The 'pro-sense' approach to Duchenne muscular dystrophy

European Journal of Human Genetics

Volumn 13, Issue 5, 2005, Pages 518-519

  van Deutekom, Judith C T ^a  

^a LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

Author keywords

[No Author keywords available]

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; DRUG CARRIER; DYSTROPHIN; F 127; MESSENGER RNA; NUCLEASE; PARVOVIRUS VECTOR; POLOXAMER; RIBONUCLEASE H; SMALL NUCLEAR RIBONUCLEOPROTEIN; UNCLASSIFIED DRUG; SMALL NUCLEAR RNA;

3' UNTRANSLATED REGION; 5' UNTRANSLATED REGION; ADENO ASSOCIATED VIRUS; BECKER MUSCULAR DYSTROPHY; CELL REGENERATION; CHEMICAL MODIFICATION; DETERIORATION; DISEASE COURSE; DISEASE SEVERITY; DUCHENNE MUSCULAR DYSTROPHY; ENHANCER REGION; EXON; FRAMESHIFT MUTATION; GENE MUTATION; GENE THERAPY; HUMAN; MOUSE STRAIN; MUSCLE CELL; MUSCLE CONTRACTILITY; MUSCLE FUNCTION; MUSCLE POTENTIAL; MUTAGENESIS; NONHUMAN; NOTE; NUCLEOTIDE SEQUENCE; OPEN READING FRAME; PLASMID; PRIORITY JOURNAL; PROTEIN ANALYSIS; PROTEIN DEFICIENCY; PROTEIN EXPRESSION; PROTEIN LOCALIZATION; RISK FACTOR; RNA SPLICING; ANIMAL; ARTICLE; BIOSYNTHESIS; GENE REPRESSION; GENETICS; MOUSE;

ADENO-ASSOCIATED VIRUS; PARVOVIRUS;

ANIMALS; DYSTROPHIN; EXONS; GENE THERAPY; HUMANS; MICE; MUSCULAR DYSTROPHY, DUCHENNE; OLIGORIBONUCLEOTIDES, ANTISENSE; RNA, SMALL NUCLEAR; SUPPRESSION, GENETIC;

EID: 18844442551     PISSN: 10184813     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.ejhg.5201381     Document Type: Note

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