In utero fetal liver cell transplantation without toxic irradiation alleviates lysosomal storage in mice with mucopolysaccharidosis type VII

Blood Cells, Molecules, and Diseases

Volumn 27, Issue 5, 2001, Pages 861-873

  Barker, Jane E ^a   Deveau, Sue ^a   Lessard, Mark ^a   Hamblen, Nancy ^a   Vogler, Carole ^b   Levy, Beth ^b  

^a JACKSON LABORATORY   (United States)

^b Saint Louis Medical Center   (United States)

Author keywords

Fetal liver cells; Lysosomal storage; MPS VII; Myeloablation; Transplantation

Indexed keywords

BETA GLUCURONIDASE;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; BLOOD BRAIN BARRIER; BONE DYSPLASIA; BONE MARROW CELL; CELL TRANSPLANTATION; CONTROLLED STUDY; ENZYME DEFECT; FATALITY; FETUS; FETUS LIVER; HEMATOPOIETIC CELL; INTELLECTUAL IMPAIRMENT; LEPTOMENINX; LIFESPAN; LONG TERM CARE; LYSOSOME STORAGE DISEASE; MOBILIZATION; MOUSE; MUCOPOLYSACCHARIDOSIS TYPE 7; NONHUMAN; PRIORITY JOURNAL; QUALITY OF LIFE; RADIATION DOSE; ANIMAL; BRAIN; DISEASE MODEL; EMBRYOLOGY; FETAL TISSUE TRANSPLANTATION; FETUS DISEASE; GENETICS; LIVER; METHODOLOGY; MOUSE MUTANT; PATHOLOGY; STEM CELL TRANSPLANTATION;

MURINAE;

ANIMAL; BLOOD-BRAIN BARRIER; BRAIN; DISEASE MODELS, ANIMAL; FETAL DISEASES; FETAL TISSUE TRANSPLANTATION; FETUS; LIVER; LYSOSOMAL STORAGE DISEASES; MICE; MICE, KNOCKOUT; MUCOPOLYSACCHARIDOSIS VII; RADIATION DOSAGE; STEM CELL TRANSPLANTATION; SUPPORT, U.S. GOV'T, P.H.S.;

EID: 0035207085     PISSN: 10799796     EISSN: None     Source Type: Journal    
DOI: 10.1006/bcmd.2001.0453     Document Type: Article

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