메뉴 건너뛰기




Volumn 31, Issue 11, 2003, Pages 1112-1118

Donor cell expansion is delayed following nonablative in utero transplantation to treat murine mucopolysaccharidosis type VII

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLUCURONIDASE; GLYCOSAMINOGLYCAN;

EID: 0142258090     PISSN: 0301472X     EISSN: None     Source Type: Journal    
DOI: 10.1016/S0301-472X(03)00234-0     Document Type: Article
Times cited : (2)

References (28)
  • 1
    • 0029848406 scopus 로고    scopus 로고
    • Treatment of X-linked severe combined immunodeficiency by in utero transplantation of paternal bone marrow
    • Flake A.W., Roncarolo M.G., Puck J.M., et al. Treatment of X-linked severe combined immunodeficiency by in utero transplantation of paternal bone marrow. N Engl J Med. 335:1996;1806-1810.
    • (1996) N Engl J Med , vol.335 , pp. 1806-1810
    • Flake, A.W.1    Roncarolo, M.G.2    Puck, J.M.3
  • 2
    • 16144362330 scopus 로고    scopus 로고
    • In-utero transplantation of parental CD34 haematopoietic progenitor cells in a patient with X-linked severe combined immunodeficiency (SCIDXI)
    • Wengler G.S., Lanfranchi A., Frusca T., et al. In-utero transplantation of parental CD34 haematopoietic progenitor cells in a patient with X-linked severe combined immunodeficiency (SCIDXI). Lancet. 348:1996;1484-1487.
    • (1996) Lancet , vol.348 , pp. 1484-1487
    • Wengler, G.S.1    Lanfranchi, A.2    Frusca, T.3
  • 3
    • 0033018253 scopus 로고    scopus 로고
    • Stem cell transplants in utero for genetic diseases: Treatment and a model for induction of immunologic tolerance
    • Touraine J.L., Raudrant D., Laplace S., Gebuhrer L. Stem cell transplants in utero for genetic diseases: treatment and a model for induction of immunologic tolerance. Transplant Proc. 31:1999;681-682.
    • (1999) Transplant Proc , vol.31 , pp. 681-682
    • Touraine, J.L.1    Raudrant, D.2    Laplace, S.3    Gebuhrer, L.4
  • 4
    • 0036323491 scopus 로고    scopus 로고
    • Fetal hematopoietic stem cell transplantation: A challenge for the twenty-first century
    • Shields L.E., Lindton B., Andrews R.G., Westgren M. Fetal hematopoietic stem cell transplantation: a challenge for the twenty-first century. J Hematother Stem Cell Res. 11:2002;616-631.
    • (2002) J Hematother Stem Cell Res , vol.11 , pp. 616-631
    • Shields, L.E.1    Lindton, B.2    Andrews, R.G.3    Westgren, M.4
  • 5
    • 0028825086 scopus 로고
    • In utero transfer of adult bone marrow cells into recipients with severe combined immunodeficiency disorder yields lymphoid progeny with T- and B-cell functional capabilities
    • Blazar B.R., Taylor P.A., Vallera D.A. In utero transfer of adult bone marrow cells into recipients with severe combined immunodeficiency disorder yields lymphoid progeny with T- and B-cell functional capabilities. Blood. 86:1995;4353-4366.
    • (1995) Blood , vol.86 , pp. 4353-4366
    • Blazar, B.R.1    Taylor, P.A.2    Vallera, D.A.3
  • 6
    • 0035958110 scopus 로고    scopus 로고
    • Postnatal cytokines and boosts improve chimerism and hematological parameters in beta-thalassemic mice transplanted in utero
    • Donahue J., Gilpin E., Young D., Carrier E. Postnatal cytokines and boosts improve chimerism and hematological parameters in beta-thalassemic mice transplanted in utero. Transplantation. 71:2001;1491-1494.
