메뉴 건너뛰기




Volumn 10, Issue 4, 2017, Pages 259-266

Hematopoietic stem cell transplantation for sickle cell disease: The changing landscape

Author keywords

Chronic blood transfusion; Hematopoietic stem cell transplantation; Sickle cell anemia

Indexed keywords

CD45 ANTIGEN; DEFERASIROX; FERRITIN; HEMOGLOBIN S; HYDROXYUREA;

EID: 85026540280     PISSN: 16583876     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.hemonc.2017.05.008     Document Type: Review
Times cited : (58)

References (61)
  • 1
    • 84987827733 scopus 로고    scopus 로고
    • Survival in adults with sickle cell disease in a high-income setting
    • Gardner, K., Douiri, A., Drasar, E., Allman, M., Mwirigi, A., Awogbade, M., et al. Survival in adults with sickle cell disease in a high-income setting. Blood 128 (2016), 1436–1438.
    • (2016) Blood , vol.128 , pp. 1436-1438
    • Gardner, K.1    Douiri, A.2    Drasar, E.3    Allman, M.4    Mwirigi, A.5    Awogbade, M.6
  • 2
    • 0022628893 scopus 로고
    • Prophylaxis with oral penicillin in children with sickle cell anemia. A randomized trial
    • Gaston, M.H., Verter, J.I., Woods, G., Pegelow, C., Kelleher, J., Presbury, G., et al. Prophylaxis with oral penicillin in children with sickle cell anemia. A randomized trial. N Engl J Med 314 (1986), 1593–1599.
    • (1986) N Engl J Med , vol.314 , pp. 1593-1599
    • Gaston, M.H.1    Verter, J.I.2    Woods, G.3    Pegelow, C.4    Kelleher, J.5    Presbury, G.6
  • 3
    • 2942703899 scopus 로고    scopus 로고
    • Pneumococcal vaccines for sickle cell disease. Cochrane Database Sys Rrev;. CD003885.
    • Davies EG, Riddington C, Lottenberg R, Dower N. Pneumococcal vaccines for sickle cell disease. Cochrane Database Sys Rrev; 2004. CD003885.
    • (2004)
    • Davies, E.G.1    Riddington, C.2    Lottenberg, R.3    Dower, N.4
  • 4
    • 62649144053 scopus 로고    scopus 로고
    • Trends in pediatric sickle cell disease-related mortality in the United States, 1983–2002
    • Yanni, E., Grosse, S.D., Yang, Q., Olney, R.S., Trends in pediatric sickle cell disease-related mortality in the United States, 1983–2002. J Pediatr 154 (2009), 541–545.
    • (2009) J Pediatr , vol.154 , pp. 541-545
    • Yanni, E.1    Grosse, S.D.2    Yang, Q.3    Olney, R.S.4
  • 5
    • 0023906590 scopus 로고
    • Newborn screening for sickle cell disease: effect on mortality
    • Vichinsky, E., Hurst, D., Earles, A., Kleman, K., Lubin, B., Newborn screening for sickle cell disease: effect on mortality. Pediatrics 81 (1988), 749–755.
    • (1988) Pediatrics , vol.81 , pp. 749-755
    • Vichinsky, E.1    Hurst, D.2    Earles, A.3    Kleman, K.4    Lubin, B.5
  • 6
    • 0026724041 scopus 로고
    • Transcranial Doppler correlation with cerebral angiography in sickle cell disease
    • Adams, R.J., Nichols, F.T., Figueroa, R., McKie, V., Lott, T., Transcranial Doppler correlation with cerebral angiography in sickle cell disease. Stroke 23 (1992), 1073–1077.
    • (1992) Stroke , vol.23 , pp. 1073-1077
    • Adams, R.J.1    Nichols, F.T.2    Figueroa, R.3    McKie, V.4    Lott, T.5
  • 7
    • 0032474692 scopus 로고    scopus 로고
    • Prevention of a first stroke by transfusions in children with sickle cell anemia and abnormal results on transcranial Doppler ultrasonography
    • Adams, R.J., Snieder, H., McKie, V.C., Clair, B., Brambilla, D., Adams, R.J., et al. Prevention of a first stroke by transfusions in children with sickle cell anemia and abnormal results on transcranial Doppler ultrasonography. N Eng J Med 339 (1998), 5–11.
