Safety and efficacy of enzyme replacement therapy in combination with hematopoietic stem cell transplantation in Hurler syndrome

Genetics in Medicine

Volumn 7, Issue 2, 2005, Pages 143-146

  Grewal, Satkiran S ^a,l   Wynn, Robert ^b   Abdenur, Jose E ^c   Burton, Barbara K ^d   Gharib, Maged ^b   Haase, Claudia ^e   Hayashi, Robert J ^f   Shenoy, Shalini ^f   Sillence, David ^g   Tiller, George E ^h   Dudek, Martha E ^h   Van Royen Kerkhof, Annet ⁱ   Wraith, James E ^j   Woodard, Paul ^k   Young, Guy A ^c   Wulffraat, Nico ⁱ   Whitley, Chester B ^a   Peters, Charles ^a  

^a UNIVERSITY OF MINNESOTA MEDICAL SCHOOL   (United States)

^b ROYAL MANCHESTER CHILDREN S HOSPITAL   (United Kingdom)

^c CHILDREN S HOSPITAL OF ORANGE COUNTY   (United States)

^d CHILDREN'S MEMORIAL HOSPITAL   (United States)

^e University Children's Hospitals   (Germany)

^f ST LOUIS CHILDREN S HOSPITAL   (United States)

^g CHILDREN S HOSPITAL AT WESTMEAD   (Australia)

^h VANDERBILT UNIVERSITY MEDICAL CENTER   (United States)

ⁱ UNIVERSITY MEDICAL CENTER UTRECHT   (Netherlands)

^j Willink Biochemical Genetics Unit   (United Kingdom)

^k ST JUDE CHILDREN S RESEARCH HOSPITAL   (United States)

^l UNIVERSITY OF MINNESOTA   (United States)

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Author keywords

Enzyme replacement therapy; Hematopoietic stem cell transplantation; Hurler syndrome; Laronidase; Mucopolysaccharidosis

Indexed keywords

ENZYME ANTIBODY; GLYCOSAMINOGLYCAN; LARONIDASE;

ARTICLE; ASSISTED VENTILATION; CLINICAL ARTICLE; CONTROLLED STUDY; DRUG EFFICACY; DRUG SAFETY; DRUG TOLERABILITY; ENZYME REPLACEMENT; FOLLOW UP; GRAFT FAILURE; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; HURLER SYNDROME; INFANT; LUNG HEMORRHAGE; MULTIPLE ORGAN FAILURE; PRACTICE GUIDELINE; PRESCHOOL CHILD; RESPIRATORY FAILURE; SURVIVAL RATE; TREATMENT PLANNING; URINE LEVEL; VEIN OCCLUSION;

ACUTE DISEASE; COMBINED MODALITY THERAPY; FEMALE; GRAFT REJECTION; GRAFT VS HOST DISEASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; IDURONIDASE; INFANT; MALE; MUCOPOLYSACCHARIDOSIS I; RECOMBINANT PROTEINS; RESPIRATION, ARTIFICIAL; TREATMENT OUTCOME;

EID: 20944443759     PISSN: 10983600     EISSN: None     Source Type: Journal    
DOI: 10.1097/01.GIM.0000154299.22120.6A     Document Type: Article

References (12)

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