-
1
-
-
0003260971
-
Hemophilia and related conditions-inherited deficiencies of prothrombin (factor II), factor V, and factors VII to XII
-
Beutler E, Lichtman MA, Coller BS, Kipps TJ (eds): New York, NY, McGraw Hill
-
Roberts HR, Huffman R: Hemophilia and related conditions-inherited deficiencies of prothrombin (factor II), factor V, and factors VII to XII, in Beutler E, Lichtman MA, Coller BS, Kipps TJ (eds): Hematology. New York, NY, McGraw Hill, 1995, p 1413
-
(1995)
Hematology
, pp. 1413
-
-
Roberts, H.R.1
Huffman, R.2
-
2
-
-
0028904215
-
Prospects for gene therapy for haemophilia A and B
-
Brownlee GG: Prospects for gene therapy for haemophilia A and B. Br Med Bull 51:91, 1995
-
(1995)
Br Med Bull
, vol.51
, pp. 91
-
-
Brownlee, G.G.1
-
3
-
-
0029144825
-
Progress towards gene therapy for the hemophilias
-
Thompson AR: Progress towards gene therapy for the hemophilias. Thromb Hemost 74:45, 1995
-
(1995)
Thromb Hemost
, vol.74
, pp. 45
-
-
Thompson, A.R.1
-
4
-
-
0028009619
-
Gene therapy and the hemophilias
-
Lozier J, Brinkhous KM: Gene therapy and the hemophilias. JAMA 271:47, 1994
-
(1994)
JAMA
, vol.271
, pp. 47
-
-
Lozier, J.1
Brinkhous, K.M.2
-
5
-
-
15044364852
-
Gene delivery for systemic expression
-
March K (ed): New York, NY, McGraw-Hill (in press)
-
Ponder KP: Gene delivery for systemic expression, in March K (ed): Gene Therapy for Cardiovascular Disease. New York, NY, McGraw-Hill (in press)
-
Gene Therapy for Cardiovascular Disease
-
-
Ponder, K.P.1
-
6
-
-
0028991820
-
In vivo gene delivery and expression of physiological levels of functional human factor VIII in mice
-
Connelly S, Smith TAG, Dhir G, Gardner JM, Mehaffey MG, Zaret KS, McClelland A, Kaleko M: In vivo gene delivery and expression of physiological levels of functional human factor VIII in mice. Hum Gene Ther 6:185, 1995
-
(1995)
Hum Gene Ther
, vol.6
, pp. 185
-
-
Connelly, S.1
Smith, T.A.G.2
Dhir, G.3
Gardner, J.M.4
Mehaffey, M.G.5
Zaret, K.S.6
McClelland, A.7
Kaleko, M.8
-
7
-
-
0030069229
-
High-level tissue-specific expression of functional human factor VIII in mice
-
Connelly S, Gardner JM, McClelland A, Kaleko M: High-level tissue-specific expression of functional human factor VIII in mice. Hum Gene Ther 7:183, 1996
-
(1996)
Hum Gene Ther
, vol.7
, pp. 183
-
-
Connelly, S.1
Gardner, J.M.2
McClelland, A.3
Kaleko, M.4
-
8
-
-
0028934815
-
Cellular and humoral immune responses to adenoviral vectors containing factor IX gene: Tolerization of factor IX and vector antigens allows for long-term expression
-
Dai Y, Schwartz EM, Gu D, Zhang W-W, Sarvetnick N, Verma IM: Cellular and humoral immune responses to adenoviral vectors containing factor IX gene: Tolerization of factor IX and vector antigens allows for long-term expression. Proc Natl Acad Sci USA 92:1401, 1995
-
(1995)
Proc Natl Acad Sci USA
, vol.92
, pp. 1401
-
-
Dai, Y.1
Schwartz, E.M.2
Gu, D.3
Zhang, W.-W.4
Sarvetnick, N.5
