Disease rescue and increased lifespan in a model of cardiomyopathy and muscular dystrophy by combined AAV treatments

PLoS ONE

Volumn 4, Issue 3, 2009, Pages

  Vitiello, Carmen ^a   Faraso, Stefania ^a   Sorrentino, Nicolina Cristina ^a   Di Salvo, Giovanni ^b   Nusco, Edoardo ^a   Nigro, Gerardo ^b   Cutillo, Luisa ^a   Calabrò, Raffaele ^b   Auricchio, Alberto ^a,c   Nigro, Vincenzo ^a,b  

^a TELETHON INSTITUTE OF GENETICS AND MEDICINE TIGEM   (Italy)

^b SECOND UNIVERSITY OF NAPLES   (Italy)

^c UNIVERSITY OF NAPLES FEDERICO II   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; COMPLEMENTARY DNA; DELTA SARCOGLYCAN; SARCOGLYCAN;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CARDIOMYOPATHY; CONTROLLED STUDY; DRUG EFFICACY; GENE THERAPY; HAMSTER; HEART FUNCTION; LIFESPAN; MALE; MOTOR PERFORMANCE; MUSCLE FUNCTION; MUSCULAR DYSTROPHY; NONHUMAN; SEROTYPE; VIRAL GENE DELIVERY SYSTEM; ANIMAL; GENE VECTOR; GENETIC TRANSDUCTION; GENETICS; HEART MUSCLE; HUMAN; METABOLISM; METHODOLOGY; SKELETAL MUSCLE; SURVIVAL RATE;

ANIMALIA; CRICETINAE;

ANIMALS; CARDIOMYOPATHIES; CRICETINAE; DEPENDOVIRUS; DNA, COMPLEMENTARY; GENE THERAPY; GENETIC VECTORS; HUMANS; MUSCLE, SKELETAL; MUSCULAR DYSTROPHIES; MYOCARDIUM; SARCOGLYCANS; SURVIVAL RATE; TRANSDUCTION, GENETIC;

EID: 63749122186     PISSN: None     EISSN: 19326203     Source Type: Journal    
DOI: 10.1371/journal.pone.0005051     Document Type: Article

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