-
2
-
-
0003020112
-
Models of dystrophinopathy, pathological mechanisms and assessment of therapies
-
Brown SC, Lucy JA (eds). Cambridge University Press: Cambridge
-
Partridge TA. Models of dystrophinopathy, pathological mechanisms and assessment of therapies. In: Brown SC, Lucy JA (eds). Dystrophin: Gene, Protein and Cell Biology. Cambridge University Press: Cambridge, 1997, pp 310-331.
-
(1997)
Dystrophin: Gene, Protein and Cell Biology
, pp. 310-331
-
-
Partridge, T.A.1
-
3
-
-
0000801692
-
Dystrophinopathies
-
Engel AG, Franzini-Armstrong C (eds). McGraw-Hill: New York
-
Engel AG, Yamamoto M, Fischbeck KH. Dystrophinopathies. In: Engel AG, Franzini-Armstrong C (eds). Myology. McGraw-Hill: New York, 1994, pp 1133-1187.
-
(1994)
Myology
, pp. 1133-1187
-
-
Engel, A.G.1
Yamamoto, M.2
Fischbeck, K.H.3
-
4
-
-
0029857641
-
In vivo muscle gene transfer of full-length dystrophin with an adenoviral vector that lacks all viral genes
-
Clemens PR et al. In vivo muscle gene transfer of full-length dystrophin with an adenoviral vector that lacks all viral genes. Gene Therapy 1996; 3: 965-972.
-
(1996)
Gene Therapy
, vol.3
, pp. 965-972
-
-
Clemens, P.R.1
-
5
-
-
0029741231
-
Transient immunosuppression by FK506 permits a sustained high-level dystrophin expression after adenovirus-mediated dystrophin minigene transfer to skeletal muscles of adult dystrophic (mdx) mice
-
Lochmuller H et al. Transient immunosuppression by FK506 permits a sustained high-level dystrophin expression after adenovirus-mediated dystrophin minigene transfer to skeletal muscles of adult dystrophic (mdx) mice. Gene Therapy 1996; 3: 706-716.
-
(1996)
Gene Therapy
, vol.3
, pp. 706-716
-
-
Lochmuller, H.1
-
6
-
-
0030633693
-
Gene therapy of Duchenne muscular dystrophy
-
Fassati A, Murphy S, Dickson G. Gene therapy of Duchenne muscular dystrophy. Adv Genet 1997; 35: 117-153.
-
(1997)
Adv Genet
, vol.35
, pp. 117-153
-
-
Fassati, A.1
Murphy, S.2
Dickson, G.3
-
7
-
-
0031935395
-
The efficient expression of intravascularly delivered DNA in rat muscles
-
Budker V et al. The efficient expression of intravascularly delivered DNA in rat muscles. Gene Therapy 1998; 5: 272-276.
-
(1998)
Gene Therapy
, vol.5
, pp. 272-276
-
-
Budker, V.1
-
8
-
-
0031917023
-
Lipofection of cultured mouse muscle cells: A direct comparison of Lipofectamine and DOSPER
-
Dodds E et al. Lipofection of cultured mouse muscle cells: a direct comparison of Lipofectamine and DOSPER. Gene Therapy 1998; 5: 542-551.
-
(1998)
Gene Therapy
, vol.5
, pp. 542-551
-
-
Dodds, E.1
-
9
-
-
0029982279
-
Condensation of plasmid DNA with polylysine improves liposome-mediated gene transfer into established and primary muscle cells
-
Vitiello L et al. Condensation of plasmid DNA with polylysine improves liposome-mediated gene transfer into established and primary muscle cells. Gene Therapy 1996; 3: 396-404.
-
(1996)
Gene Therapy
, vol.3
, pp. 396-404
-
-
Vitiello, L.1
-
10
-
-
0002390589
-
Human dystrophin gene expression in mdx muscles after in vivo ballistic transfection, application of synthetic oligopeptide complexes and cationic liposomes
-
Baranov V et al. Human dystrophin gene expression in mdx muscles after in vivo ballistic transfection, application of synthetic oligopeptide complexes and cationic liposomes. In: NATO ASI, Subseries M, 1997, 105: 219-223.
-
(1997)
NATO ASI, Subseries M
, vol.105
, pp. 219-223
-
-
Baranov, V.1
-
11
-
-
0031559914
-
Bacterial β-galactosidase and human dystrophin genes are expressed in mouse skeletal muscle fibers after ballistic transfection
-
Zelenin V, Tarasenko O, Kolesnikov VA et al. Bacterial β-galactosidase and human dystrophin genes are expressed in mouse skeletal muscle fibers after ballistic transfection. FEBS Lett 1997; 414: 319-322.
-
(1997)
FEBS Lett
, vol.414
, pp. 319-322
-
-
Zelenin, V.1
Tarasenko, O.2
Kolesnikov, V.A.3
-
12
-
-
0030949396
-
Biologically erodable microspheres as potential oral drug delivery system
-
Mathiowitz E, Jacob JS, Jong YS et al. Biologically erodable microspheres as potential oral drug delivery system. Nature 1997; 386: 410-414.