Verma, I.M.6
-
9
-
-
0028274169
-
In vivo hepatic gene therapy: Complete albeit transient correction of factor IX deficiency in hemophilia B dogs
-
Kay MA, Landen CN, Rothenberg SR, Taylor LA, Leland F, Wiehle S, Fang B, Bellinger D, Finegold M, Thompson AR, Read M, Brinkhous KM, Woo SLC: In vivo hepatic gene therapy: Complete albeit transient correction of factor IX deficiency in hemophilia B dogs. Proc Natl Acad Sci USA 91:2353, 1994
-
(1994)
Proc Natl Acad Sci USA
, vol.91
, pp. 2353
-
-
Kay, M.A.1
Landen, C.N.2
Rothenberg, S.R.3
Taylor, L.A.4
Leland, F.5
Wiehle, S.6
Fang, B.7
Bellinger, D.8
Finegold, M.9
Thompson, A.R.10
Read, M.11
Brinkhous, K.M.12
Woo, S.L.C.13
-
10
-
-
0027521773
-
Adenovirus mediated expression of therapeutic plasma levels of human factor IX in mice
-
Smith TAG, Mehaffey MG, Kayda DB, Saunders JM, Yei S, Trapneck BC, McClelland A, Kaleko M: Adenovirus mediated expression of therapeutic plasma levels of human factor IX in mice. Nat Genet 5:397, 1993
-
(1993)
Nat Genet
, vol.5
, pp. 397
-
-
Smith, T.A.G.1
Mehaffey, M.G.2
Kayda, D.B.3
Saunders, J.M.4
Yei, S.5
Trapneck, B.C.6
McClelland, A.7
Kaleko, M.8
-
11
-
-
0029916598
-
Successful expression of human factor IX following repeat administration of an adenoviral vector in mice
-
Walter J, You Q, Hagstrom JN, Sands M, High KA: Successful expression of human factor IX following repeat administration of an adenoviral vector in mice. Proc Natl Acad Sci USA 93:3056, 1996
-
(1996)
Proc Natl Acad Sci USA
, vol.93
, pp. 3056
-
-
Walter, J.1
You, Q.2
Hagstrom, J.N.3
Sands, M.4
High, K.A.5
-
12
-
-
0028223310
-
Gene transfer in vivo: Sustained expression of genes introduced into the liver by receptor-targeted uptake
-
Perales JC, Ferkol T, Beegen H, Ratnoft OD, Hanson RW: Gene transfer in vivo: Sustained expression of genes introduced into the liver by receptor-targeted uptake. Proc Natl Acad Sci USA 91:4086, 1994
-
(1994)
Proc Natl Acad Sci USA
, vol.91
, pp. 4086
-
-
Perales, J.C.1
Ferkol, T.2
Beegen, H.3
Ratnoft, O.D.4
Hanson, R.W.5
-
13
-
-
0027686238
-
In vivo gene therapy of hemophilia B: Sustained partial correction in factor IX deficient dogs
-
Kay MA, Rothenberg S, Bellinger DA, Leland F, Tomin C, Reed MS, Brinkhouse KM, Woo SLC: In vivo gene therapy of hemophilia B: Sustained partial correction in factor IX deficient dogs. Science 266:117, 1993
-
(1993)
Science
, vol.266
, pp. 117
-
-
Kay, M.A.1
Rothenberg, S.2
Bellinger, D.A.3
Leland, F.4
Tomin, C.5
Reed, M.S.6
Brinkhouse, K.M.7
Woo, S.L.C.8
-
14
-
-
0026486612
-
Gene therapy via primary myoblasts: Long-term expression of factor IX protein following transplantation in vivo
-
Dai Y, Roman M, Naviaux RK, Verma IM: Gene therapy via primary myoblasts: Long-term expression of factor IX protein following transplantation in vivo. Proc Natl Acad Sci USA 89:10892, 1992
-
(1992)
Proc Natl Acad Sci USA
, vol.89
, pp. 10892
-
-
Dai, Y.1
Roman, M.2
Naviaux, R.K.3
