Gene induction for the treatment of methylmalonic aciduria

Journal of Gene Medicine

Volumn 11, Issue 4, 2009, Pages 361-369

  Hu, Ruimei ^a,b   Buck, Nicole E ^a   Khaniani, Mahmoud S ^a,c   Wood, Leonie ^a   Wardan, Hady ^a   Benoist, Jean Francois ^d   Li, Lingli ^a   Vadolas, Jim ^a   Sarsero, Joseph P ^a   Ioannou, Panos A ^a   Peters, Heidi L ^a  

^a UNIVERSITY OF MELBOURNE   (Australia)

^b SHANDONG UNIVERSITY   (China)

^c TABRIZ UNIVERSITY OF MEDICAL SCIENCES   (Iran)

^d HÔPITAL ROBERT DEBRÉ   (France)

Author keywords

Gene induction; Genomic reporter assay; Methylmalonic aciduria

Indexed keywords

ACICLOVIR; ADEFOVIR; ADENOSINE TRIPHOSPHATE; ALPHA TOCOPHEROL; ASCORBIC ACID; BEZAFIBRATE; BUTYRIC ACID; CARNITINE; CISPLATIN; DEFERIPRONE; DEOXYCHOLIC ACID; DEXAMETHASONE; EMTRICITABINE; ENHANCED GREEN FLUORESCENT PROTEIN; ERYTHROPOIETIN; GLUTATHIONE; HEMIN; HYDROXOCOBALAMIN; HYDROXYUREA; IMIDAZOLE; LAMIVUDINE; MESSENGER RNA; METHYLMALONYL COENZYME A MUTASE; RESVERATROL; RETINOIC ACID; RIBAVIRIN; TENOFOVIR; UNINDEXED DRUG; VALGANCICLOVIR; ZIDOVUDINE;

ARTICLE; CONCENTRATION RESPONSE; CONTROLLED STUDY; DRUG DETERMINATION; DRUG POTENCY; DRUG SCREENING; DRUG TARGETING; FLOW CYTOMETRY; GENE CASSETTE; GENE CONSTRUCT; GENE EXPRESSION REGULATION; GENE INDUCTION; GENE THERAPY; HELA CELL; HOMOLOGOUS RECOMBINATION; HUMAN; HUMAN CELL; METHYLMALONIC ACIDURIA; MOLECULAR CLONING; PRIORITY JOURNAL; REPORTER GENE; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; UPREGULATION;

ADENINE; CISPLATIN; DRUG EVALUATION, PRECLINICAL; GENE EXPRESSION REGULATION; GREEN FLUORESCENT PROTEINS; HELA CELLS; HUMANS; METABOLISM, INBORN ERRORS; METHYLMALONYL-COA MUTASE; PHOSPHONIC ACIDS; RNA, MESSENGER; ZIDOVUDINE;

EID: 65949124685     PISSN: 1099498X     EISSN: 15212254     Source Type: Journal    
DOI: 10.1002/jgm.1297     Document Type: Article

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