    • (1998) N Eng J Med , vol.339 , pp. 5-11
    • Adams, R.J.1    Snieder, H.2    McKie, V.C.3    Clair, B.4    Brambilla, D.5    Adams, R.J.6
  • 8
    • 79251628870 scopus 로고    scopus 로고
    • Impact of early transcranial Doppler screening and intensive therapy on cerebral vasculopathy outcome in a newborn sickle cell anemia cohort
    • [quiz 1436]
    • Bernaudin, F., Verlhac, S., Arnaud, C., Kamdem, A., Chevret, S., Hau, I., et al. Impact of early transcranial Doppler screening and intensive therapy on cerebral vasculopathy outcome in a newborn sickle cell anemia cohort. Blood 117 (2011), 1130–1140 [quiz 1436].
    • (2011) Blood , vol.117 , pp. 1130-1140
    • Bernaudin, F.1    Verlhac, S.2    Arnaud, C.3    Kamdem, A.4    Chevret, S.5    Hau, I.6
  • 10
    • 2542455639 scopus 로고    scopus 로고
    • Survival of children with sickle cell disease
    • Quinn, C.T., Rogers, Z.R., Buchanan, G.R., Survival of children with sickle cell disease. Blood 103 (2004), 4023–4027.
    • (2004) Blood , vol.103 , pp. 4023-4027
    • Quinn, C.T.1    Rogers, Z.R.2    Buchanan, G.R.3
  • 11
    • 34548753905 scopus 로고    scopus 로고
    • Clinical outcomes in children with sickle cell disease living in England: a neonatal cohort in East London
    • Telfer, P., Coen, P., Chakravorty, S., Wilkey, O., Evans, J., Newell, H., et al. Clinical outcomes in children with sickle cell disease living in England: a neonatal cohort in East London. Haematologica 92 (2007), 905–912.
    • (2007) Haematologica , vol.92 , pp. 905-912
    • Telfer, P.1    Coen, P.2    Chakravorty, S.3    Wilkey, O.4    Evans, J.5    Newell, H.6
  • 12
    • 77951712618 scopus 로고    scopus 로고
    • Improved survival of children and adolescents with sickle cell disease
    • Quinn, C.T., Rogers, Z.R., McCavit, T.L., Buchanan, G.R., Improved survival of children and adolescents with sickle cell disease. Blood 115 (2010), 3447–3452.
    • (2010) Blood , vol.115 , pp. 3447-3452
    • Quinn, C.T.1    Rogers, Z.R.2    McCavit, T.L.3    Buchanan, G.R.4
  • 14
    • 0033857950 scopus 로고    scopus 로고
    • Acute clinical events in 299 homozygous sickle cell patients living in France. French study group on sickle cell disease
    • Neonato, M.G., Guilloud-Bataille, M., Beauvais, P., Bégué P., Belloy, M., Benkerrou, M., et al. Acute clinical events in 299 homozygous sickle cell patients living in France. French study group on sickle cell disease. Euro J Haematol 65 (2000), 155–164.
    • (2000) Euro J Haematol , vol.65 , pp. 155-164
    • Neonato, M.G.1    Guilloud-Bataille, M.2    Beauvais, P.3    Bégué, P.4    Belloy, M.5    Benkerrou, M.6
  • 16
    • 0034702282 scopus 로고    scopus 로고
    • Causes and outcomes of the acute chest syndrome in sickle cell disease. National Acute Chest Syndrome Study Group
    • Vichinsky, E.P., Neumayr, L.D., Earles, A.N., Williams, R., Lennette, E.T., Dean, D., et al. Causes and outcomes of the acute chest syndrome in sickle cell disease. National Acute Chest Syndrome Study Group. New Engl J Med 342 (2000), 1855–1865.
    • (2000) New Engl J Med , vol.342 , pp. 1855-1865
    • Vichinsky, E.P.1    Neumayr, L.D.2    Earles, A.N.3    Williams, R.4    Lennette, E.T.5    Dean, D.6
  • 17
    • 0029025475 scopus 로고
    • Effect of hydroxyurea on the frequency of painful crises in sickle cell anemia. Investigators of the Multicenter Study of Hydroxyurea in Sickle Cell Anemia
    • Charache, S., Terrin, M.L., Moore, R.D., Dover, G.J., Barton, F.B., Eckert, S.V., et al. Effect of hydroxyurea on the frequency of painful crises in sickle cell anemia. Investigators of the Multicenter Study of Hydroxyurea in Sickle Cell Anemia. New Engl J Med 332 (1995), 1317–1322.
