Herpes simplex virus type 1 amplicon vector-mediated gene transfer to muscle

Human Gene Therapy

Volumn 13, Issue 2, 2002, Pages 261-273

  Wang, Yaming ^a   Mukherjee, Santwana ^a   Fraefel, Cornel ^b   Breakefield, Xandra O ^c   Allen, Paul D ^a  

^a BRIGHAM AND WOMEN S HOSPITAL   (United States)

^b UNIVERSITY OF ZURICH   (Switzerland)

^c MASSACHUSETTS GENERAL HOSPITAL   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; CREATINE KINASE; DYSTROPHIN; GREEN FLUORESCENT PROTEIN;

AMPLICON; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL TISSUE; ANTIGENICITY; ARTICLE; CELL CULTURE; CONTROLLED STUDY; CYTOTOXICITY; DNA VECTOR; DUCHENNE MUSCULAR DYSTROPHY; ENHANCER REGION; GENE EXPRESSION; GENE TRANSFER; HERPES SIMPLEX VIRUS 1; HUMAN; HUMAN CELL; IMMUNOCYTOCHEMISTRY; IMMUNOGENICITY; IMMUNOHISTOCHEMISTRY; LYMPHOCYTIC INFILTRATION; MOLECULAR SIZE; MOUSE; MUSCLE CELL; MYOBLAST; MYOTUBE; NEWBORN; NONHUMAN; PROMOTER REGION; PROTEIN EXPRESSION; SPECIES DIFFERENCE; SUPERINFECTION; T LYMPHOCYTE; TIBIALIS ANTERIOR MUSCLE; TRANSGENE;

ANIMALS; CREATINE KINASE; CYTOMEGALOVIRUS; DYSTROPHIN; FEASIBILITY STUDIES; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; GREEN FLUORESCENT PROTEINS; HERPESVIRUS 1, HUMAN; HUMANS; LUMINESCENT PROTEINS; MICE; MICE, INBRED C57BL; MUSCLES; PROMOTER REGIONS (GENETICS);

ANIMALIA; DNA VIRUSES; HUMAN HERPESVIRUS 1; MURINAE; SIMPLEXVIRUS;

EID: 0036173625     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/10430340252769789     Document Type: Article

References (77)

