메뉴 건너뛰기




Volumn 189, Issue 4, 2005, Pages 697-714

The possible place of autologus cell therapy in facioscapulohumeral muscular dystrophy;Peut-on envisager une thérapie cellulaire autologue de la dystrophie musculaire facio-scapulo-humérale?

Author keywords

Biological therapy; Cell differenciation; Muscular dystrophies

Indexed keywords


EID: 25144523092     PISSN: 00014079     EISSN: None     Source Type: Journal    
DOI: 10.1016/s0001-4079(19)33546-0     Document Type: Article
Times cited : (2)

References (39)
  • 2
    • 1542750032 scopus 로고    scopus 로고
    • Facioscapulohumeral Muscular Dystrophy
    • TAWIL R. - Facioscapulohumeral Muscular Dystrophy. Curr. Neurol. Neurosci. Reports 2004, 4, 51-54.
    • (2004) Curr. Neurol. Neurosci. Reports , vol.4 , pp. 51-54
    • Tawil, R.1
  • 4
    • 7344231685 scopus 로고    scopus 로고
    • Inter and intrachromosomal subtelomeric rearrangements on 4q35: Implications for facioscapulohumeral muscular dystrophy (FSHD) etiology an ddiagnosis
    • LEMMERS RJ., VAN DER MAAREL S., VAN DEUKETOM JC., VAN DER WIELEN MJ., DEIDDA G., DAUWERSE HG. et al. - Inter and intrachromosomal subtelomeric rearrangements on 4q35 : implications for facioscapulohumeral muscular dystrophy (FSHD) etiology an ddiagnosis. Hum. Mol. Genet., 1998, 7, 1207-1214.
    • (1998) Hum. Mol. Genet. , vol.7 , pp. 1207-1214
    • Lemmers, R.J.1    Van Der Maarel, S.2    Van Deuketom, J.C.3    Van Der Wielen, M.J.4    Deidda, G.5    Dauwerse, H.G.6
  • 5
    • 0029984970 scopus 로고    scopus 로고
    • Evidence for anticipation: An association of deletion size with severity in facioscapulohumeral muscular dystrophy
    • TAWIL R., FORRESTER J., GRIGGS RC., MENDELL JR., KISSEL J., MCDERMOTT MP. et al. - Evidence for anticipation : an association of deletion size with severity in facioscapulohumeral muscular dystrophy. Ann. Neurol., 1996, 39, 744-748.
    • (1996) Ann. Neurol. , vol.39 , pp. 744-748
    • Tawil, R.1    Forrester, J.2    Griggs, R.C.3    Mendell, J.R.4    Kissel, J.5    Mcdermott, M.P.6
  • 6
    • 0037047439 scopus 로고    scopus 로고
    • Inappropriate gene activation in FSHD: A repressor complex binds a chromosomal repeat deleted in dystrophic muscle
    • GABELLINI D., GREEN MR., TUPLER R. - Inappropriate gene activation in FSHD : a repressor complex binds a chromosomal repeat deleted in dystrophic muscle. Cell., 2002, 110, 339-348.
    • (2002) Cell. , vol.110 , pp. 339-348
    • Gabellini, D.1    Green, M.R.2    Tupler, R.3
  • 7
    • 1642377315 scopus 로고    scopus 로고
    • Molecular basis of facioscapulohumeral dystrophy
    • TUPLER R., GABELLINI D. - Molecular basis of facioscapulohumeral dystrophy. Cell. Mol. Life Sci., 2004, 61, 557-566.
    • (2004) Cell. Mol. Life Sci. , vol.61 , pp. 557-566
    • Tupler, R.1    Gabellini, D.2
  • 8
    • 0000642664 scopus 로고
    • Satellite cell of skeletal muscle fibres
    • MAURO A. - Satellite cell of skeletal muscle fibres J. Biophys. Biochem. Cytol., 1961, 9, 493-495.
    • (1961) J. Biophys. Biochem. Cytol. , vol.9 , pp. 493-495
    • Mauro, A.1
  • 9
    • 0021889692 scopus 로고
    • Myoblast senescence in muscular dystrophy
    • WRIGHT WE. - Myoblast senescence in muscular dystrophy. Exp. Cell. Res., 1985, 157, 343-354.
    • (1985) Exp. Cell. Res. , vol.157 , pp. 343-354
    • Wright, W.E.1
  • 10
    • 84861249764 scopus 로고    scopus 로고
    • Procédé d'obtention de populations cellulaires d'origine musculaire et utilisations
    • (007304) déposé en France le 7 Juin 2000 et aux USA le 16 Octobre 2000 sous l'égide de l'AP-HP, l'INSERM et l'AFM
    • VILQUIN JT., MAROLLEAU JP., TREMBLAY JP., ROBERT I., TERNAUX B. - Procédé d'obtention de populations cellulaires d'origine musculaire et utilisations. Brevet (007304) déposé en France le 7 Juin 2000 et aux USA le 16 Octobre 2000 sous l'égide de l'AP-HP, l'INSERM et l'AFM.
    • Brevet
    • Vilquin, J.T.1    Marolleau, J.P.2    Tremblay, J.P.3    Robert, I.4    Ternaux, B.5
  • 11
  • 12
    • 0023818351 scopus 로고
