Adeno-associated virus-based gene therapy for inherited disorders

Pediatric Research

Volumn 58, Issue 6, 2005, Pages 1143-1147

  Flotte, Terence R ^a  

^a UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA 1 ANTITRYPSIN; BETA ACTIN; PARVOVIRUS VECTOR; RECOMBINANT ALPHA 1 ANTITRYPSIN; RECOMBINANT PROTEIN; RECOMBINANT TRANSMEMBRANE CONDUCTANCE REGULATOR; TRANSMEMBRANE CONDUCTANCE REGULATOR; UNCLASSIFIED DRUG;

ALPHA 1 ANTITRYPSIN DEFICIENCY; CLINICAL TRIAL; CYSTIC FIBROSIS; CYTOMEGALOVIRUS; DRUG EFFICACY; GENE TRANSFER; GENETIC DISORDER; HUMAN; NONHUMAN; PRIORITY JOURNAL; PROMOTER REGION; REVIEW; SAFETY; SEROTYPE; VIRAL GENE DELIVERY SYSTEM; VIRUS CAPSID; VIRUS MUTANT; VIRUS RECOMBINANT; VIRUS TYPING; ADENO ASSOCIATED VIRUS; CHILD; FEMALE; GENE THERAPY; GENE VECTOR; GENETICS; MALE; PRESCHOOL CHILD;

CHILD; CHILD, PRESCHOOL; CYSTIC FIBROSIS; DEPENDOVIRUS; FEMALE; GENE THERAPY; GENETIC DISEASES, INBORN; GENETIC VECTORS; HUMANS; MALE;

EID: 33644815296     PISSN: 00313998     EISSN: None     Source Type: Journal    
DOI: 10.1203/01.pdr.0000189226.03684.fe     Document Type: Review

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