Verma, I.M.4
-
15
-
-
0028386527
-
Primary myoblast-mediated gene transfer: Persistent expression of human factor IX in mice
-
Yao S-N, Smith KJ, Kurachi K: Primary myoblast-mediated gene transfer: Persistent expression of human factor IX in mice. Gene Ther 1:99, 1994
-
(1994)
Gene Ther
, vol.1
, pp. 99
-
-
Yao, S.-N.1
Smith, K.J.2
Kurachi, K.3
-
16
-
-
0028158811
-
Liver-directed gene therapy: Quantitative evaluation of promoter elements using in vivo retroviral transduction
-
Rettinger SD, Kennedy S, Wu X, Hafenrichter D, Flye MW, Ponder KP: Liver-directed gene therapy: Quantitative evaluation of promoter elements using in vivo retroviral transduction. Proc Natl Acad Sci USA 91:1460, 1994
-
(1994)
Proc Natl Acad Sci USA
, vol.91
, pp. 1460
-
-
Rettinger, S.D.1
Kennedy, S.2
Wu, X.3
Hafenrichter, D.4
Flye, M.W.5
Ponder, K.P.6
-
17
-
-
0027992935
-
Quantitative evaluation of liver-specific promoters from retroviral vectors after in vivo transduction of hepatocytes
-
Hafenrichter DG, Rettinger SD, Kennedy S, Wu X, Flye MW, Ponder KP: Quantitative evaluation of liver-specific promoters from retroviral vectors after in vivo transduction of hepatocytes. Blood 84:3394, 1994
-
(1994)
Blood
, vol.84
, pp. 3394
-
-
Hafenrichter, D.G.1
Rettinger, S.D.2
Kennedy, S.3
Wu, X.4
Flye, M.W.5
Ponder, K.P.6
-
18
-
-
0030008178
-
1-antitrypsin in vivo
-
1-antitrypsin in vivo. Hum Gene Ther 5:637, 1996
-
(1996)
Hum Gene Ther
, vol.5
, pp. 637
-
-
Okuyama, T.1
Huber, R.M.2
Bowling, W.3
Pearline, R.4
Kennedy, S.C.5
Flye, M.W.6
Ponder, K.P.7
-
19
-
-
0027489294
-
In vivo hepatocyte transduction with retrovirus during in-flow occlusion
-
Rettinger SD, Ponder KP, Saylors RL, Kennedy SC, Hafenrichter DG, Flye MW: In vivo hepatocyte transduction with retrovirus during in-flow occlusion. J Surg Res 52:418, 1993
-
(1993)
J Surg Res
, vol.52
, pp. 418
-
-
Rettinger, S.D.1
Ponder, K.P.2
Saylors, R.L.3
Kennedy, S.C.4
Hafenrichter, D.G.5
Flye, M.W.6
-
20
-
-
0004118979
-
Characterization of a cDNA for human factor X
-
Leytus SP, Chung DW, Kisiel W, Kurachi K, Davie EW: Characterization of a cDNA for human factor X. Proc Natl Acad Sci USA 81:3699, 1984
-
(1984)
Proc Natl Acad Sci USA
, vol.81
, pp. 3699
-
-
Leytus, S.P.1
Chung, D.W.2
Kisiel, W.3
Kurachi, K.4
Davie, E.W.5
-
21
-
-
0024239024
-
Construction and use of a safe and efficient amphotropic packaging cell line
-
Markowitz D, Goff S, Bank A: Construction and use of a safe and efficient amphotropic packaging cell line. Virology 167:400, 1988
-
(1988)
Virology
, vol.167
, pp. 400
-
-
Markowitz, D.1
Goff, S.2
Bank, A.3
-
22
-
-
0014604721
-
Murine sarcoma and leukemia viruses: Assay using clonal lines of contact inhibited mouse cells
-
Jainchill JL, Aaronson SA, Todoro GJ: Murine sarcoma and leukemia viruses: Assay using clonal lines of contact inhibited mouse cells. J Virol 4:549, 1969
-
(1969)
J Virol
, vol.4
, pp. 549
-
-
Jainchill, J.L.1
Aaronson, S.A.2
