-
1
-
-
9344231922
-
Bone marrow transplantation for sickle cell disease
-
Walters M.C., Patience M., Leisenring W., et al. Bone marrow transplantation for sickle cell disease. N Engl J Med 335 (1996) 369-376
-
(1996)
N Engl J Med
, vol.335
, pp. 369-376
-
-
Walters, M.C.1
Patience, M.2
Leisenring, W.3
-
2
-
-
0344522826
-
Non-myeloablative hematopoietic cell transplant for treatment of nonmalignant disorders in children
-
Woolfrey A.E., Pulsipher M.A., and Storb R. Non-myeloablative hematopoietic cell transplant for treatment of nonmalignant disorders in children. Int J Hematol 76 Suppl 2 (2002) 271-277
-
(2002)
Int J Hematol
, vol.76
, Issue.SUPPL. 2
, pp. 271-277
-
-
Woolfrey, A.E.1
Pulsipher, M.A.2
Storb, R.3
-
4
-
-
0037129435
-
Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy
-
Hacein-Bey-Abina S., Le Deist F., Carlier F., et al. Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy. N Engl J Med 346 (2002) 1185-1193
-
(2002)
N Engl J Med
, vol.346
, pp. 1185-1193
-
-
Hacein-Bey-Abina, S.1
Le Deist, F.2
Carlier, F.3
-
5
-
-
0037189401
-
Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning
-
Aiuti A., Slavin S., Aker M., et al. Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning. Science 296 (2002) 2410-2413
-
(2002)
Science
, vol.296
, pp. 2410-2413
-
-
Aiuti, A.1
Slavin, S.2
Aker, M.3
-
6
-
-
33645734405
-
Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1
-
Ott M.G., Schmidt M., Schwarzwaelder K., et al. Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1. Nat Med 12 (2006) 401-409
-
(2006)
Nat Med
, vol.12
, pp. 401-409
-
-
Ott, M.G.1
Schmidt, M.2
Schwarzwaelder, K.3
-
7
-
-
0034199170
-
Introduction of a xenogeneic gene via hematopoietic stem cells leads to specific tolerance in a rhesus monkey model
-
Heim D.A., Hanazono Y., Giri N., et al. Introduction of a xenogeneic gene via hematopoietic stem cells leads to specific tolerance in a rhesus monkey model. Mol Ther 1 (2000) 533-544
-
(2000)
Mol Ther
, vol.1
, pp. 533-544
-
-
Heim, D.A.1
Hanazono, Y.2
Giri, N.3
-
8
-
-
0029876727
-
Enhanced engraftment of hematopoietic progenitor cells in mice treated with granulocyte colony-stimulating factor before low-dose irradiation: implications for gene therapy
-
Mardiney III M., and Malech H.L. Enhanced engraftment of hematopoietic progenitor cells in mice treated with granulocyte colony-stimulating factor before low-dose irradiation: implications for gene therapy. Blood 87 (1996) 4049-4056
-
(1996)
Blood
, vol.87
, pp. 4049-4056
-
-
Mardiney III, M.1
Malech, H.L.2
-
9
-
-
0034981505
-
The effects of SCF/G-CSF prestimulation on radiation sensitivity and engraftment in nonmyeloablated murine hosts
-
Giri N., Kaushiva A., Wu T., Sellers S.E., and Tisdale J.F. The effects of SCF/G-CSF prestimulation on radiation sensitivity and engraftment in nonmyeloablated murine hosts. Exp Hematol 29 (2001) 779-785
-
(2001)
Exp Hematol
, vol.29
, pp. 779-785
-
-
Giri, N.1
Kaushiva, A.2
Wu, T.3
Sellers, S.E.4
Tisdale, J.F.5
-
10
-
-
0034809177
-
In vivo persistence of retrovirally transduced murine long-term repopulating cells is not limited by expression of foreign gene products in the fully or minimally myeloablated setting
-
Kang E., Giri N., Wu T., et al. In vivo persistence of retrovirally transduced murine long-term repopulating cells is not limited by expression of foreign gene products in the fully or minimally myeloablated setting. Hum Gene Ther 12 (2001) 1663-1672
-
(2001)
Hum Gene Ther
, vol.12
, pp. 1663-1672
-
-
Kang, E.1
Giri, N.2
Wu, T.3
-
11
-
-
0033587487
-