    • (2001) Transplantation , vol.71 , pp. 1491-1494
    • Donahue, J.1    Gilpin, E.2    Young, D.3    Carrier, E.4
  • 7
    • 0035869531 scopus 로고    scopus 로고
    • In utero transplantation of fetal liver cells in the mucopolysaccharidosis type VII mouse results in low-level chimerism, but overexpression of β-glucuronidase can delay onset of clinical signs
    • Casal M.L., Wolfe J.H. In utero transplantation of fetal liver cells in the mucopolysaccharidosis type VII mouse results in low-level chimerism, but overexpression of β-glucuronidase can delay onset of clinical signs. Blood. 97:2001;1625-1634.
    • (2001) Blood , vol.97 , pp. 1625-1634
    • Casal, M.L.1    Wolfe, J.H.2
  • 8
    • 0021327109 scopus 로고
    • Development of adult bone marrow stem cells in H-2-compatible and -incompatible mouse fetuses
    • Fleischman R.A., Mintz B. Development of adult bone marrow stem cells in H-2-compatible and -incompatible mouse fetuses. J Exp Med. 159:1984;731-745.
    • (1984) J Exp Med , vol.159 , pp. 731-745
    • Fleischman, R.A.1    Mintz, B.2
  • 9
    • 0345624487 scopus 로고    scopus 로고
    • A kinetic model for the homing and migration of prenatally transplanted marrow
    • Shaaban A.F., Kim H.B., Milner R., Flake A.W. A kinetic model for the homing and migration of prenatally transplanted marrow. Blood. 94:1999;3251-3257.
    • (1999) Blood , vol.94 , pp. 3251-3257
    • Shaaban, A.F.1    Kim, H.B.2    Milner, R.3    Flake, A.W.4
  • 10
    • 0027451062 scopus 로고
    • In utero engraftment of fully H-2-incompatible versus congenic adult bone marrow transferred into nonanemic or anemic murine fetal recipients
    • Howson-Jan K., Matloub Y.H., Vallera D.A., Blazar B.R. In utero engraftment of fully H-2-incompatible versus congenic adult bone marrow transferred into nonanemic or anemic murine fetal recipients. Transplantation. 56:1993;709-716.
    • (1993) Transplantation , vol.56 , pp. 709-716
    • Howson-Jan, K.1    Matloub, Y.H.2    Vallera, D.A.3    Blazar, B.R.4
  • 11
  • 12
    • 0035207085 scopus 로고    scopus 로고
    • In utero fetal liver cell transplantation without toxic irradiation alleviates lysosomal storage in mucopolysaccharidosis type VII
    • Barker J.E., Deveau S., Lessard M., Hamblen N., Vogler C., Levy B. In utero fetal liver cell transplantation without toxic irradiation alleviates lysosomal storage in mucopolysaccharidosis type VII. Blood Cells Mol Dis. 27:2001;861-873.
    • (2001) Blood Cells Mol Dis , vol.27 , pp. 861-873
    • Barker, J.E.1    Deveau, S.2    Lessard, M.3    Hamblen, N.4    Vogler, C.5    Levy, B.6
  • 13
    • 0028928897 scopus 로고
    • Adult bone marrow-derived pluripotent hematopoietic stem cells are engraftable when transferred in utero into moderately anemic fetal recipients
    • Blazar B.R., Taylor P.A., Vallera D.A. Adult bone marrow-derived pluripotent hematopoietic stem cells are engraftable when transferred in utero into moderately anemic fetal recipients. Blood. 85:1995;833-841.
    • (1995) Blood , vol.85 , pp. 833-841
    • Blazar, B.R.1    Taylor, P.A.2    Vallera, D.A.3
  • 14
    • 0027492416 scopus 로고
    • Liver-derived fetal hematopoietic stem cells selectively and preferentially home to the fetal bone marrow
    • Zanjani E.D., Ascensao J.L., Tavassoli M. Liver-derived fetal hematopoietic stem cells selectively and preferentially home to the fetal bone marrow. Blood. 81:1993;399-404.
    • (1993) Blood , vol.81 , pp. 399-404
    • Zanjani, E.D.1    Ascensao, J.L.2    Tavassoli, M.3
  • 15
    • 0030038665 scopus 로고    scopus 로고
    • Long term engraftment following in utero T cell-depleted parental marrow transplantation into fetal rhesus monkeys
    • Cowan M.J., Tarantal A.F., Capper J., Harrison M., Garovoy M. Long term engraftment following in utero T cell-depleted parental marrow transplantation into fetal rhesus monkeys. Bone Marrow Transplant. 17:1996;1156-1165.
