Gene redundancy and pharmacological gene therapy: Implications for X- linked adrenoleukodystrophy

Nature Medicine

Volumn 4, Issue 11, 1998, Pages 1261-1268

  Kemp, Stephan ^a   Wei, He Ming ^a   Lu, Jyh Feng ^a   Braiterman, Lelita T ^a   Mcguinness, Martina C ^a   Moser, Ann B ^a   Watkins, Paul A ^a   Smith, Kirby D ^a  

^a NONE

Author keywords

[No Author keywords available]

Indexed keywords

ARYLBUTYRIC ACID DERIVATIVE; COMPLEMENTARY DNA; PEROXISOME PROLIFERATOR; PEROXISOME PROLIFERATOR ACTIVATED RECEPTOR; VERY LONG CHAIN FATTY ACID;

ADRENOLEUKODYSTROPHY; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DIET THERAPY; DRUG EFFICACY; FATTY ACID OXIDATION; FIBROBLAST; GENE EXPRESSION; GENE THERAPY; HUMAN; HUMAN CELL; KNOCKOUT MOUSE; LYMPHOBLASTOID CELL; NONHUMAN; ORAL DRUG ADMINISTRATION; PEROXISOME; PRIORITY JOURNAL; X CHROMOSOME LINKED DISORDER;

ADRENOLEUKODYSTROPHY; ANIMALS; ATP-BINDING CASSETTE TRANSPORTERS; CELL LINE; CELLS, CULTURED; DNA PRIMERS; FIBROBLASTS; GENE THERAPY; HUMANS; LYMPHOCYTES; MICE; MICE, KNOCKOUT; MICROBODIES; MULTIGENE FAMILY; PHENYLBUTYRATES; PROTEINS; REVERSE TRANSCRIPTASE POLYMERASE CHAIN REACTION; X CHROMOSOME;

ANIMALIA; MAMMALIA;

EID: 0031730433     PISSN: 10788956     EISSN: None     Source Type: Journal    
DOI: 10.1038/3242     Document Type: Article

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