Retroviral marking and transplantation of rhesus hematopoietic cells by nonmyeloablative conditioning
-
Huhn R.D., Tisdale J.F., Agricola B., Metzger M.E., Donahue R.E., and Dunbar C.E. Retroviral marking and transplantation of rhesus hematopoietic cells by nonmyeloablative conditioning. Hum Gene Ther 10 (1999) 1783-1790
-
(1999)
Hum Gene Ther
, vol.10
, pp. 1783-1790
-
-
Huhn, R.D.1
Tisdale, J.F.2
Agricola, B.3
Metzger, M.E.4
Donahue, R.E.5
Dunbar, C.E.6
-
12
-
-
0034959561
-
Persistent low-level engraftment of rhesus peripheral blood progenitor cells transduced with the fanconi anemia C gene after conditioning with low-dose irradiation
-
Kang E.M., Hanazano Y., Frare P., et al. Persistent low-level engraftment of rhesus peripheral blood progenitor cells transduced with the fanconi anemia C gene after conditioning with low-dose irradiation. Mol Ther 3 (2001) 911-919
-
(2001)
Mol Ther
, vol.3
, pp. 911-919
-
-
Kang, E.M.1
Hanazano, Y.2
Frare, P.3
-
13
-
-
0001286133
-
Myleran in chronic myeloid leukaemia; chemical constitution and biological action
-
Haddow A., and Timmis G.M. Myleran in chronic myeloid leukaemia; chemical constitution and biological action. Lancet 264 (1953) 207-208
-
(1953)
Lancet
, vol.264
, pp. 207-208
-
-
Haddow, A.1
Timmis, G.M.2
-
14
-
-
50449139497
-
Myleran in chronic myeloid leukaemia; results of treatment
-
Galton D.A. Myleran in chronic myeloid leukaemia; results of treatment. Lancet 264 (1953) 208-213
-
(1953)
Lancet
, vol.264
, pp. 208-213
-
-
Galton, D.A.1
-
15
-
-
0021035301
-
Marrow transplantation for acute nonlymphocytic leukemia after treatment with busulfan and cyclophosphamide
-
Santos G.W., Tutschka P.J., Brookmeyer R., et al. Marrow transplantation for acute nonlymphocytic leukemia after treatment with busulfan and cyclophosphamide. N Engl J Med 309 (1983) 1347-1353
-
(1983)
N Engl J Med
, vol.309
, pp. 1347-1353
-
-
Santos, G.W.1
Tutschka, P.J.2
Brookmeyer, R.3
-
16
-
-
0023805068
-
Recipient preparation for bone marrow transplantation. I. Efficacy of total-body irradiation and busulfan
-
Mauch P., Down J.D., Warhol M., and Hellman S. Recipient preparation for bone marrow transplantation. I. Efficacy of total-body irradiation and busulfan. Transplantation 46 (1988) 205-210
-
(1988)
Transplantation
, vol.46
, pp. 205-210
-
-
Mauch, P.1
Down, J.D.2
Warhol, M.3
Hellman, S.4
-
17
-
-
0026331307
-
Lymphoid reconstitution after transplantation of congenic hematopoietic cells in busulfan-treated mice
-
Yeager A.M., Shinn C., and Pardoll D.M. Lymphoid reconstitution after transplantation of congenic hematopoietic cells in busulfan-treated mice. Blood 78 (1991) 3312-3316
-
(1991)
Blood
, vol.78
, pp. 3312-3316
-
-
Yeager, A.M.1
Shinn, C.2
Pardoll, D.M.3
-
18
-
-
0034567061
-
Acute safety and pharmacokinetics of intravenous busulfan when used with oral busulfan and cyclophosphamide as pretransplantation conditioning therapy: a phase I study
-
Andersson B.S., Madden T., Tran H.T., et al. Acute safety and pharmacokinetics of intravenous busulfan when used with oral busulfan and cyclophosphamide as pretransplantation conditioning therapy: a phase I study. Biol Blood Marrow Transplant 6 (2000) 548-554
-
(2000)
Biol Blood Marrow Transplant
, vol.6
, pp. 548-554
-
-
Andersson, B.S.1
Madden, T.2
Tran, H.T.3
-
19
-
-
0036402048
-
Evaluation of safety and pharmacokinetics of administering intravenous busulfan in a twice-daily or daily schedule to patients with advanced hematologic malignant disease undergoing stem cell transplantation
-
