-
1
-
-
0032725075
-
Gene therapy for hemophilia A and B: Patient selection and follow-up, requirements for a cure
-
(1999)
Thromb. Haemostasis
, vol.82
, pp. 572-575
-
-
Lusher, J.M.1
-
3
-
-
0027686238
-
In vivo gene therapy of hemophilia B: Sustained partial correction in factor IX-deficient dogs
-
(1993)
Science
, vol.262
, pp. 117-119
-
-
Kay, M.A.1
Rothenberg, S.2
Landen, C.N.3
Bellinger, D.A.4
Leland, F.5
Toman, C.6
Finegold, M.7
Thompson, A.R.8
Read, M.S.9
Brinkhous, K.M.10
-
4
-
-
17444387438
-
Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector
-
(1999)
Nat. Med.
, vol.5
, pp. 56-63
-
-
Herzog, R.W.1
Yang, E.Y.2
Couto, L.B.3
Hagstrom, J.N.4
Elwell, D.5
Fields, P.A.6
Burton, M.7
Bellinger, D.A.8
Read, M.S.9
Brinkhous, K.M.10
Podsakoff, G.M.11
Nichols, T.C.12
Kurtzman, G.J.13
High, K.A.14
-
5
-
-
17444372024
-
Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors
-
(1999)
Nat. Med.
, vol.5
, pp. 64-70
-
-
Snyder, R.O.1
Miao, C.2
Meuse, L.3
Tubb, J.4
Donahue, B.A.5
Lin, H.F.6
Stafford, D.W.7
Patel, S.8
Thompson, A.R.9
Nichols, T.10
Read, M.S.11
Bellinger, D.A.12
Brinkhous, K.M.13
Kay, M.A.14
-
9
-
-
0027521773
-
Adenovirus mediated expression of therapeutic plasma levels of human factor IX in mice
-
(1993)
Nat. Genet.
, vol.5
, pp. 397-402
-
-
Smith, T.A.1
Mehaffey, M.G.2
Kayda, D.B.3
Saunders, J.M.4
Yei, S.5
Trapnell, B.C.6
McClelland, A.7
Kaleko, M.8
-
11
-
-
0032853032
-
Repeat delivery of adeno-associated virus vectors to the rabbit airway
-
(1999)
J. Virol.
, vol.73
, pp. 9446-9455
-
-
Beck, S.E.1
Jones, L.A.2
Chesnut, K.3
Walsh, S.M.4
Reynolds, T.C.5
Carter, B.J.6
Askin, F.B.7
Flotte, T.R.8
Guggino, W.B.9
-
17
-
-
13044286785
-
Efficient and regulated erythropoietin production by naked DNA injection and muscle electroporation
-
(1999)
Proc. Natl. Acad. Sci. USA
, vol.96
, pp. 6417-6422
-
-
Rizzuto, G.1
Cappelletti, M.2
D'Maione, R.3
Savino, R.4
Lazzaro, D.5
Costa, P.6
Mathiesen, I.7
Cortese, R.8
Ciliberto, G.9
Laufer, R.10
La Monica, N.11
Fattori, E.12
-
18
-
-
12944273467
-
Highly efficient electro-gene therapy of solid tumor by using an expression plasmid for the herpes simplex virus thymidine kinase gene
-
(2000)
Proc. Natl. Acad. Sci. USA
, vol.97
, pp. 354-359
-
-
Goto, T.1
Nishi, T.2
Tamura, T.3
Dev, S.B.4
Takeshima, H.5
Kochi, M.6
Yoshizato, K.7
Kuratsu, J.8
Sakata, T.9
Hofmann, G.A.10
Ushio, Y.11
-
20
-
-
0034269179
-
High-level protein secretion into blood circulation after electric pulse-mediated gene transfer into skeletal muscle
-
(2000)
Mol. Ther.
, vol.2
, pp. 204-210
-
-
Bettan, M.1
Emmanuel, F.2
Darteil, R.3
Caillaud, J.M.4
Soubrier, F.5
Delaere, P.6
Branelec, D.7
Mahfoudi, A.8
Duverger, N.9
Scherman, D.10
-
21
-
-
0033542389
-
Ligand-dependent regulation of plasmid-based transgene expression in vivo
-
(1999)
Hum. Gene Ther.
, vol.10
, pp. 1499-1507
-
-
Abruzzese, R.V.1
Godin, D.2
Burcin, M.3
Mehta, V.4
French, M.5
Li, Y.6
O'Malley, B.W.7
Nordstrom, J.L.8
-
25
-
-
0028842611
-
Interferon-gamma inhibits transgene expression driven by SV40 or CMV promoters but augments expression driven by the mammalian MHC I promoter
-
(1995)
Hum. Gene Ther.
, vol.6
, pp. 1291-1297
-
-
Harms, J.S.1
Splitter, G.A.2
-
26
-
-
0034630175
-
Muscle transfection by electroporation with high-voltage and short-pulse currents provides high-level and long-lasting gene expression
-
(2000)
Hum. Gene Ther.
, vol.11
, pp. 909-916
-
-
Vicat, J.M.1
Boisseau, S.2
Jourdes, P.3
Laine, M.4
Wion, D.5
Bouali-Benazzouz, R.6
Benabid, A.L.7
Berger, F.8
-
28
-
-
13044257108
-
High-efficiency gene transfer into skeletal muscle mediated by electric pulses
-
(1999)
Proc. Natl. Acad. Sci. USA
, vol.96
, pp. 4262-4267
-
-
Mir, L.M.1
Bureau, M.F.2
Gehl, J.3
Rangara, R.4
Rouy, D.5
Caillaud, J.M.6
Delaere, P.7
Branellec, D.8
Schwartz, B.9
Scherman, D.10
-
29
-
-
85031516553
-
Erythropoietin expression and biological effect after single intramuscular administration of PINC formulated plasmid and in vivo electroporation
-
[Abstract]
-
(2000)
Mol. Ther.
, vol.1
-
-
MacLaughlin, F.C.1
Gondo, M.2
Fewell, J.3
Nicol, F.4
Nolan, E.5
Ash, O.6
Amoss, M.7
Mehta, V.8
Nordstrom, J.9
Smith, L.C.10
-
30
-
-
0034151775
-
Role of vector activation of T cell subsets in immune responses against the secreted transgene product factor IX
-
(2000)
Mol. Ther.
, vol.1
, pp. 225-235
-
-
Fields, P.A.1
Kowalczyk, W.2
Arruda, V.R.3
Armstrong, E.4
McCleland, W.L.5
Hagstrom, J.N.6
Pasi, K.J.7
Hildegund, C.J.E.8
Herzog, R.W.9
High, K.A.10
-
33
-
-
0034008961
-
The use of adeno-associated virus to circumvent the maturation-dependent viral transduction of muscle fibers
-
(2000)
Hum. Gene Ther.
, vol.11
, pp. 521-536
-
-
Pruchnic, R.1
Cao, B.2
Peterson, Z.Q.3
Xiao, X.4
Li, J.5
Samulski, R.J.6
Epperly, M.7
Huard, J.8
|