Systematic evidence review of newborn screening and treatment of severe combined immunodeficiency

Pediatrics

Volumn 125, Issue 5, 2010, Pages

  Lipstein, Ellen A ^a   Vorono, Sienna ^a,b   Browning, Marsha F ^a,c   Green, Nancy S ^d   Kemper, Alex R ^e   Knapp, Alixandra A ^a   Prosser, Lisa A ^f   Perrin, James M ^a,c  

^a MASSACHUSETTS GENERAL HOSPITAL   (United States)

^b BROWN UNIVERSITY   (United States)

^c HARVARD MEDICAL SCHOOL   (United States)

^d Och Spine at New York Presbyterian Hospitals   (United States)

^e DUKE CLINICAL RESEARCH INSTITUTE   (United States)

^f UNIVERSITY OF MICHIGAN HEALTH SYSTEM   (United States)

Author keywords

Bone marrow transplant; Evidence review; Health policy; Newborn screening; Severe combined immunodeficiency

Indexed keywords

CHILD DEATH; COST EFFECTIVENESS ANALYSIS; COST OF ILLNESS; DISEASE SEVERITY; HUMAN; INFECTION; NEWBORN SCREENING; PRIORITY JOURNAL; REVIEW; SCREENING TEST; SENSITIVITY AND SPECIFICITY; SEVERE COMBINED IMMUNODEFICIENCY; SYSTEMATIC REVIEW;

BONE MARROW TRANSPLANTATION; CHILD; CHILD, PRESCHOOL; COST-BENEFIT ANALYSIS; EVIDENCE-BASED MEDICINE; FEMALE; HEALTH POLICY; HEALTH PRIORITIES; HISTOCOMPATIBILITY TESTING; HUMANS; INFANT; INFANT, NEWBORN; MALE; NEONATAL SCREENING; SEVERE COMBINED IMMUNODEFICIENCY; SURVIVAL RATE; TREATMENT OUTCOME; UNITED STATES;

EID: 77951778042     PISSN: 00314005     EISSN: 10984275     Source Type: Journal    
DOI: 10.1542/peds.2009-1567     Document Type: Review

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