Fernandez H.F., Tran H.T., Albrecht F., Lennon S., Caldera H., and Goodman M.S. Evaluation of safety and pharmacokinetics of administering intravenous busulfan in a twice-daily or daily schedule to patients with advanced hematologic malignant disease undergoing stem cell transplantation. Biol Blood Marrow Transplant 8 (2002) 486-492
-
(2002)
Biol Blood Marrow Transplant
, vol.8
, pp. 486-492
-
-
Fernandez, H.F.1
Tran, H.T.2
Albrecht, F.3
Lennon, S.4
Caldera, H.5
Goodman, M.S.6
-
20
-
-
3242810563
-
Once-daily intravenous busulfan and fludarabine: clinical and pharmacokinetic results of a myeloablative, reduced-toxicity conditioning regimen for allogeneic stem cell transplantation in AML and MDS
-
de Lima M., Couriel D., Thall P.F., et al. Once-daily intravenous busulfan and fludarabine: clinical and pharmacokinetic results of a myeloablative, reduced-toxicity conditioning regimen for allogeneic stem cell transplantation in AML and MDS. Blood 104 (2004) 857-864
-
(2004)
Blood
, vol.104
, pp. 857-864
-
-
de Lima, M.1
Couriel, D.2
Thall, P.F.3
-
21
-
-
33845984552
-
Pharmacokinetics of once-daily IV busulfan as part of pretransplantation preparative regimens: a comparison with an every 6-hour dosing schedule
-
Madden T., de Lima M., Thapar N., et al. Pharmacokinetics of once-daily IV busulfan as part of pretransplantation preparative regimens: a comparison with an every 6-hour dosing schedule. Biol Blood Marrow Transplant 13 (2007) 56-64
-
(2007)
Biol Blood Marrow Transplant
, vol.13
, pp. 56-64
-
-
Madden, T.1
de Lima, M.2
Thapar, N.3
-
22
-
-
31844442082
-
Busulfan pharmacokinetics, toxicity, and low-dose conditioning for autologous transplantation of genetically modified hematopoietic stem cells in the rhesus macaque model
-
Kang E.M., Hsieh M.M., Metzger M., et al. Busulfan pharmacokinetics, toxicity, and low-dose conditioning for autologous transplantation of genetically modified hematopoietic stem cells in the rhesus macaque model. Exp Hematol 34 (2006) 132-139
-
(2006)
Exp Hematol
, vol.34
, pp. 132-139
-
-
Kang, E.M.1
Hsieh, M.M.2
Metzger, M.3
-
23
-
-
33644923202
-
Effects of busulfan dose escalation on engraftment of infant rhesus monkey hematopoietic stem cells after gene marking by a lentiviral vector
-
Kahl C.A., Tarantal A.F., Lee C.I., et al. Effects of busulfan dose escalation on engraftment of infant rhesus monkey hematopoietic stem cells after gene marking by a lentiviral vector. Exp Hematol 34 (2006) 369-381
-
(2006)
Exp Hematol
, vol.34
, pp. 369-381
-
-
Kahl, C.A.1
Tarantal, A.F.2
Lee, C.I.3
-
24
-
-
0037896838
-
The action of chlorambucil (CB. 1348) and busulphan (myleran) on the haemopoietic organs of the rat
-
Elson L.A., Galton D.A., and Till M. The action of chlorambucil (CB. 1348) and busulphan (myleran) on the haemopoietic organs of the rat. Br J Haematol 4 (1958) 355-374
-
(1958)
Br J Haematol
, vol.4
, pp. 355-374
-
-
Elson, L.A.1
Galton, D.A.2
Till, M.3
-
25
-
-
0016281114
-
The chemical and biological properties of busulphan ("Myleran")
-
Dunn C.D. The chemical and biological properties of busulphan ("Myleran"). Exp Hematol 2 (1974) 101-117
-
(1974)
Exp Hematol
, vol.2
, pp. 101-117
-
-
Dunn, C.D.1
-
26
-
-
20244383694
-
Nonmyeloablative hematopoietic cell transplantation: status quo and future perspectives
-
Mielcarek M., Sandmaier B.M., Maloney D.G., et al. Nonmyeloablative hematopoietic cell transplantation: status quo and future perspectives. J Clin Immunol 22 (2002) 70-74
-
(2002)
J Clin Immunol
, vol.22
, pp. 70-74
-
-
Mielcarek, M.1
Sandmaier, B.M.2
Maloney, D.G.3
-
27
-
-
0038651208
-