    • (1995) New Engl J Med , vol.332 , pp. 1317-1322
    • Charache, S.1    Terrin, M.L.2    Moore, R.D.3    Dover, G.J.4    Barton, F.B.5    Eckert, S.V.6
  • 18
    • 77950622293 scopus 로고    scopus 로고
    • The effect of prolonged administration of hydroxyurea on morbidity and mortality in adult patients with sickle cell syndromes: results of a 17-year, single-center trial (LaSHS)
    • Voskaridou, E., Christoulas, D., Bilalis, A., Plata, E., Varvagiannis, K., Stamatopoulos, G., et al. The effect of prolonged administration of hydroxyurea on morbidity and mortality in adult patients with sickle cell syndromes: results of a 17-year, single-center trial (LaSHS). Blood 115 (2010), 2354–2363.
    • (2010) Blood , vol.115 , pp. 2354-2363
    • Voskaridou, E.1    Christoulas, D.2    Bilalis, A.3    Plata, E.4    Varvagiannis, K.5    Stamatopoulos, G.6
  • 20
    • 84942162711 scopus 로고    scopus 로고
    • Survival among children and adults with sickle cell disease in Belgium: benefit from hydroxyurea treatment
    • Le, P.Q., Gulbis, B., Dedeken, L., Dupont, S., Vanderfaeillie, A., Heijmans, C., et al. Survival among children and adults with sickle cell disease in Belgium: benefit from hydroxyurea treatment. Pediatr Blood Cancer 62 (2015), 1956–1961.
    • (2015) Pediatr Blood Cancer , vol.62 , pp. 1956-1961
    • Le, P.Q.1    Gulbis, B.2    Dedeken, L.3    Dupont, S.4    Vanderfaeillie, A.5    Heijmans, C.6
  • 22
    • 77649288154 scopus 로고    scopus 로고
    • Psychosocial impact of sickle cell disorder: perspectives from a Nigerian setting
    • Anie, K.A., Egunjobi, F.E., Akinyanju, O.O., Psychosocial impact of sickle cell disorder: perspectives from a Nigerian setting. Global Health, 6, 2010, 2.
    • (2010) Global Health , vol.6 , pp. 2
    • Anie, K.A.1    Egunjobi, F.E.2    Akinyanju, O.O.3
  • 23
    • 0035942334 scopus 로고    scopus 로고
    • Poor school and cognitive functioning with silent cerebral infarcts and sickle cell disease
    • Schatz, J., Brown, R.T., Pascual, J.M., Hsu, L., DeBaun, M.R., Poor school and cognitive functioning with silent cerebral infarcts and sickle cell disease. Neurology 56 (2001), 1109–1111.
    • (2001) Neurology , vol.56 , pp. 1109-1111
    • Schatz, J.1    Brown, R.T.2    Pascual, J.M.3    Hsu, L.4    DeBaun, M.R.5
  • 24
    • 15844366370 scopus 로고    scopus 로고
    • Cognitive functioning and brain magnetic resonance imaging in children with sickle Cell disease. Neuropsychology Committee of the Cooperative Study of Sickle Cell Disease
    • Armstrong, F.D., Thompson, R.J. Jr., Wang, W., Zimmerman, R., Pegelow, C.H., Miller, S., et al. Cognitive functioning and brain magnetic resonance imaging in children with sickle Cell disease. Neuropsychology Committee of the Cooperative Study of Sickle Cell Disease. Pediatrics 97 (1996), 864–870.
    • (1996) Pediatrics , vol.97 , pp. 864-870
    • Armstrong, F.D.1    Thompson, R.J.2    Wang, W.3    Zimmerman, R.4    Pegelow, C.H.5    Miller, S.6
  • 25
    • 0025939624 scopus 로고
    • Chronic renal failure in sickle cell disease: risk factors, clinical course, and mortality
    • Powars, D.R., Elliott-Mills, D.D., Chan, L., Niland, J., Hiti, A.L., Opas, L.M., et al. Chronic renal failure in sickle cell disease: risk factors, clinical course, and mortality. Ann Int Med 115 (1991), 614–620.
    • (1991) Ann Int Med , vol.115 , pp. 614-620
    • Powars, D.R.1    Elliott-Mills, D.D.2    Chan, L.3    Niland, J.4    Hiti, A.L.5    Opas, L.M.6
  • 26
    • 84867469590 scopus 로고    scopus 로고
    • High 1 year mortality in adults with sickle cell disease and end-stage renal disease
    • McClellan, A.C., Luthi, J.C., Lynch, J.R., Soucie, J.M., Kulkarni, R., Guasch, A., et al. High 1 year mortality in adults with sickle cell disease and end-stage renal disease. Br J Haematol 159 (2012), 360–367.
