takeo ^a   Niwa, Akira ^a   Hiramatsu, Hidefumi ^a   Umeda, Katsutsugu ^a   Watanabe, Ken Ichiro ^a   Shibata, Minoru ^a   Yamanaka, Yasunari ^a   Maruya, Etsuko ^b   Saji, Hiroh ^b   Nakahata, Tatsutoshi ^a   Adachi, Souichi ^a  

^a KYOTO UNIVERSITY   (Japan)

^b Japanese Red Cross Kanto Koshinetsu Block Blood Center   (Japan)

Author keywords

adrenoleukodystrophy; cord blood stem cell transplantation; hematopoietic stem cell transplantation; reduced intensity stem cell transplantation

Indexed keywords

FLUDARABINE; IMMUNOGLOBULIN; MELPHALAN; METHOTREXATE; MYCOPHENOLIC ACID 2 MORPHOLINOETHYL ESTER; PREDNISOLONE; TACROLIMUS;

ADRENOLEUKODYSTROPHY; ARTICLE; BEHAVIOR CHANGE; CASE REPORT; CEREBELLUM DISEASE; CHILD; CHILDHOOD DISEASE; CHILDHOOD ONSET CEREBRAL FORM OF X LINKED ADRENOLEUKODYSTROPHY; CONTINUOUS INFUSION; CORD BLOOD STEM CELL TRANSPLANTATION; DISEASE COURSE; FOLLOW UP; GENETIC ANALYSIS; GRAFT VERSUS HOST REACTION; HLA MATCHING; HUMAN; MALE; PNEUMONIA; POINT MUTATION; POLYNEUROPATHY; RADIATION DOSE; REDUCED INTENSITY CONDITIONING; SCHOOL CHILD; VISUAL IMPAIRMENT; WHOLE BODY RADIATION; X CHROMOSOME LINKED DISORDER;

ADRENOLEUKODYSTROPHY; ATP-BINDING CASSETTE TRANSPORTERS; BRAIN DISEASES; CHILD; CORD BLOOD STEM CELL TRANSPLANTATION; DISEASE PROGRESSION; FETAL BLOOD; HUMANS; MAGNETIC RESONANCE IMAGING; MALE; MUTATION; NEUROPSYCHOLOGICAL TESTS; TIME FACTORS; TRANSPLANTATION CONDITIONING; TREATMENT OUTCOME;

EID: 80052091213     PISSN: 13973142     EISSN: 13993046     Source Type: Journal    
DOI: 10.1111/j.1399-3046.2009.01188.x     Document Type: Article

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