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Volumn 115, Issue 3, 2010, Pages 500-509

Induction of immune tolerance to FIX by intramuscular AAV gene transfer is independent of the activation status of dendritic cells

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; BLOOD CLOTTING FACTOR 9; CD40 ANTIGEN; LIPOPOLYSACCHARIDE;

EID: 77449143240     PISSN: 00064971     EISSN: 15280020     Source Type: Journal    
DOI: 10.1182/blood-2009-08-239509     Document Type: Article
Times cited : (4)

References (27)
  • 2
    • 0037103167 scopus 로고    scopus 로고
    • Dangerous liaisons: The role of "danger" signals in the immune response to gene therapy
    • Brown BD, Lillicrap D. Dangerous liaisons: the role of "danger" signals in the immune response to gene therapy. Blood. 2002;100:1133-1140.
    • (2002) Blood , vol.100 , pp. 1133-1140
    • Brown, B.D.1    Lillicrap, D.2
  • 3
    • 33644820684 scopus 로고    scopus 로고
    • Successful transduction of liver in hemophilia by AAV-factor IX and limitations imposed by the host immune response
    • Manno CS, Pierce GF, Arruda VR, et al. Successful transduction of liver in hemophilia by AAV-factor IX and limitations imposed by the host immune response. Nat Med. 2006;12:342-347.
    • (2006) Nat Med , vol.12 , pp. 342-347
    • Manno, C.S.1    Pierce, G.F.2    Arruda, V.R.3
  • 4
    • 0142089747 scopus 로고    scopus 로고
    • Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer
    • Raper SE, Chirmule N, Lee FS, et al. Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer. Mol Genet Metab. 2003; 80:148-158.
    • (2003) Mol Genet Metab , vol.80 , pp. 148-158
    • Raper, S.E.1    Chirmule, N.2    Lee, F.S.3
  • 5
    • 0028201732 scopus 로고
    • Tolerance, danger, and the extended family
    • Matzinger P. Tolerance, danger, and the extended family. Annu Rev Immunol. 1994;12:991-1045.
    • (1994) Annu Rev Immunol , vol.12 , pp. 991-1045
    • Matzinger, P.1
  • 6
    • 46749117207 scopus 로고    scopus 로고
    • Determination of T-cell fate by dendritic cells
    • Diebold SS. Determination of T-cell fate by dendritic cells. Immunol Cell Biol. 2008;86:389-397.
    • (2008) Immunol Cell Biol , vol.86 , pp. 389-397
    • Diebold, S.S.1
  • 7
    • 0035838984 scopus 로고    scopus 로고
    • Dendritic cells: Specialized and regulated antigen processing machines
    • Mellman I, Steinman RM. Dendritic cells: specialized and regulated antigen processing machines. Cell. 2001;106:255-258.
    • (2001) Cell , vol.106 , pp. 255-258
    • Mellman, I.1    Steinman, R.M.2
  • 8
    • 0034919938 scopus 로고    scopus 로고
    • Dendritic cell lineage, plasticity and cross-regulation
    • Liu YJ, Kanzler H, Soumelis V, Gilliet M. Dendritic cell lineage, plasticity and cross-regulation. Nat Immunol. 2001;2:585-589.
    • (2001) Nat Immunol , vol.2 , pp. 585-589
    • Liu, Y.J.1    Kanzler, H.2    Soumelis, V.3    Gilliet, M.4
  • 10
    • 33748162638 scopus 로고    scopus 로고
    • Tolerogenic dendritic cells: Cytokine modulation comes of age
    • Rutella S, Danese S, Leone G. Tolerogenic dendritic cells: cytokine modulation comes of age. Blood. 2006;108:1435-1440.
    • (2006) Blood , vol.108 , pp. 1435-1440
    • Rutella, S.1    Danese, S.2    Leone, G.3
  • 11
    • 42549161844 scopus 로고    scopus 로고
    • The host response to adenovirus, helper-dependent adenovirus, and adeno-associated virus in mouse liver
    • McCaffrey AP, Fawcett P, Nakai H, et al. The host response to adenovirus, helper-dependent adenovirus, and adeno-associated virus in mouse liver. Mol Ther. 2008;16:931-941.