    • (2012) Br J Haematol , vol.159 , pp. 360-367
    • McClellan, A.C.1    Luthi, J.C.2    Lynch, J.R.3    Soucie, J.M.4    Kulkarni, R.5    Guasch, A.6
  • 27
    • 0027450929 scopus 로고
    • Acute chest syndrome in sickle cell disease: CT evidence of microvascular occlusion
    • Bhalla, M., Abboud, M.R., McLoud, T.C., Shepard, J.A., Munden, M.M., Jackson, S.M., et al. Acute chest syndrome in sickle cell disease: CT evidence of microvascular occlusion. Radiology 187 (1993), 45–49.
    • (1993) Radiology , vol.187 , pp. 45-49
    • Bhalla, M.1    Abboud, M.R.2    McLoud, T.C.3    Shepard, J.A.4    Munden, M.M.5    Jackson, S.M.6
  • 28
    • 0037441758 scopus 로고    scopus 로고
    • Pulmonary hypertension in sickle cell disease: cardiac catheterization results and survival
    • Castro, O., Hoque, M., Brown, B.D., Pulmonary hypertension in sickle cell disease: cardiac catheterization results and survival. Blood 101 (2003), 1257–1261.
    • (2003) Blood , vol.101 , pp. 1257-1261
    • Castro, O.1    Hoque, M.2    Brown, B.D.3
  • 29
    • 0036624892 scopus 로고    scopus 로고
    • Microvascular abnormalities in sickle cell disease: a computer-assisted intravital microscopy study
    • Cheung, A.T., Chen, P.C., Larkin, E.C., Duong, P.L., Ramanujam, S., Tablin, F., et al. Microvascular abnormalities in sickle cell disease: a computer-assisted intravital microscopy study. Blood 99 (2002), 3999–4005.
    • (2002) Blood , vol.99 , pp. 3999-4005
    • Cheung, A.T.1    Chen, P.C.2    Larkin, E.C.3    Duong, P.L.4    Ramanujam, S.5    Tablin, F.6
  • 30
    • 84908601771 scopus 로고    scopus 로고
    • Transfusions for silent cerebral infarcts in sickle cell anemia
    • van der Land, V., Heijboer, H., Fijnvandraat, K., Transfusions for silent cerebral infarcts in sickle cell anemia. New Engl J Med, 371, 2014, 1841.
    • (2014) New Engl J Med , vol.371 , pp. 1841
    • van der Land, V.1    Heijboer, H.2    Fijnvandraat, K.3
  • 31
    • 84957891583 scopus 로고    scopus 로고
    • Hydroxycarbamide versus chronic transfusion for maintenance of transcranial Doppler flow velocities in children with sickle cell anaemia-TCD With Transfusions Changing to Hydroxyurea (TWiTCH): a multicentre, open-label, phase 3, noninferiority trial
    • Ware, R.E., Davis, B.R., Schultz, W.H., Brown, R.C., Aygun, B., Sarnaik, S., et al. Hydroxycarbamide versus chronic transfusion for maintenance of transcranial Doppler flow velocities in children with sickle cell anaemia-TCD With Transfusions Changing to Hydroxyurea (TWiTCH): a multicentre, open-label, phase 3, noninferiority trial. Lancet 387 (2016), 661–670.
    • (2016) Lancet , vol.387 , pp. 661-670
    • Ware, R.E.1    Davis, B.R.2    Schultz, W.H.3    Brown, R.C.4    Aygun, B.5    Sarnaik, S.6
  • 32
    • 84860348352 scopus 로고    scopus 로고
    • Stroke with transfusions changing to hydroxyurea (SWiTCH)
    • Ware, R.E., Helms, R.W., Investigators, S.W., Stroke with transfusions changing to hydroxyurea (SWiTCH). Blood 119 (2012), 3925–3932.
    • (2012) Blood , vol.119 , pp. 3925-3932
    • Ware, R.E.1    Helms, R.W.2    Investigators, S.W.3
  • 33
    • 78751697297 scopus 로고    scopus 로고
    • Silent cerebral infarcts occur despite regular blood transfusion therapy after first strokes in children with sickle cell disease
    • Hulbert, M.L., McKinstry, R.C., Lacey, J.L., Moran, C.J., Panepinto, J.A., Thompson, A.A., et al. Silent cerebral infarcts occur despite regular blood transfusion therapy after first strokes in children with sickle cell disease. Blood 117 (2011), 772–779.