    • Isolation of human myoblasts with the fluorescent- Activated cell sorter
    • WEBSTER C., PAVLATH GK., PARKS DR., WALSH FS., BLAU HM. - Isolation of human myoblasts with the fluorescent- activated cell sorter. Exp. Cell Res., 1988, 174, 252-265.
    • (1988) Exp. Cell Res. , vol.174 , pp. 252-265
    • Webster, C.1    Pavlath, G.K.2    Parks, D.R.3    Walsh, F.S.4    Blau, H.M.5
  • 18
  • 19
    • 0031031974 scopus 로고    scopus 로고
    • A pilot trial of prednisone in facioscapulohumeral muscular dystrophy
    • TAWIL R., MCDERMOTT MP., PANDYA S., KISSEL J., GRIGGS RC., and the FSHD-DY Group. - A pilot trial of prednisone in facioscapulohumeral muscular dystrophy. Neurology, 1997, 48, 46-49.
    • (1997) Neurology , vol.48 , pp. 46-49
    • Tawil, R.1    Mcdermott, M.P.2    Pandya, S.3    Kissel, J.4    Griggs, R.C.5
  • 20
    • 0343022262 scopus 로고    scopus 로고
    • Creatine monohydrate in muscular dystrophies: A double blind placebo controlled clinical study
    • WALTER MC., LOCHMULLER H., REILICH P., KLOPSTOCK T., HUBERT R., HARTARD M. et al. - Creatine monohydrate in muscular dystrophies : a double blind placebo controlled clinical study. Neurology, 2000, 54, 1848-1850.
    • (2000) Neurology , vol.54 , pp. 1848-1850
    • Walter, M.C.1    Lochmuller, H.2    Reilich, P.3    Klopstock, T.4    Hubert, R.5    Hartard, M.6
  • 22
    • 10244267483 scopus 로고    scopus 로고
    • Hematopoietic stem cell transplantation does not restore dystrophin expression in Duchenne Muscular Dystrophy dogs
    • DELL'AGNOLA C., WANG Z., STORB R., TAPSCOTT SJ., KUHR CS., HAUSCHKA SD. et al. - Hematopoietic stem cell transplantation does not restore dystrophin expression in Duchenne Muscular Dystrophy dogs. Blood, 2004, 182, 4311-4318.
    • (2004) Blood , vol.182 , pp. 4311-4318
    • Dell'agnola, C.1    Wang, Z.2    Storb, R.3    Tapscott, S.J.4    Kuhr, C.S.5    Hauschka, S.D.6
  • 23
    • 85047690272 scopus 로고    scopus 로고
    • Fusion of bone marrow derived stem cells with striated muscle may not be sufficient to activate gene expression
    • COSSU G. - Fusion of bone marrow derived stem cells with striated muscle may not be sufficient to activate gene expression. J. Clin. Invest., 2004, 114, 1540-1543.
    • (2004) J. Clin. Invest. , vol.114 , pp. 1540-1543
    • Cossu, G.1
  • 24
    • 0024540879 scopus 로고
    • Conversion of mdx myofibres from dystrophin-negative to dystrophine-positive by injection of normal myoblasts
    • PARTRIDGE TA., MORGAN JE., COULTON GR., HOFFMAN EP., KUNKEL LM. - Conversion of mdx myofibres from dystrophin-negative to dystrophine-positive by injection of normal myoblasts, Nature, 1989, 337, 176-179.
    • (1989) Nature , vol.337 , pp. 176-179
    • Partridge, T.A.1    Morgan, J.E.2    Coulton, G.R.3    Hoffman, E.P.4    Kunkel, L.M.5
  • 25
    • 0028295454 scopus 로고
    • High efficiency of muscle regeneration after human myoblats clone transplantation in SCID mice
    • HUARD J., VERRAULT S., ROY R., TREMBLAY M., TREMBLAY JP. - High efficiency of muscle regeneration after human myoblats clone transplantation in SCID mice. J. Clin. Invest, 1994, 93, 586-599.
    • (1994) J. Clin. Invest. , vol.93 , pp. 586-599
    • Huard, J.1    Verrault, S.2    Roy, R.3    Tremblay, M.4    Tremblay, J.P.5
  • 28
    • 0026560260 scopus 로고
    • Normal dystrophin transcripts detected in Duchenne musculare dystrophy patients after myoblats transplantation
    • GUSSONI E., PAVLATH GK., LANCTOT AM., SHARLA KR., MILLER RG. et al. - Normal dystrophin transcripts detected in Duchenne musculare dystrophy patients after myoblats transplantation. Nature, 1992, 356, 435-438.
    • (1992) Nature , vol.356 , pp. 435-438
    • Gussoni, E.1    Pavlath, G.K.2    Lanctot, A.M.3    Sharla, K.R.4    Miller, R.G.5
  • 32
    • 0037414086 scopus 로고    scopus 로고
    • Autologous skeletal myoblast transplantation for sever post infarction left ventriular dysfunction
    • MENASCHÉ P., HAGEGE AA., VILQUIN JT., DESNOS M., ABERGEL E., POUZET B., et al. - Autologous skeletal myoblast transplantation for sever post infarction left ventriular dysfunction. J. Am. Coll. Cardiol., 2003, 41, 1078-1083.
