From serendipity to therapy

Annual Review of Biochemistry

Volumn 80, Issue , 2011, Pages 1-15

  Neufeld, Elizabeth F ^a  

^a UNIVERSITY OF CALIFORNIA   (United States)

Author keywords

enzyme replacement; Hurler syndrome; lysosomes; mucopolysaccharidosis; Sanfilippo syndrome

Indexed keywords

BETA N ACETYLHEXOSAMINIDASE; COMPLEMENTARY DNA; GLUCOSYLCERAMIDASE; LEVO IDURONIDASE; LYSOSOME ENZYME; LYSOZYME; MANNOSE; MANNOSE 6 PHOSPHATE; RECOMBINANT ALPHA LEVO IDURONIDASE; RECOMBINANT ENZYME; TAU PROTEIN; UNCLASSIFIED DRUG;

ARTICLE; CELL INCLUSION; CLINICAL TRIAL (TOPIC); DISEASE MODEL; DOG; DRUG APPROVAL; ENZYME METABOLISM; ENZYME REPLACEMENT; GAUCHER DISEASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; HUMAN CELL CULTURE; HUNTER SYNDROME; HURLER SYNDROME; IMMUNOHISTOCHEMISTRY; MAROTEAUX LAMY SYNDROME; MEDICAL EDUCATION; NATIONAL HEALTH ORGANIZATION; NONHUMAN; PATHOGENESIS; POSTGRADUATE EDUCATION; PRIORITY JOURNAL; PROTEIN PHOSPHORYLATION; QUALITY OF LIFE; SANFILIPPO SYNDROME; TREATMENT DURATION; TREATMENT RESPONSE;

ANIMALS; EDUCATION, GRADUATE; HISTORY, 20TH CENTURY; HISTORY, 21ST CENTURY; HUMANS; LYSOSOMAL STORAGE DISEASES; NATIONAL INSTITUTES OF HEALTH (U.S.); RESEARCH; UNITED STATES; UNIVERSITIES;

EID: 79959432220     PISSN: 00664154     EISSN: 00664154     Source Type: Book Series    
DOI: 10.1146/annurev.biochem.031209.093756     Document Type: Article

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