    • (2008) Mol Ther , vol.16 , pp. 931-941
    • McCaffrey, A.P.1    Fawcett, P.2    Nakai, H.3
  • 12
    • 1642525192 scopus 로고    scopus 로고
    • Role of viral vectors and virion shells in cellular gene expression
    • Stilwell JL, Samulski RJ. Role of viral vectors and virion shells in cellular gene expression. Mol Ther. 2004;9:337-346.
    • (2004) Mol Ther , vol.9 , pp. 337-346
    • Stilwell, J.L.1    Samulski, R.J.2
  • 13
    • 34250193312 scopus 로고    scopus 로고
    • Efficient induction of immune tolerance to coagulation factor IX following direct intramuscular gene transfer
    • Cohn EF, Zhuo J, Kelly ME, Chao HJ. Efficient induction of immune tolerance to coagulation factor IX following direct intramuscular gene transfer. J Thromb Haemost. 2007;5:1227-1236.
    • (2007) J Thromb Haemost , vol.5 , pp. 1227-1236
    • Cohn, E.F.1    Zhuo, J.2    Kelly, M.E.3    Chao, H.J.4
  • 14
    • 0034842912 scopus 로고    scopus 로고
    • Sustained and complete phenotype correction of hemophilia B mice following intramuscular injection of AAV1 serotype vectors
    • Chao H, Monahan PE, Liu Y, Samulski RJ, Walsh CE. Sustained and complete phenotype correction of hemophilia B mice following intramuscular injection of AAV1 serotype vectors. Mol Ther. 2001;4:217-222.
    • (2001) Mol Ther , vol.4 , pp. 217-222
    • Chao, H.1    Monahan, P.E.2    Liu, Y.3    Samulski, R.J.4    Walsh, C.E.5
  • 15
    • 67349217385 scopus 로고    scopus 로고
    • Induction of immune tolerance to FIX following muscular AAV gene transfer is AAV-dose/FIX-level dependent
    • Kelly ME, Zhuo J, Bharadwaj AS, Chao H. Induction of immune tolerance to FIX following muscular AAV gene transfer is AAV-dose/FIX-level dependent. Mol Ther. 2009;17:857-863.
    • (2009) Mol Ther , vol.17 , pp. 857-863
    • Kelly, M.E.1    Zhuo, J.2    Bharadwaj, A.S.3    Chao, H.4
  • 16
    • 0028934815 scopus 로고
    • Cellular and humoral immune responses to adenoviral vectors containing factor IX gene: Tolerization of factor IX and vector antigens allows for long-term expression
    • Dai Y, Schwarz EM, Gu D, Zhang WW, Sarvetnick N, Verma IM. Cellular and humoral immune responses to adenoviral vectors containing factor IX gene: tolerization of factor IX and vector antigens allows for long-term expression. Proc Natl Acad Sci U S A. 1995;92:1401-1405.
    • (1995) Proc Natl Acad Sci U S a , vol.92 , pp. 1401-1405
    • Dai, Y.1    Schwarz, E.M.2    Gu, D.3    Zhang, W.W.4    Sarvetnick, N.5    Verma, I.M.6
  • 17
    • 0035877984 scopus 로고    scopus 로고
    • Factors influencing the development of an anti-factor IX (FIX) immune response following administration of adeno-associated virus-FIX
    • Ge Y, Powell S, Van Roey M, McArthur JG. Factors influencing the development of an anti-factor IX (FIX) immune response following administration of adeno-associated virus-FIX. Blood. 2001; 97:3733-3737.
    • (2001) Blood , vol.97 , pp. 3733-3737
    • Ge, Y.1    Powell, S.2    Van Roey, M.3    McArthur, J.G.4
  • 18
    • 33847186699 scopus 로고    scopus 로고
    • Transgene expression levels and kinetics determine risk of humoral immune response modeled in factor IX knockout and missense mutant mice
    • Zhang TP, Jin DY, Wardrop RM III, et al. Transgene expression levels and kinetics determine risk of humoral immune response modeled in factor IX knockout and missense mutant mice. Gene Ther. 2007;14:429-440.
    • (2007) Gene Ther , vol.14 , pp. 429-440