Todoro, G.J.3
-
23
-
-
0023613541
-
Liver cell lines
-
Darlington G: Liver cell lines. Methods Enzymol 151:1938. 1987
-
(1987)
Methods Enzymol
, vol.151
, pp. 1938
-
-
Darlington, G.1
-
24
-
-
0028076782
-
Improved methods of retroviral vector transduction and production for gene therapy
-
Kotani H, Newton PB, Zhang S, Chiang YL, Otto E, Weaver L, Blaese RM, Anderson WF, McGarrity GJ: Improved methods of retroviral vector transduction and production for gene therapy. Hum Gene Ther 5:19, 1994
-
(1994)
Hum Gene Ther
, vol.5
, pp. 19
-
-
Kotani, H.1
Newton, P.B.2
Zhang, S.3
Chiang, Y.L.4
Otto, E.5
Weaver, L.6
Blaese, R.M.7
Anderson, W.F.8
McGarrity, G.J.9
-
25
-
-
0003085947
-
Immunoassays
-
Harlow E, Lane D (eds): Cold Spring Harbor, NY, Cold Spring Harbor Laboratory
-
Harlow E, Lane D: Immunoassays, in Harlow E, Lane D (eds): Antibodies: A Laboratory Manual. Cold Spring Harbor, NY, Cold Spring Harbor Laboratory, 1988, p 553
-
(1988)
Antibodies: A Laboratory Manual
, pp. 553
-
-
Harlow, E.1
Lane, D.2
-
26
-
-
0030028515
-
Liver-enriched transcription factor HNF-4 and ubiquitous factor NF-Y are critical for expression of blood coagulation factor X
-
Hung H-L, High KA: Liver-enriched transcription factor HNF-4 and ubiquitous factor NF-Y are critical for expression of blood coagulation factor X. J Biol Chem 271:2323, 1996
-
(1996)
J Biol Chem
, vol.271
, pp. 2323
-
-
Hung, H.-L.1
High, K.A.2
-
27
-
-
0029154012
-
Gene therapy for hemophilia B: Host immunosuppression prolongs the therapeutic effect of adenovirus-mediated factor IX expression
-
Fang B, Eisensmith RC, Want H, Kay MA, Cross RE, Landen CN, Gordon G, Bellinger DA, Read MS, Hu PC, Brinkhous KM, Woo SLC: Gene therapy for hemophilia B: Host immunosuppression prolongs the therapeutic effect of adenovirus-mediated factor IX expression. Hum Gene Ther 6:1039, 1995
-
(1995)
Hum Gene Ther
, vol.6
, pp. 1039
-
-
Fang, B.1
Eisensmith, R.C.2
Want, H.3
Kay, M.A.4
Cross, R.E.5
Landen, C.N.6
Gordon, G.7
Bellinger, D.A.8
Read, M.S.9
Hu, P.C.10
Brinkhous, K.M.11
Woo, S.L.C.12
-
28
-
-
0029849258
-
Portal branch occlusion safely facilitates in vivo retroviral vector transduction of rat liver
-
Bowling WM, Kennedy SC, Cai SR, Duncan JR, Gao C, Flye MW, Ponder KP: Portal branch occlusion safely facilitates in vivo retroviral vector transduction of rat liver. Hum Gene Ther 7:2113, 1996
-
(1996)
Hum Gene Ther
, vol.7
, pp. 2113
-
-
Bowling, W.M.1
Kennedy, S.C.2
Cai, S.R.3
Duncan, J.R.4
Gao, C.5
Flye, M.W.6
Ponder, K.P.7
-
29
-
-
0029088057
-
A modified urokinase activator induces liver regeneration without bleeding
-
Lieber A, Vrancken Peeters MJ, Gown A, Perkins J, May MA: A modified urokinase activator induces liver regeneration without bleeding. Hum Gene Ther 6:1029, 1995
-
(1995)
Hum Gene Ther
, vol.6
, pp. 1029
-
-
Lieber, A.1
Vrancken Peeters, M.J.2
Gown, A.3
Perkins, J.4
May, M.A.5
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