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Chichester, UK: John Wiley and Sons Ltd
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Report on the 124th ENMC International Workshop. Treatment of Duchenne muscular dystrophy: Defining the gold standard of management
Naarden, The Netherlands, April 2-4th 2004
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Conversion of mdx myofibres from dystrophin-negative to positive by injection of normal myoblasts
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Cell therapy of alpha-sarcoglycan null dystrophic mice through intra-arterial delivery of mesoangioblasts
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Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies. Part I: Rationale
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Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies. Part II: Clinical protocol
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Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies. Part III: Ethical considerations
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Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy
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Highly efficient EIAV-mediated in utero gene transfer and expression in the major muscle groups affected by Duchenne muscular dystrophy
May 13 [Epub ahead of print]
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