Various cells retrovirally transduced with N-acetylgalactosoamine-6-sulfate sulfatase correct Morquio skin fibroblasts in vitro

Human Gene Therapy

Volumn 12, Issue 16, 2001, Pages 2007-2016

  Toietta, G ^a   Severini, G M ^a   Traversari, C ^a   Tomatsu, S ^a   Sukegawa, K ^a   Fukuda, S ^a   Kondo, N ^a   Tortora, P ^a   Bordignon, C ^a  

^a UNIVERSITY OF MILANO BICOCCA   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; MANNOSE 6 PHOSPHATE; N ACETYLGALACTOSAMINE 6 SULFATASE; VIRUS VECTOR;

ANIMAL CELL; ARTICLE; B LYMPHOCYTE; COCULTURE; CONTROLLED STUDY; DNA TRANSFER; ENZYME ACTIVITY; ENZYME DEFICIENCY; GENE THERAPY; GENETIC TRANSDUCTION; HUMAN; HUMAN CELL; KERATINOCYTE; LYMPHOBLASTOID CELL; MORQUIO SYNDROME; MYOBLAST; NONHUMAN; NORMAL HUMAN; PROTEIN EXPRESSION; RABBIT; RETROVIRUS; RODENT; SKIN FIBROBLAST; SYNOVIOCYTE;

ANIMALS; CHONDROITINSULFATASES; COCULTURE TECHNIQUES; GENE THERAPY; HUMANS; MUCOPOLYSACCHARIDOSIS IV; RABBITS; RETROVIRIDAE; TRANSDUCTION, GENETIC;

ANIMALIA; MURINAE; ORYCTOLAGUS CUNICULUS; RODENTIA; UNIDENTIFIED RETROVIRUS;

EID: 0035195967     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/104303401753204571     Document Type: Article

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