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Volumn 23, Issue 2, 2004, Pages

Current and future therapy in muscular dystrophy; need for a common language between basic scientists and clinicians

Author keywords

Duchenne muscular dystrophy; Terminology

Indexed keywords

ADENOVIRUS VECTOR; ANABOLIC AGENT; ANTISENSE OLIGONUCLEOTIDE; BETA GALACTOSIDASE; CORTICOSTEROID; CREATINE; DYSTROPHIN; NAKED DNA; PARVOVIRUS VECTOR; PREDNISOLONE; UTROPHIN;

EID: 9344240818     PISSN: 11282460     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Review
Times cited : (6)

References (13)
  • 2
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    • Glucocorticoid corticosteroids for Duchenne muscular dystrophy (Cochrane review)
    • Chichester, UK: John Wiley and Sons Ltd
    • Manzur A, Kuntzer T, Pike MG, et al. Glucocorticoid corticosteroids for Duchenne muscular dystrophy (Cochrane Review). The Cochrane Library. Chichester, UK: John Wiley and Sons Ltd; 2004.
    • (2004) The Cochrane Library
    • Manzur, A.1    Kuntzer, T.2    Pike, M.G.3
  • 3
    • 4344588135 scopus 로고    scopus 로고
    • Report on the 124th ENMC International Workshop. Treatment of Duchenne muscular dystrophy: Defining the gold standard of management
    • Naarden, The Netherlands, April 2-4th 2004
    • Bushby K, Muntoni F, Urtizberea A, et al. Report on the 124th ENMC International Workshop. Treatment of Duchenne muscular dystrophy: defining the gold standard of management. Naarden, The Netherlands, April 2-4th 2004. Neuromusc Disord 2004;14:526-34.
    • (2004) Neuromusc Disord , vol.14 , pp. 526-534
    • Bushby, K.1    Muntoni, F.2    Urtizberea, A.3
  • 4
    • 0024540879 scopus 로고
    • Conversion of mdx myofibres from dystrophin-negative to positive by injection of normal myoblasts
    • Partridge TA, Morgan JE, Coulton GR, et al Conversion of mdx myofibres from dystrophin-negative to positive by injection of normal myoblasts. Nature 1989;337:176-9.
    • (1989) Nature , vol.337 , pp. 176-179
    • Partridge, T.A.1    Morgan, J.E.2    Coulton, G.R.3
  • 6
    • 0027269957 scopus 로고
    • Myoblast transfer in Duchenne muscular dystrophy
    • Karpati G, Ajdukovic D, Arnold D, et al. Myoblast transfer in Duchenne muscular dystrophy. Ann Neurol 1993;34:8-17.
    • (1993) Ann Neurol , vol.34 , pp. 8-17
    • Karpati, G.1    Ajdukovic, D.2    Arnold, D.3
  • 7
    • 0042344907 scopus 로고    scopus 로고
    • Cell therapy of alpha-sarcoglycan null dystrophic mice through intra-arterial delivery of mesoangioblasts
    • Sampaolesi M, Torrente Y, Innocenzi A, et al. Cell therapy of alpha-sarcoglycan null dystrophic mice through intra-arterial delivery of mesoangioblasts. Science 2003;301:487-92.
    • (2003) Science , vol.301 , pp. 487-492
    • Sampaolesi, M.1    Torrente, Y.2    Innocenzi, A.3
  • 8
    • 0036823752 scopus 로고    scopus 로고
    • Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies. Part I: Rationale
    • Thioudellet C, Blot S, Squiban P, et al. Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies. Part I: Rationale. Neuromusc Disord 2002;12:S49-51.
    • (2002) Neuromusc Disord , vol.12
    • Thioudellet, C.1    Blot, S.2    Squiban, P.3
  • 9
    • 0036824011 scopus 로고    scopus 로고
    • Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies. Part II: Clinical protocol
    • Romero NB, Benveniste O, Payan C, et al. Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies. Part II: Clinical protocol. Neuromusc Disord 2002;12:S45-S48.
    • (2002) Neuromusc Disord , vol.12
    • Romero, N.B.1    Benveniste, O.2    Payan, C.3
  • 10
    • 0036823512 scopus 로고    scopus 로고
    • Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies. Part III: Ethical considerations
    • Fardeau M. Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies. Part III: Ethical considerations. Neuromusc Disord 2002;12:S52-S54.
    • (2002) Neuromusc Disord , vol.12
    • Fardeau, M.1
  • 11
    • 0036823504 scopus 로고    scopus 로고
    • Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy
    • Aartsma-Rus A, Bremmer-Bout M, Janson AAM, et al. Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy. Neuromusc Disord 2002;12:S71-S77.
    • (2002) Neuromusc Disord , vol.12
    • Aartsma-Rus, A.1    Bremmer-Bout, M.2    Janson, A.A.M.3
  • 12
    • 0036823499 scopus 로고    scopus 로고
    • The role of utrophin in the potential therapy of Duchenne muscular dystrophy
    • Perkins KJ, Davies KE. The role of utrophin in the potential therapy of Duchenne muscular dystrophy. Neuromusc Disord 2002;12:S78-S89.
    • (2002) Neuromusc Disord , vol.12
    • Perkins, K.J.1    Davies, K.E.2
  • 13
    • 4243132862 scopus 로고    scopus 로고
    • Highly efficient EIAV-mediated in utero gene transfer and expression in the major muscle groups affected by Duchenne muscular dystrophy
    • May 13 [Epub ahead of print]
    • Gregory LG, Waddington SN, Holder MV, et al. Highly efficient EIAV-mediated in utero gene transfer and expression in the major muscle groups affected by Duchenne muscular dystrophy. Gene Ther 2004; May 13 [Epub ahead of print].
    • (2004) Gene Ther
    • Gregory, L.G.1    Waddington, S.N.2    Holder, M.V.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.