-
(1997)
Nature
, vol.386
, pp. 410-414
-
-
Mathiowitz, E.1
Jacob, J.S.2
Jong, Y.S.3
-
13
-
-
0345068594
-
Simultaneous delivery of drugs and genes by gelatin nanospheres
-
Walsh S et al. Simultaneous delivery of drugs and genes by gelatin nanospheres. Pediatric Pulmonology 1997; (Suppl. 14) 255-257.
-
(1997)
Pediatric Pulmonology
, Issue.SUPPL. 14
, pp. 255-257
-
-
Walsh, S.1
-
14
-
-
0031914186
-
Aging normal and dystrophic muscle: Analysis of myogenicity in cultures of living single fibers
-
Bockhold KJ, Rosenblatt JD, Partridge TA. Aging normal and dystrophic muscle: analysis of myogenicity in cultures of living single fibers. Muscle Nerve 1998; 21: 173-183.
-
(1998)
Muscle Nerve
, vol.21
, pp. 173-183
-
-
Bockhold, K.J.1
Rosenblatt, J.D.2
Partridge, T.A.3
-
15
-
-
0030794156
-
Selection and use of ligands for receptor-mediated gene delivery to myogenic cells
-
Feero WG et al. Selection and use of ligands for receptor-mediated gene delivery to myogenic cells. Gene Therapy 1997; 4: 664-674.
-
(1997)
Gene Therapy
, vol.4
, pp. 664-674
-
-
Feero, W.G.1
-
16
-
-
0027186053
-
Overexpression of dystrophin in transgenic mdx mice eliminated dystrophic symptoms without toxicity
-
Cox GA et al. Overexpression of dystrophin in transgenic mdx mice eliminated dystrophic symptoms without toxicity. Nature 1993; 364: 725-729.
-
(1993)
Nature
, vol.364
, pp. 725-729
-
-
Cox, G.A.1
-
17
-
-
0030000074
-
Expression of full-length human dystrophin cDNA in mdx mouse muscle by HVJ-liposome injection
-
Yanagihara I et al. Expression of full-length human dystrophin cDNA in mdx mouse muscle by HVJ-liposome injection. Gene Therapy 1996; 3: 549-553.
-
(1996)
Gene Therapy
, vol.3
, pp. 549-553
-
-
Yanagihara, I.1
-
18
-
-
0031917799
-
Myosin regulatory elements as vector for gene transfer by intramuscular injection
-
Skarli M et al. Myosin regulatory elements as vector for gene transfer by intramuscular injection. Gene Therapy 1998; 5: 514-520.
-
(1998)
Gene Therapy
, vol.5
, pp. 514-520
-
-
Skarli, M.1
-
19
-
-
0030813879
-
Factors controlling the efficiency of cationic lipid-mediated transfection in vivo via intravenous administration
-
Liu F, Qi H, Huang L, Liu D. Factors controlling the efficiency of cationic lipid-mediated transfection in vivo via intravenous administration. Gene Therapy 1997; 4: 517-523.
-
(1997)
Gene Therapy
, vol.4
, pp. 517-523
-
-
Liu, F.1
Qi, H.2
Huang, L.3
Liu, D.4
-
20
-
-
0031435917
-
On the mechanism of DNA transfection: Efficient gene transfer without viruses
-
Coonrod A, Li F-Q, Horwitz M. On the mechanism of DNA transfection: efficient gene transfer without viruses. Gene Therapy 1997; 4: 1313-1321.
-
(1997)
Gene Therapy
, vol.4
, pp. 1313-1321
-
-
Coonrod, A.1
Li, F.-Q.2
Horwitz, M.3
-
21
-
-
0029122522
-
Expression of human full length and mini-dystrophin in transgenic mdx mice: Implication for gene therapy of duchenne muscular dystrophy
-
Wells D, Wells K, Asante EA et al. Expression of human full length and mini-dystrophin in transgenic mdx mice: implication for gene therapy of Duchenne muscular dystrophy. Hum Mol Genet 1995; 3: 1245-1250.
-
(1995)
Hum Mol Genet
, vol.3
, pp. 1245-1250
-
-
Wells, D.1
Wells, K.2
Asante, E.A.3
-
22
-
-
0026343877
-
Direct detection of dystrophin gene rearrangements by analysis of dystrophin mRNA in peripheral blood lymphocytes
-
Roberts RG, Barby TFM, Manner E et al. Direct detection of dystrophin gene rearrangements by analysis of dystrophin mRNA in peripheral blood lymphocytes. Am J Hum Genet 1991; 49: 298-310.
-
(1991)
Am J Hum Genet
, vol.49
, pp. 298-310
-
-
Roberts, R.G.1
Barby, T.F.M.2
Manner, E.3
|