    • Zhang, T.P.1    Jin, D.Y.2    Wardrop III, R.M.3
  • 19
    • 0034853102 scopus 로고    scopus 로고
    • Risk and prevention of anti-factor IX formation in AAV-mediated gene transfer in the context of a large deletion of F9
    • Fields PA, Arruda VR, Armstrong E, et al. Risk and prevention of anti-factor IX formation in AAV-mediated gene transfer in the context of a large deletion of F9. Mol Ther. 2001;4:201-210.
    • (2001) Mol Ther , vol.4 , pp. 201-210
    • Fields, P.A.1    Arruda, V.R.2    Armstrong, E.3
  • 20
    • 0036376642 scopus 로고    scopus 로고
    • Influence of vector dose on factor IX-specific T and B cell responses in muscle-directed gene therapy
    • Herzog RW, Fields PA, Arruda VR, et al. Influence of vector dose on factor IX-specific T and B cell responses in muscle-directed gene therapy. Hum Gene Ther. 2002;13:1281-1291.
    • (2002) Hum Gene Ther , vol.13 , pp. 1281-1291
    • Herzog, R.W.1    Fields, P.A.2    Arruda, V.R.3
  • 21
    • 0035500862 scopus 로고    scopus 로고
    • Lipopolysaccharides from distinct pathogens induce different classes of immune responses in vivo
    • Pulendran B, Kumar P, CutlerCW, Mohamadzadeh M, Van Dyke T, Banchereau J. Lipopolysaccharides from distinct pathogens induce different classes of immune responses in vivo. J Immunol. 2001;167: 5067-5076.
    • (2001) J Immunol , vol.167 , pp. 5067-5076
    • Pulendran, B.1    Kumar, P.2    Cutler, C.W.3    Mohamadzadeh, M.4    Van Dyke, T.5    Banchereau, J.6
  • 22
  • 23
    • 0033557713 scopus 로고    scopus 로고
    • CD40 activation boosts T cell immunity in vivo by enhancing T cell clonal expansion and delaying peripheral T cell deletion
    • Maxwell JR, Campbell JD, Kim CH, Vella AT. CD40 activation boosts T cell immunity in vivo by enhancing T cell clonal expansion and delaying peripheral T cell deletion. J Immunol. 1999;162: 2024-2034.
    • (1999) J Immunol , vol.162 , pp. 2024-2034
    • Maxwell, J.R.1    Campbell, J.D.2    Kim, C.H.3    Vella, A.T.4
  • 24
    • 0035080378 scopus 로고    scopus 로고
    • Intravenous administration of an E1/E3-deleted adenoviral vector induces tolerance to factor IX in C57BL/6 mice
    • Fields PA, Armstrong E, Hagstrom JN, et al. Intravenous administration of an E1/E3-deleted adenoviral vector induces tolerance to factor IX in C57BL/6 mice. Gene Ther. 2001;8:354-361.
    • (2001) Gene Ther , vol.8 , pp. 354-361
    • Fields, P.A.1    Armstrong, E.2    Hagstrom, J.N.3
  • 26
    • 2142751261 scopus 로고    scopus 로고
    • Evaluation of risks related to the use of adeno-associated virus-based vectors
    • Tenenbaum L, Lehtonen E, Monahan PE. Evaluation of risks related to the use of adeno-associated virus-based vectors. Curr Gene Ther. 2003;3:545-565.
    • (2003) Curr Gene Ther , vol.3 , pp. 545-565
    • Tenenbaum, L.1    Lehtonen, E.2    Monahan, P.E.3
  • 27
    • 2342561729 scopus 로고    scopus 로고
    • Targeting lentiviral vector expression to hepatocytes limits transgene-specific immune response and establishes long-term expression of human antihemophilic factor IX in mice
    • Follenzi A, Battaglia M, Lombardo A, Annoni A, Roncarolo MG, Naldini L. Targeting lentiviral vector expression to hepatocytes limits transgene-specific immune response and establishes long-term expression of human antihemophilic factor IX in mice. Blood. 2004;103:3700-3709.
    • (2004) Blood , vol.103 , pp. 3700-3709
    • Follenzi, A.1    Battaglia, M.2    Lombardo, A.3    Annoni, A.4    Roncarolo, M.G.5    Naldini, L.6


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.