Systemic Gene Transfer to Skeletal Muscle Using Reengineered AAV Vectors

Methods in Molecular Biology

Volumn 709, Issue , 2011, Pages 141-151

  Phillips, Jana L ^a   Hegge, Julia ^b   Wolff, Jon A ^b   Samulski, R Jude ^a   Asokan, Aravind ^a  

^a UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

^b Mirus Bio Corporation   (United States)

Author keywords

AAV; Capsid; Gene therapy; Gene transfer; Isolated limb infusion; Muscle; Reengineering; Tropism

Indexed keywords

CAPSID PROTEIN;

ADENO ASSOCIATED VIRUS; ANIMAL; ANIMAL MUSCULAR DYSTROPHY; ARTICLE; DISEASE MODEL; GENE THERAPY; GENE TRANSFER; GENE VECTOR; GENETIC ENGINEERING; GENETICS; METHODOLOGY; MOUSE; MUSCULAR DYSTROPHY; SKELETAL MUSCLE; TROPISM;

ANIMALS; CAPSID PROTEINS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC ENGINEERING; GENETIC VECTORS; MICE; MUSCLE, SKELETAL; MUSCULAR DYSTROPHIES; MUSCULAR DYSTROPHY, ANIMAL; TROPISM;

EID: 79960059878     PISSN: 10643745     EISSN: 19406029     Source Type: Book Series    
DOI: 10.1007/978-1-61737-982-6_9     Document Type: Chapter

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