Oral rapamycin in the treatment of patients with hamartoma syndromes and PTEN mutation

Pediatric Blood and Cancer

Volumn 57, Issue 2, 2011, Pages 321-323

  Iacobas, Ionela ^a   Burrows, Patricia E ^b   Adams, Denise M ^c   Sutton, Vernon R ^b   Hollier, Larry H ^b   Chintagumpala, Murali M ^b  

^a SAINT PETER S UNIVERSITY HOSPITAL   (United States)

^b BAYLOR COLLEGE OF MEDICINE   (United States)

^c CINCINNATI CHILDREN'S HOSPITAL MEDICAL CENTER   (United States)

Author keywords

Angiogenesis; Molecular biology and oncogenes; New agents; Vascular malformations

Indexed keywords

CHOLESTEROL; PHOSPHATIDYLINOSITOL 3,4,5 TRISPHOSPHATE 3 PHOSPHATASE; RAPAMYCIN;

ANGIOGRAPHY; ARTERIOVENOUS FISTULA; ARTERIOVENOUS MALFORMATION; ARTICLE; ARTIFICIAL EMBOLISM; BANNAYAN RILEY RUVACALBA SYNDROME; CASE REPORT; CAVERNOUS HEMANGIOMA; CHILD; CHOLESTEROL BLOOD LEVEL; DRUG BLOOD LEVEL; DRUG DOSE TITRATION; DRUG TOLERABILITY; EXON; FLEXION CONTRACTURE; FLEXOR TENDON; FOLLOW UP; FOREARM; GENE INSERTION; GENE MUTATION; GROWTH DISORDER; HAMARTOMA; HAND; HAND STRENGTH; HETEROZYGOTE DETECTION; HUMAN; HYPERCHOLESTEROLEMIA; KYPHOSIS; LIMB PAIN; MACROCEPHALY; MAGNETIC RESONANCE ANGIOGRAPHY; MALE; MEDICAL HISTORY; MOUTH ULCER; NEUROIMAGING; NUCLEAR MAGNETIC RESONANCE IMAGING; PENIS DISEASE; PHYSICAL MOBILITY; PRESCHOOL CHILD; PRIORITY JOURNAL; RANGE OF MOTION; SEQUENCE ANALYSIS; SIDE EFFECT; TREATMENT DURATION; ULTRASOUND; VASCULARIZATION; VEIN DILATATION;

ADMINISTRATION, ORAL; ANTIBIOTICS, ANTINEOPLASTIC; ARTERIOVENOUS MALFORMATIONS; CHILD; HAMARTOMA SYNDROME, MULTIPLE; HUMANS; MALE; SIROLIMUS; UPPER EXTREMITY;

EID: 79958805057     PISSN: 15455009     EISSN: 15455017     Source Type: Journal    
DOI: 10.1002/pbc.23098     Document Type: Article

References (6)

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