Successful cord blood transplantation in a 42-day-old boy with infantile Krabbe disease

International Journal of Hematology

Volumn 93, Issue 4, 2011, Pages 566-568

  Yagasaki, Hiroshi ^a   Kato, Maiko ^a   Ishige, Mika ^a   Shichino, Hiroyuki ^a   Chin, Motoaki ^a   Mugishima, Hideo ^a  

^a NIHON UNIVERSITY   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

BUSULFAN; CYCLOSPORIN A; CYTARABINE; FLUDARABINE; GALACTOSYLCERAMIDE; MELPHALAN; METHOTREXATE; PROTEIN; THYMOCYTE ANTIBODY;

CASE REPORT; CHIMERA; CORD BLOOD STEM CELL TRANSPLANTATION; DNA SEQUENCE; DRUG BLOOD LEVEL; ENGRAFTMENT; ENZYME ACTIVITY; EVOKED BRAIN STEM AUDITORY RESPONSE; GENOTYPE; GLOBOID CELL LEUKODYSTROPHY; GRAFT VERSUS HOST REACTION; HUMAN; INFANT; LETTER; LOW DRUG DOSE; MALE; OUTCOME ASSESSMENT; PROTEIN BLOOD LEVEL; THROMBOCYTE TRANSFUSION; TREATMENT INDICATION;

BUSULFAN; CORD BLOOD STEM CELL TRANSPLANTATION; FETAL BLOOD; HUMANS; IMMUNOSUPPRESSIVE AGENTS; INFANT; LEUKODYSTROPHY, GLOBOID CELL; MALE;

EID: 79955937357     PISSN: 09255710     EISSN: None     Source Type: Journal    
DOI: 10.1007/s12185-011-0835-6     Document Type: Letter

References (8)

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4. Escolar ML, Poe MD, Provenzale JM, Richards KC, Allison J, Wood S, et al. Transplantation of umbilical-cord blood in babies with infantile Krabbe's disease. New Eng J Med. 2005;352:2069-81. (Pubitemid 40664308)
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7. Prasad VK, Mendizabal A, Parikh SH, Szabolcs P, Driscoll TA, Page K, et al. Unrelated donor umbilical cord blood transplantation for inherited metabolic disorders in 159 pediatric patients from a single center: influence of cellular composition of the graft on transplantation outcomes. Blood. 2008;112:2979-89.
8. Tokimasa S, Ohta H, Takizawa S, Kusuki S, Hashii Y, Sakai N, et al. Umbilical cord-blood transplantations from unrelated donors in patients with inherited metabolic diseases: Single-institute experience. Pediatr Transplant. 2008;12:672-6.