Sustained expression of α1-antitrypsin after transplantation of manipulated hematopoietic stem cells

American Journal of Respiratory Cell and Molecular Biology

Volumn 39, Issue 2, 2008, Pages 133-141

  Wilson, Andrew A ^a   Kwok, Letty W ^a   Hovav, Avi Hai ^b   Ohle, Sarah J ^a   Little, Frederic F ^a   Fine, Alan ^a   Kotton, Darrell N ^a  

^a BOSTON UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b HEBREW UNIVERSITY OF JERUSALEM   (Israel)

Author keywords

1 antitrypsin; Bone marrow; Gene therapy; Lung; Stem cells

Indexed keywords

ALPHA 1 ANTITRYPSIN; COMPLEMENTARY DNA; CYTOKINE; LENTIVIRUS VECTOR;

ADOLESCENT; ALPHA 1 ANTITRYPSIN DEFICIENCY; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; CELL RENEWAL; CELL STIMULATION; CONTROLLED STUDY; CYTOKINE RELEASE; DISEASE COURSE; DISEASE PREDISPOSITION; DNA TRANSFER; GENE EXPRESSION; GENE MUTATION; GENE THERAPY; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMATOPOIETIC SYSTEM; HORMONE RELEASE; HUMAN; HUMAN CELL; INTERNAL RIBOSOME ENTRY SITE; LUNG ALVEOLUS MACROPHAGE; LUNG EMPHYSEMA; MOUSE; MULTIPOTENT STEM CELL; NONHUMAN; PROTEIN EXPRESSION; REPORTER GENE; SPLEEN CELL; ANIMAL; BIOSYNTHESIS; CELL LINE; CYTOLOGY; GENE VECTOR; GENETIC TRANSDUCTION; GENETICS; HEMATOPOIETIC STEM CELL; LENTIVIRINAE; LUNG; METABOLISM; MUTATION;

MURINAE;

ALPHA 1-ANTITRYPSIN; ANIMALS; CELL LINE; GENES, REPORTER; GENETIC VECTORS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMATOPOIETIC STEM CELLS; HUMANS; LENTIVIRUS; LUNG; MICE; MULTIPOTENT STEM CELLS; MUTATION; TRANSDUCTION, GENETIC;

EID: 48649084090     PISSN: 10441549     EISSN: None     Source Type: Journal    
DOI: 10.1165/rcmb.2007-0133OC     Document Type: Article

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