Hematopoietic Stem Cell Transplantation for Patients with Mucopolysaccharidosis II

Biology of Blood and Marrow Transplantation

Volumn 23, Issue 10, 2017, Pages 1795-1803

  Kubaski, Francyne ^a,b,c   Yabe, Hiromasa ^d   Suzuki, Yasuyuki ^e   Seto, Toshiyuki ^f   Hamazaki, Takashi ^f   Mason, Robert W ^a,b   Xie, Li ^a   Onsten, Tor Gunnar Hugo ^g,h   Leistner Segal, Sandra ^c,g,h   Giugliani, Roberto ^c,g,h   Dũng, Vũ Chí ⁱ   Ngoc, Can Thi Bich ⁱ   Yamaguchi, Seiji ^j   Montaño, Adriana M ^k   Orii, Kenji E ^e   Fukao, Toshiyuki ^e   Shintaku, Haruo ^f   Orii, Tadao ^e   Tomatsu, Shunji ^a,e,j,l  

^a NEMOURS ALFRED I DUPONT HOSPITAL FOR CHILDREN   (United States)

^b UNIVERSITY OF DELAWARE   (United States)

^c Instituto Nacional de Genética Médica Populacional INAGEMP   (Brazil)

^d TOKAI UNIVERSITY SCHOOL OF MEDICINE   (Japan)

^e GIFU UNIVERSITY   (Japan)

^f OSAKA CITY UNIVERSITY GRADUATE SCHOOL OF MEDICINE   (Japan)

^g HOSPITAL DE CLÍNICAS DE PORTO ALEGRE   (Brazil)

^h FEDERAL UNIVERSITY OF RIO GRANDE DO SUL   (Brazil)

ⁱ NATIONAL HOSPITAL OF PEDIATRICS   (Viet Nam)

^j SHIMANE UNIVERSITY   (Japan)

^k SAINT LOUIS UNIVERSITY SCHOOL OF MEDICINE   (United States)

^l THOMAS JEFFERSON UNIVERSITY   (United States)

more..

Author keywords

Enzyme replacement therapy; Hematopoietic stem cell transplantation; Hunter syndrome; Iduronate 2 sulfatase; Mucopolysaccharidosis II

Indexed keywords

GLYCOSAMINOGLYCAN;

ADOLESCENT; ADULT; ARTICLE; BLOOD SAMPLING; CHILD; CONTROLLED STUDY; DAILY LIFE ACTIVITY; ENZYME REPLACEMENT; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; HUNTER SYNDROME; JOINT FUNCTION; LIQUID CHROMATOGRAPHY-MASS SPECTROMETRY; MAJOR CLINICAL STUDY; NEUROIMAGING; NUCLEAR MAGNETIC RESONANCE IMAGING; SURVIVAL RATE; BLOOD; MORTALITY; PRESCHOOL CHILD; PROCEDURES; YOUNG ADULT;

ADOLESCENT; CHILD; CHILD, PRESCHOOL; ENZYME REPLACEMENT THERAPY; GLYCOSAMINOGLYCANS; GRAFT VS HOST DISEASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; MAGNETIC RESONANCE IMAGING; MUCOPOLYSACCHARIDOSIS II; YOUNG ADULT;

EID: 85028300855     PISSN: 10838791     EISSN: 15236536     Source Type: Journal    
DOI: 10.1016/j.bbmt.2017.06.020     Document Type: Article

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