New hope for gene therapy of β-thalassemia

Emirates Medical Journal

Volumn 20, Issue 2, 2002, Pages 121-124

  Sadelain, Michel ^a  

^a MEMORIAL SLOAN KETTERING CANCER CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA GLOBIN; BETA GLOBIN; DEFEROXAMINE; ERYTHROPOIETIN; HEMOGLOBIN; HEMOGLOBIN F; IRON; IRON CHELATING AGENT; VIRUS VECTOR;

APOPTOSIS; AUTOLOGOUS BONE MARROW TRANSPLANTATION; BETA THALASSEMIA; BLOOD TRANSFUSION; CELL DAMAGE; CELL MATURATION; CHROMOSOME POSITIONING; ERYTHROPOIESIS; EXTRAMEDULLARY HEMATOPOIESIS; GASTROINTESTINAL ABSORPTION; GENE CONTROL; GENE EXPRESSION; GENE FREQUENCY; GENE FUNCTION; GENE MUTATION; GENE THERAPY; GENE TRANSFER; GENETIC TRANSCRIPTION; GLOBIN GENE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMOLYSIS; HEMOLYTIC ANEMIA; IRON OVERLOAD; MONOGENIC DISORDER; NONHUMAN; REGULATOR GENE; REVIEW; SKELETON MALFORMATION; SPLENECTOMY; SPLENOMEGALY;

EID: 0347865992     PISSN: 02506882     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Review

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