Review of "minitransplantation": nonmyeloablative allogeneic hematopoietic stem cell transplantation
-
Georges G.E., and Storb R. Review of "minitransplantation": nonmyeloablative allogeneic hematopoietic stem cell transplantation. Int J Hematol 77 (2003) 3-14
-
(2003)
Int J Hematol
, vol.77
, pp. 3-14
-
-
Georges, G.E.1
Storb, R.2
-
28
-
-
28844458445
-
Allogeneic hematopoietic cell transplantation following nonmyeloablative conditioning as treatment for hematologic malignancies and inherited blood disorders
-
Baron F., and Storb R. Allogeneic hematopoietic cell transplantation following nonmyeloablative conditioning as treatment for hematologic malignancies and inherited blood disorders. Mol Ther 13 (2006) 26-41
-
(2006)
Mol Ther
, vol.13
, pp. 26-41
-
-
Baron, F.1
Storb, R.2
-
29
-
-
0016314288
-
Marrow transplantation in the busulfan-treated rat: preclinical model of aplastic anemia
-
Santos G.W., and Tutschka P.J. Marrow transplantation in the busulfan-treated rat: preclinical model of aplastic anemia. J Natl Cancer Inst 53 (1974) 1781-1785
-
(1974)
J Natl Cancer Inst
, vol.53
, pp. 1781-1785
-
-
Santos, G.W.1
Tutschka, P.J.2
-
30
-
-
0035879193
-
Costimulation blockade, busulfan, and bone marrow promote titratable macrochimerism, induce transplantation tolerance, and correct genetic hemoglobinopathies with minimal myelosuppression
-
Adams A.B., Durham M.M., Kean L., et al. Costimulation blockade, busulfan, and bone marrow promote titratable macrochimerism, induce transplantation tolerance, and correct genetic hemoglobinopathies with minimal myelosuppression. J Immunol 167 (2001) 1103-1111
-
(2001)
J Immunol
, vol.167
, pp. 1103-1111
-
-
Adams, A.B.1
Durham, M.M.2
Kean, L.3
-
31
-
-
31144447883
-
Low dose busulfan facilitates chimerism and tolerance in a murine model
-
Anam K., Black A.T., and Hale D.A. Low dose busulfan facilitates chimerism and tolerance in a murine model. Transpl Immunol 15 (2006) 199-204
-
(2006)
Transpl Immunol
, vol.15
, pp. 199-204
-
-
Anam, K.1
Black, A.T.2
Hale, D.A.3
-
32
-
-
33751175651
-
Correction of the disease phenotype in canine leukocyte adhesion deficiency using ex vivo hematopoietic stem cell gene therapy
-
Bauer Jr. T.R., Hai M., Tuschong L.M., et al. Correction of the disease phenotype in canine leukocyte adhesion deficiency using ex vivo hematopoietic stem cell gene therapy. Blood 108 (2006) 3313-3320
-
(2006)
Blood
, vol.108
, pp. 3313-3320
-
-
Bauer Jr., T.R.1
Hai, M.2
Tuschong, L.M.3
-
33
-
-
33845365042
-
Genetics, biology and clinical management of myeloid cell primary immune deficiencies: chronic granulomatous disease and leukocyte adhesion deficiency
-
Malech H.L., and Hickstein D.D. Genetics, biology and clinical management of myeloid cell primary immune deficiencies: chronic granulomatous disease and leukocyte adhesion deficiency. Curr Opin Hematol 14 (2007) 29-36
-
(2007)
Curr Opin Hematol
, vol.14
, pp. 29-36
-
-
Malech, H.L.1
Hickstein, D.D.2
-
34
-
-
7044220536
-
Gene therapy for the hemoglobin disorders
-
Persons D.A., and Tisdale J.F. Gene therapy for the hemoglobin disorders. Semin Hematol 41 (2004) 279-286
-
(2004)
Semin Hematol
, vol.41
, pp. 279-286
-
-
Persons, D.A.1
Tisdale, J.F.2
-
35
-
-
33846196263
-
Therapeutic options for patients with severe beta-thalassemia: the need for globin gene therapy
-
Sadelain M., Boulad F., Galanello R., et al. Therapeutic options for patients with severe beta-thalassemia: the need for globin gene therapy. Hum Gene Ther 18 (2007) 1-9
-
(2007)
Hum Gene Ther
, vol.18
, pp. 1-9
-
-
Sadelain, M.1
Boulad, F.2
Galanello, R.3
|