Allogeneic cellular gene therapy for hemoglobinopathies

Hematology/Oncology Clinics of North America

Volumn 24, Issue 6, 2010, Pages 1145-1163

  Gaziev, Javid ^a   Lucarelli, Guido ^a  

^a TOR VERGATA UNIVERSITY HOSPITAL   (Italy)

Author keywords

Cellular gene therapy; Sickle cell anemia; Stem cell transplantation; Thalassemia

Indexed keywords

AZATHIOPRINE; BUSULFAN; CYCLOPHOSPHAMIDE; CYCLOSPORIN; DEFEROXAMINE; ERYTHROPOIETIN; FLUDARABINE; GRANULOCYTE COLONY STIMULATING FACTOR; HYDROXYUREA; METHOTREXATE; METHYLPREDNISOLONE; THYMOCYTE ANTIBODY;

ALLOGENEIC PERIPHERAL BLOOD STEM CELL TRANSPLANTATION; BETA THALASSEMIA; BLOOD TRANSFUSION; GENE THERAPY; GRAFT FAILURE; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMOGLOBINOPATHY; HUMAN; IRON CHELATION; LOW DRUG DOSE; PRIORITY JOURNAL; PROPHYLAXIS; REVIEW; SICKLE CELL ANEMIA; SURVIVAL RATE;

ANEMIA, SICKLE CELL; CORD BLOOD STEM CELL TRANSPLANTATION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMOGLOBINOPATHIES; HISTOCOMPATIBILITY TESTING; HUMANS; THALASSEMIA; TISSUE DONORS; TRANSPLANTATION CONDITIONING; TRANSPLANTATION, HOMOLOGOUS;

EID: 78249273618     PISSN: 08898588     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.hoc.2010.08.004     Document Type: Review

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