Homologous recombination in human iPS and ES cells for use in gene correction therapy

Drug Discovery Today

Volumn 15, Issue 5-6, 2010, Pages 198-202

  Nakayama, Manabu ^a,b  

^a KAZUSA DNA RESEARCH INSTITUTE   (Japan)

^b CHIBA UNIVERSITY   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; HYPOXANTHINE PHOSPHORIBOSYLTRANSFERASE; NUCLEASE; OCTAMER TRANSCRIPTION FACTOR 4; RECOMBINASE; RETROVIRUS VECTOR; THYMIDINE KINASE; ZINC FINGER PROTEIN;

CELL VIABILITY; CYTOTOXICITY; DNA MODIFICATION; ELECTROPORATION; EMBRYONIC STEM CELL; GENE CASSETTE; GENE CORRECTION THERAPY; GENE EXPRESSION REGULATION; GENE LOCUS; GENE MUTATION; GENE SILENCING; GENE TARGETING; GENE TECHNOLOGY; GENE THERAPY; GENE TRANSFER; GENETIC DISORDER; HOMOLOGOUS RECOMBINATION; HUMAN; HUMAN CELL CULTURE; HUMAN GENOME; LESCH NYHAN SYNDROME; NONHUMAN; PLURIPOTENT STEM CELL; REPORTER GENE; REVIEW; SAFETY; VIRAL GENE DELIVERY SYSTEM;

ANIMALS; CELL CULTURE TECHNIQUES; EMBRYONIC STEM CELLS; GENE THERAPY; HUMANS; INDUCED PLURIPOTENT STEM CELLS; RECOMBINATION, GENETIC; TARGETED GENE REPAIR;

EID: 77649233529     PISSN: 13596446     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.drudis.2010.01.006     Document Type: Review

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