    • (1996) Bone Marrow Transplant , vol.17 , pp. 1156-1165
    • Cowan, M.J.1    Tarantal, A.F.2    Capper, J.3    Harrison, M.4    Garovoy, M.5
  • 16
    • 0036682932 scopus 로고    scopus 로고
    • Complete allogeneic hematopoietic chimerism achieved by a combined strategy of in utero hematopoietic stem cell transplantation and postnatal donor lymphocyte infusion
    • Hayashi S., Peranteau W.H., Shaaban A.F., Flake A.W. Complete allogeneic hematopoietic chimerism achieved by a combined strategy of in utero hematopoietic stem cell transplantation and postnatal donor lymphocyte infusion. Blood. 100:2002;804-812.
    • (2002) Blood , vol.100 , pp. 804-812
    • Hayashi, S.1    Peranteau, W.H.2    Shaaban, A.F.3    Flake, A.W.4
  • 17
    • 0035283136 scopus 로고    scopus 로고
    • Non-ablative neonatal marrow transplantation attenuates functional and physical defects of β-glucuronidase deficiency
    • Soper B.W., Lessard M.D., Vogler C.A., et al. Non-ablative neonatal marrow transplantation attenuates functional and physical defects of β-glucuronidase deficiency. Blood. 97:2001;1498-1504.
    • (2001) Blood , vol.97 , pp. 1498-1504
    • Soper, B.W.1    Lessard, M.D.2    Vogler, C.A.3
  • 18
    • 0001351056 scopus 로고    scopus 로고
    • Murine mucopolysaccharidosis type VII: A model system for somatic gene therapy of the central nervous system
    • P.R. Lowenstein, & L.W. Enquist. Chichester: Wiley
    • Wolfe J.H., Sands M.S. Murine mucopolysaccharidosis type VII: a model system for somatic gene therapy of the central nervous system. Lowenstein P.R., Enquist L.W. Protocols for Gene Transfer in Neurological Disorders. 1996;263-274 Wiley, Chichester.
    • (1996) Protocols for Gene Transfer in Neurological Disorders , pp. 263-274
    • Wolfe, J.H.1    Sands, M.S.2
  • 19
    • 0025139019 scopus 로고
    • A murine model of mucopolysaccharidosis VII: Gross and microscopic findings in beta-glucuronidase-deficient mice
    • Vogler C., Birkenmeier E.H., Sly W.S., et al. A murine model of mucopolysaccharidosis VII: gross and microscopic findings in beta-glucuronidase-deficient mice. Am J Pathol. 136:1990;206-217.
    • (1990) Am J Pathol , vol.136 , pp. 206-217
    • Vogler, C.1    Birkenmeier, E.H.2    Sly, W.S.3
  • 20
    • 0025719951 scopus 로고
    • Increased life span and correction of metabolic defects in murine mucopolysaccharidosis type VII after syngeneic bone marrow transplantation
    • Birkenmeier E.H., Barker J.E., Vogler C.A., et al. Increased life span and correction of metabolic defects in murine mucopolysaccharidosis type VII after syngeneic bone marrow transplantation. Blood. 78:1991;3081-3092.
    • (1991) Blood , vol.78 , pp. 3081-3092
    • Birkenmeier, E.H.1    Barker, J.E.2    Vogler, C.A.3
  • 21
    • 0032699530 scopus 로고    scopus 로고
    • A genetically myeloablated MPS VII model detects the expansion and curative properties of as few as 100 enriched murine stem cells
    • Soper B.W., Duffy T.M., Vogler C.A., Barker J.E. A genetically myeloablated MPS VII model detects the expansion and curative properties of as few as 100 enriched murine stem cells. Exp Hematol. 27:1999;1691-1704.
