Targeted correction of a thalassemia-associated β-globin mutation induced by pseudo-complementary peptide nucleic acids

Nucleic Acids Research

Volumn 37, Issue 11, 2009, Pages 3635-3644

  Lonkar, Pallavi ^a   Kim, Ki Hyun ^a   Kuan, Jean Y ^a   Chin, Joanna Y ^a   Rogers, Faye A ^a   Knauert, Melissa P ^a   Kole, Ryszard ^b   Nielsen, Peter E ^c   Glazer, Peter M ^a  

^a YALE UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

^c UNIVERSITY OF COPENHAGEN   (Denmark)

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLOBIN; PEPTIDE NUCLEIC ACID;

ARTICLE; BINDING AFFINITY; CONTROLLED STUDY; DNA BINDING; DNA REPAIR; DNA SEQUENCE; FIBROBLAST; GENE LOCUS; GENE MUTATION; GENE TARGETING; HUMAN; HUMAN CELL; INTRON; PLASMID; PRIORITY JOURNAL; PROTEIN BINDING; PROTEIN MOTIF; PROTEIN STRUCTURE; RNA SPLICING; TARGETED GENE REPAIR; THALASSEMIA;

ANIMALS; BETA-GLOBINS; CELL LINE; CHO CELLS; CRICETINAE; CRICETULUS; GENE TARGETING; HUMANS; MUTATION; PEPTIDE NUCLEIC ACIDS; PLASMIDS; RECOMBINATION, GENETIC; S PHASE; THALASSEMIA; XERODERMA PIGMENTOSUM GROUP A PROTEIN;

MAMMALIA;

EID: 67649832344     PISSN: 03051048     EISSN: 13624962     Source Type: Journal    
DOI: 10.1093/nar/gkp217     Document Type: Article

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