    • (2003) J. Am. Coll. Cardiol. , vol.41 , pp. 1078-1083
    • Menasché, P.1    Hagege, A.A.2    Vilquin, J.T.3    Desnos, M.4    Abergel, E.5    Pouzet, B.6
  • 33
    • 0025646136 scopus 로고    scopus 로고
    • Accelerated age-related decline in replicative life-span of Duchenne muscular dystrophy myoblasts: Implications for cell and gene therapy
    • WESBSTER C., BLAU HM. - Accelerated age-related decline in replicative life-span of Duchenne muscular dystrophy myoblasts : implications for cell and gene therapy. Somat. Cell Mol. Genet., 16, 557-565.
    • Somat. Cell Mol. Genet. , vol.16 , pp. 557-565
    • Wesbster, C.1    Blau, H.M.2
  • 34
    • 0032827422 scopus 로고    scopus 로고
    • Transplantation of human myoblasts in SCID mice as a potential muscular model of myotonic dystrophy
    • SKUK D., FURLING D., BOUCHARD JP., GOULET M., ROY B., LACROIX Y., et al. - Transplantation of human myoblasts in SCID mice as a potential muscular model of myotonic dystrophy. Neuropathol. Exp. Neurol., 1999, 58, 921-931.
    • (1999) Neuropathol. Exp. Neurol. , vol.58 , pp. 921-931
    • Skuk, D.1    Furling, D.2    Bouchard, J.P.3    Goulet, M.4    Roy, B.5    Lacroix, Y.6
  • 35
    • 0043095483 scopus 로고    scopus 로고
    • Facioscapulohumeral dystrophy (FSHD) myoblasts demontrate increased susceptibility to oxidative stress
    • WINOKUR ST., BARRETT K., MARTIN JH., FORRESTER JR., SIMON M., TAWIL R. et al. - Facioscapulohumeral dystrophy (FSHD) myoblasts demontrate increased susceptibility to oxidative stress. Neuromusc. Disorders, 2003, 13, 322-333.
    • (2003) Neuromusc. Disorders , vol.13 , pp. 322-333
    • Winokur, S.T.1    Barrett, K.2    Martin, J.H.3    Forrester, J.R.4    Simon, M.5    Tawil, R.6
  • 36
    • 0034739841 scopus 로고    scopus 로고
    • Loss of calpain3 proteolytic activity leads to muscular dystrophy and to apoptosis-associated κβα/nuclear factor kappaβ pathway perturbation in mice
    • RICHARD I., ROUDAUT C., MARCHAND S., BAGHDIGUIAN, HERASSE M., STOCKHOLM D. et al. - Loss of calpain3 proteolytic activity leads to muscular dystrophy and to apoptosis-associated κβα/nuclear factor kappaβ pathway perturbation in mice. J. Cell. Biol., 2000, 151, 1583-1590.
    • (2000) J. Cell. Biol. , vol.151 , pp. 1583-1590
    • Richard, I.1    Roudaut, C.2    Marchand, S.3    Baghdiguian4    Herasse, M.5    Stockholm, D.6
  • 37
    • 10344223978 scopus 로고    scopus 로고
    • Myoblast transplantation for inherited myopathie: A clinical approach
    • SKUK D. - Myoblast transplantation for inherited myopathie : a clinical approach. Expert Opin. Biol. Ther., 2004, 4, 1871-1885.
    • (2004) Expert Opin. Biol. Ther. , vol.4 , pp. 1871-1885
    • Skuk, D.1
  • 38
    • 12144289797 scopus 로고    scopus 로고
    • Dystrophin expression of myofibers of Duchenne muscular dystrophy patients following intra muscular injections of normal myogenic cells
    • SKUK D., ROY B., GOULET A., CHAPDELAINE P., BOUCHARD JP., ROY R. et al. - Dystrophin expression of myofibers of Duchenne muscular dystrophy patients following intra muscular injections of normal myogenic cells. Mol. Ther., 2004, 9, 475-482.
    • (2004) Mol. Ther. , vol.9 , pp. 475-482
    • Skuk, D.1    Roy, B.2    Goulet, A.3    Chapdelaine, P.4    Bouchard, J.P.5    Roy, R.6
  • 39
    • 0036255397 scopus 로고    scopus 로고
    • Efficacy of myoblast transplantation in whole muscle of non-human primates following simple intramuscular injections: Toward defining strategies applicable to humans
    • SKUK D., GOULET M., ROY B., TREMBLAY JP. - Efficacy of myoblast transplantation in whole muscle of non-human primates following simple intramuscular injections : toward defining strategies applicable to humans Exp. Neurol., 2002, 175, 112-126.
    • (2002) Exp. Neurol. , vol.175 , pp. 112-126
    • Skuk, D.1    Goulet, M.2    Roy, B.3    Tremblay, J.P.4


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.