1. Human dystrophin expression in mdx mice after intramuscular injection of DNA constructs
2. Cultured human myoblasts and myotubes show markedly different transducibility by replication-defective adenovirus recombinants
3. A differential efficiency of adenovirus-mediated in vivo gene transfer into skeletal muscle cells of different maturity
4. The structural and functional diversity of dystrophin
5. Gene transfer into muscle by electroporation in vivo
6. Herpes simplex virus vector-mediated dystrophin gene transfer and expression in MDX mouse skeletal muscle
7. The subcellular distribution of dystrophin in mouse skeletal, cardiac, and smooth muscle
8. Efficient gene transfer to human squamous cell carcinomas by the herpes simplex virus type 1 amplicon vector
9. Persistence in muscle of an adenoviral vector that lacks all viral genes
10. Gene transfer to the nigrostriatal system by hybrid herpes simplex virus/adeno-associated virus amplicon vectors
11. High expression of naked plasmid DNA in muscles of young rodents
12. Direct gene transfer into skeletal muscle in vivo: Factors affecting efficiency of transfer and stability of expression
13. Human dystrophin gene transfer: Production and expression of a functional recombinant DNA-based gene
14. Viral gene delivery to skeletal muscle: Insights on maturation-dependent loss of fiber infectivity for adenovirus and herpes simplex type 1 viral vectors
15. Muscle regeneration by bone marrow-derived myogenic progenitors
16. Divergent functional properties of ryanodine receptor types 1 and 3 expressed in a myogenic cell line
17. Helper virus-free transfer of herpes simplex virus type 1 plasmid vectors into neural cells
18. Gene transfer into hepatocytes mediated by helper virus-free HSV/AAV hybrid vectors
19. A defective HSV-1 vector expresses Escherichia coli beta-galactosidase in cultured peripheral neurons
20. Development and application of herpes simplex virus vectors for human gene therapy
21. Normal dystrophin transcripts detected in Duchenne muscular dystrophy patients after myoblast transplantation
22. The fate of individual myoblasts after transplantation into muscles of DMD patients
23. Dystrophin expression in the mdx mouse restored by stem cell transplantation
24. In vivo expression of full-length human dystrophin from adenoviral vectors deleted of all viral genes
25. Improved production of gutted adenovirus in cells expressing adenovirus preterminal protein and DNA polymerase
26. Helper virus-free herpes simplex virus type 1 amplicon vectors for granulocyte-macrophage colony-stimulating factor-enhanced vaccination therapy for experimental glioma
27. Dystrophin: The protein product of the Duchenne muscular dystrophy locus
28. Human myoblast transplantation: Preliminary results of 4 cases
29. Herpes simplex virus type 1 vector mediated gene transfer to muscle
30. The basal lamina is a physical barrier to herpes simplex virus-mediated gene delivery to mature muscle fibers
31. LacZ gene transfer to skeletal muscle using a replication-defective herpes simplex virus type 1 mutant vector
32. Gene transfer to muscle using herpes simplex virus-based vectors
33. HSV/AAV hybrid amplicon vectors extend transgene expression in human glioma cells
34. Cellular immune response to adenoviral vector infected cells does not require de novo viral gene expression: Implications for gene therapy
35. Dystrophin is expressed in mdx skeletal muscle fibers after normal myoblast implantation
36. Myoblast transfer in Duchenne muscular dystrophy
37. Gating of store-operated channels by conformational coupling to ryanodine receptors
38. A new adenoviral vector: Replacement of all viral coding sequences with 28 kb of DNA independently expressing both full-length dystrophin and beta-galactosidase
39. Site-specific integration by adeno-associated virus
40. Deletion of multiple immediate-early genes from herpes simplex virus reduces cytotoxicity and permits long-term gene expression in neurons
41. Encapsidated adenovirus minichromosomes allow delivery and expression of a 14 kb dystrophin cDNA to muscle cells
42. Cleavage of structural proteins during the assembly of the head of bacteriophage T4
43. Generation of high-titer defective HSV-1 vectors using an IE 2 deletion mutant and quantitative study of expression in cultured cortical cells
44. Myoblast implantation in Duchenne muscular dystrophy: The San Francisco study
45. High-efficiency gene transfer into skeletal muscle mediated by electric pulses
46. The basic science of gene therapy
47. In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector
48. A helper-dependent adenovirus vector system: Removal of helper virus by Cre-mediated excision of the viral packaging signal
49. Conversion of mdx myofibres from dystrophin-negative to -positive by injection of normal myoblasts
50. Impairment of force generation after adenovirus-mediated gene transfer to muscle is alleviated by adenoviral gene inactivation and host CD8+ T cell deficiency
51. RYR1 and RYR3 have different roles in the assembly of calcium release units of skeletal muscle
52. Efficient adenovirus-mediated transfer of a human minidystrophin gene to skeletal muscle of mdx mice
53. Primary mouse myoblast purification, characterization, and transplantation for cell-mediated gene therapy
54. Efficient and regulated erythropoietin production by naked DNA injection and muscle electroporation
55. Antibody formation after myoblast transplantation in Duchenne-dystrophic patients, donor HLA compatible
56. Herpes simplex virus type 1 DNA amplified as bacterial artificial chromosome inEscherichia coli: Rescue of replication-competent virus progeny and packaging of amplicon vectors
57. Improved helper virus-free packaging system for HSV amplicon vectors using an ICP27-deleted, oversized HSV-1 DNA in a bacterial artificial chromosome
58. The role of T cell immunity in the control of herpes simplex virus
59. Single-step conversion of cells to retrovirus vector producers with herpes simplex virus-Epstein-Barr virus hybrid amplicons
60. HSV-1 amplicon vectors - Simplicity and versatility
61. Efficient and stable adeno-associated virus-mediated transduction in the skeletal muscle of adult immunocompetent mice
62. The herpes simplex virus amplicon: A new eucaryotic defective-virus cloning-amplifying vector
63. The herpes simplex virus amplicon: Analyses of cis-acting replication functions
64. Long-term persistence of defective HSV-1 vectors in the rat brain is demonstrated by reactivation of vector gene expression
65. An enhanced packaging system for helper-dependent herpes simplex virus vectors
66. Immune response to green fluorescent protein: Implications for gene therapy
67. Myoblast transplantation between monozygotic twin girl carriers of Duchenne muscular dystrophy
68. Results of a triple blind clinical study of myoblast transplantations without immunosuppressive treatment in young boys with Duchenne muscular dystrophy
69. Fifty-one kilobase HSV-1 plasmid vector can be packaged using a helper virus-free system and supports expression in the rat brain
70. Diverse stabilities of expression in the rat brain from different cellular promoters in a helper virus-free herpes simplex virus type 1 vector system
71. HSV-1 amplicon vectors are a highly efficient gene delivery system for skeletal muscle myoblasts and myotubes
72. 2+sparks in dyspedic myotubes
73. Direct gene transfer into mouse muscle in vivo
74. Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector
75. Stable replication of plasmids derived from Epstein-Barr virus in various mammalian cells
76. Efficient infection of mature skeletal muscle with herpes simplex virus vectors by using dextran sulfate as a co-receptor
77. Efficient expression of naked DNA delivered intraarterially to limb muscles of nonhuman primates