Codon Optimization of the Microdystrophin Gene for Duchenne Muscular Dystrophy Gene Therapy

Methods in Molecular Biology

Volumn 709, Issue , 2011, Pages 21-37

  Athanasopoulos, Takis ^b   Foster, Helen ^a,b   Foster, Keith ^a,b   Dickson, George ^a,b  

^a ST GEORGE'S UNIVERSITY OF LONDON   (United Kingdom)

^b QUEEN MARY UNIVERSITY OF LONDON   (United Kingdom)

Author keywords

AAV; Adeno associated virus; Codon optimization; Duchenne muscular dystrophy; Dystrophin; Gene therapy; mdx; Microdystrophin; Minidystrophin; mRNA; Muscle; Quasidystrophin

Indexed keywords

COMPLEMENTARY DNA; DYSTROPHIN;

ADENO ASSOCIATED VIRUS; ANIMAL; ANIMAL MUSCULAR DYSTROPHY; ARTICLE; CODON; DUCHENNE MUSCULAR DYSTROPHY; GENE THERAPY; GENE VECTOR; GENETICS; HUMAN; METHODOLOGY; MOUSE; MUSCLE; NUCLEOTIDE SEQUENCE; X CHROMOSOME LINKED MUSCULAR DYSTROPHIC MOUSE;

ANIMALS; BASE SEQUENCE; CODON; DEPENDOVIRUS; DNA, COMPLEMENTARY; DYSTROPHIN; GENE THERAPY; GENETIC VECTORS; HUMANS; MICE; MICE, INBRED MDX; MUSCLES; MUSCULAR DYSTROPHY, ANIMAL; MUSCULAR DYSTROPHY, DUCHENNE;

EID: 79960073531     PISSN: 10643745     EISSN: 19406029     Source Type: Book Series    
DOI: 10.1007/978-1-61737-982-6_2     Document Type: Chapter

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