    • (1999) Exp Hematol , vol.27 , pp. 1691-1704
    • Soper, B.W.1    Duffy, T.M.2    Vogler, C.A.3    Barker, J.E.4
  • 22
    • 15844397404 scopus 로고    scopus 로고
    • Persistence of mixed chimerism in patients transplanted for the treatment of thalassemia
    • Andreani M., Manna M., Lucarelli G., et al. Persistence of mixed chimerism in patients transplanted for the treatment of thalassemia. Blood. 87:1996;3494-3499.
    • (1996) Blood , vol.87 , pp. 3494-3499
    • Andreani, M.1    Manna, M.2    Lucarelli, G.3
  • 23
    • 0035874519 scopus 로고    scopus 로고
    • Functional requirements for phenotypic correction of murine beta-thalassemia: Implications for human gene therapy
    • Persons D.A., Allay E.R., Sabatino D.E., Kelly P., Bodine D.M., Nienhuis A.W. Functional requirements for phenotypic correction of murine beta-thalassemia: implications for human gene therapy. Blood. 97:2001;3275-3282.
    • (2001) Blood , vol.97 , pp. 3275-3282
    • Persons, D.A.1    Allay, E.R.2    Sabatino, D.E.3    Kelly, P.4    Bodine, D.M.5    Nienhuis, A.W.6
  • 24
    • 0027051181 scopus 로고
    • Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer
    • Wolfe J., Sands M.S., Barker J.E., et al. Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer. Nature. 360:1992;749-753.
    • (1992) Nature , vol.360 , pp. 749-753
    • Wolfe, J.1    Sands, M.S.2    Barker, J.E.3
  • 25
    • 0033010571 scopus 로고    scopus 로고
    • Enzyme replacement in murine mucopolysaccharidosis type VII: Neuronal and glial response to beta glucuronidase requires early initiation of enzyme replacement therapy
    • Vogler C., Levy B., Galvin N.J., et al. Enzyme replacement in murine mucopolysaccharidosis type VII: neuronal and glial response to beta glucuronidase requires early initiation of enzyme replacement therapy. Pediatr Res. 45:1999;838-844.
    • (1999) Pediatr Res , vol.45 , pp. 838-844
    • Vogler, C.1    Levy, B.2    Galvin, N.J.3
  • 26
    • 0037369266 scopus 로고    scopus 로고
    • Engraftment of human CD34+ cells leads to widespread distribution of donor-derived cells and correction of tissue pathology in a novel murine xenotransplantation model of lysosomal storage disease
    • Hoskins A.A., Vogler C., Creer M.H., Sands M.S. Engraftment of human CD34+ cells leads to widespread distribution of donor-derived cells and correction of tissue pathology in a novel murine xenotransplantation model of lysosomal storage disease. Blood. 101:2003;2054-2063.
    • (2003) Blood , vol.101 , pp. 2054-2063
    • Hoskins, A.A.1    Vogler, C.2    Creer, M.H.3    Sands, M.S.4
  • 27
    • 0032954637 scopus 로고    scopus 로고
    • Multiple high cell dose injections of normal marrow into newborn jaundiced mice dramatically prolong life despite transient repopulation
    • Barker J.E., Kaysser-Kranich T.M., Hamblen N., Deveau S. Multiple high cell dose injections of normal marrow into newborn jaundiced mice dramatically prolong life despite transient repopulation. Exp Hematol. 27:1999;966-971.
    • (1999) Exp Hematol , vol.27 , pp. 966-971
    • Barker, J.E.1    Kaysser-Kranich, T.M.2    Hamblen, N.3    Deveau, S.4
  • 28
    • 0037105589 scopus 로고    scopus 로고
    • High-level allogeneic chimerism achieved by prenatal tolerance induction and postnatal nonmyeloablative bone marrow transplantation
    • Peranteau W.H., Hayashi S., Hsieh M., Shaaban A.F., Flake A.W. High-level allogeneic chimerism achieved by prenatal tolerance induction and postnatal nonmyeloablative bone marrow transplantation. Blood. 100:2002;2225-2234.
    • (2002) Blood , vol.100 , pp. 2225-2234
    • Peranteau, W.H.1    Hayashi, S.2    Hsieh, M.3    Shaaban, A.F.4    Flake, A.W.5


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.