Development of new therapy on muscular dystrophy

Clinical Neurology

Volumn 41, Issue 12, 2001, Pages 1154-1156

  Takeda, Shin'ichi ^a  

^a NONE

Author keywords

Cell therapy; Duchenne muscular dystrophy; Gene therapy; Micro dystrophin cDNA; Utrophin

Indexed keywords

ADENOVIRUS VECTOR; BETA GALACTOSIDASE; COMPLEMENTARY DNA; DYSTROGLYCAN; DYSTROPHIN; SARCOGLYCAN; UTROPHIN;

ADENO ASSOCIATED VIRUS; CONFERENCE PAPER; DUCHENNE MUSCULAR DYSTROPHY; GENE DELETION; GENE EXPRESSION; GENE LOCATION; GENE MUTATION; GENE THERAPY; GENE TRANSFER; IMMUNE RESPONSE; INFLAMMATION; MOUSE; NONHUMAN; PHENOTYPE; SARCOLEMMA; X CHROMOSOME LINKED DISORDER;

ANIMALS; CYTOSKELETAL PROTEINS; DRUG DESIGN; DYSTROPHIN; GENE THERAPY; HUMANS; MEMBRANE PROTEINS; MICE; MUSCULAR DYSTROPHIES; STEM CELL TRANSPLANTATION; UP-REGULATION; UTROPHIN;

EID: 0035760914     PISSN: 0009918X     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Conference Paper

References (10)

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2. Wang B, Li J, Xiao X: Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model. Proc Natl Acad Sci USA 97: 13714-13719, 2000
3. Harper SQ, DelloRusso C, Crawford RW, et al: Functional correction of muscular dystrophy by four-repeat microdystrophins. In 4th Annual Meeting of American Society of Gene Therapy, Seattle, June 1, 2001
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5. Bartlett RJ, Stockinger S, Denis MM, et al: In vivo targeted repair of a point mutation in the canine dystrophin gene by a chimeric RNA/DNA oligonucleotide. Nat Biotechnol 18: 615-622, 2000
6. ème Colloque Franco Japonais sur les Dystrophies Musculaires: progrès vers la therapié. 16 June. 2001
7. Ferrari G, Cusella-De Angelis G, Coletta M, et al: Muscle regeneration by bone marrow-derived myogenic progenitors. Science 279: 1528-1530, 1998
8. Gussoni E, Soneoka Y, Strickland CD, et al: Dystrophin expression in the mdx mouse restored by stem cell transplantation. Nature 401: 390-394, 1999
9. Yamamoto K, Yuasa K, Miyagoe Y, et al: Immune response to adenovirus-delivered antigens upregulates utrophin and results in mitigation of muscle pathology in mdx mice. Hum Gene Ther 11: 669-680, 2000
10. ème Colloque Franco-Japonais sur les Dystrophies Musculaires: progrès vets la therapié. 16 June, 2001