Combined enzyme replacement therapy and hematopoietic stem cell transplantation in mucopolysacharidosis type VI

JIMD Reports

Volumn 2, Issue , 2012, Pages 103-106

  Sillence, D ^b   Waters, K ^a   Donaldson, S ^a   Shaw, P J ^a   Ellaway, C ^a  

^a CHILDREN S HOSPITAL AT WESTMEAD   (Australia)

^b UNIVERSITY OF SYDNEY   (Australia)

Author keywords

Carpal tunnel syndrome; Dermatan sulfate; Enzyme replacement therapy; Hematopoietic stem cell transplantation; Obstructive sleep apnea

Indexed keywords

EID: 85040148540     PISSN: 21928304     EISSN: 21928312     Source Type: Book Series    
DOI: 10.1007/8904_2011_56     Document Type: Chapter

References (11)

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