    • (2011) Blood , vol.117 , pp. 772-779
    • Hulbert, M.L.1    McKinstry, R.C.2    Lacey, J.L.3    Moran, C.J.4    Panepinto, J.A.5    Thompson, A.A.6
  • 34
    • 84862778943 scopus 로고    scopus 로고
    • Chronic transfusion practices for prevention of primary stroke in children with sickle cell anemia and abnormal TCD velocities
    • Aygun, B., Wruck, L.M., Schultz, W.H., Mueller, B.U., Brown, C., Luchtman-Jones, L., et al. Chronic transfusion practices for prevention of primary stroke in children with sickle cell anemia and abnormal TCD velocities. Am J Hematol 87 (2012), 428–430.
    • (2012) Am J Hematol , vol.87 , pp. 428-430
    • Aygun, B.1    Wruck, L.M.2    Schultz, W.H.3    Mueller, B.U.4    Brown, C.5    Luchtman-Jones, L.6
  • 36
    • 75749106627 scopus 로고    scopus 로고
    • The risk of transfusion-transmitted infections in subSaharan Africa
    • Jayaraman, S., Chalabi, Z., Perel, P., Guerriero, C., Roberts, I., The risk of transfusion-transmitted infections in subSaharan Africa. Transfusion 50 (2010), 433–442.
    • (2010) Transfusion , vol.50 , pp. 433-442
    • Jayaraman, S.1    Chalabi, Z.2    Perel, P.3    Guerriero, C.4    Roberts, I.5
  • 37
    • 84876435847 scopus 로고    scopus 로고
    • Mortality rates and age at death from sickle cell disease: U.S., 1979–2005
    • Lanzkron, S., Carroll, C.P., Haywood, C. Jr., Mortality rates and age at death from sickle cell disease: U.S., 1979–2005. Public Health Rep 128 (2013), 110–116.
    • (2013) Public Health Rep , vol.128 , pp. 110-116
    • Lanzkron, S.1    Carroll, C.P.2    Haywood, C.3
  • 38
    • 27944496081 scopus 로고    scopus 로고
    • Outcome of sickle cell anemia: a 4-decade observational study of 1056 patients
    • Powars, D.R., Chan, L.S., Hiti, A., Ramicone, E., Johnson, C., Outcome of sickle cell anemia: a 4-decade observational study of 1056 patients. Medicine 84 (2005), 363–376.
    • (2005) Medicine , vol.84 , pp. 363-376
    • Powars, D.R.1    Chan, L.S.2    Hiti, A.3    Ramicone, E.4    Johnson, C.5
  • 40
    • 85015934863 scopus 로고    scopus 로고
    • Sickle cell disease: an international survey of results of HLA-identical sibling hematopoietic stem cell transplantation
    • Gluckman, E., Cappelli, B., Bernaudin, F., Labopin, M., Volt, F., Carreras, J., et al. Sickle cell disease: an international survey of results of HLA-identical sibling hematopoietic stem cell transplantation. Blood, 2016, 10.1182/blood-2016-10-745711.
    • (2016) Blood
    • Gluckman, E.1    Cappelli, B.2    Bernaudin, F.3    Labopin, M.4    Volt, F.5    Carreras, J.6
  • 41
    • 75149170038 scopus 로고    scopus 로고
    • Pulmonary, gonadal, and central nervous system status after bone marrow transplantation for sickle cell disease
    • Walters, M.C., Hardy, K., Edwards, S., Adamkiewicz, T., Barkovich, J., Bernaudin, F., et al. Pulmonary, gonadal, and central nervous system status after bone marrow transplantation for sickle cell disease. Biol Blood Marrow Transplant 16 (2010), 263–272.
    • (2010) Biol Blood Marrow Transplant , vol.16 , pp. 263-272
    • Walters, M.C.1    Hardy, K.2    Edwards, S.3    Adamkiewicz, T.4    Barkovich, J.5    Bernaudin, F.6
  • 42
    • 0031870487 scopus 로고    scopus 로고
    • Haematopoietic stem cell transplantation for sickle cell anaemia: the first 50 patients transplanted in Belgium
    • Vermylen, C., Cornu, G., Ferster, A., Brichard, B., Niane, J., Ferrant, A., et al. Haematopoietic stem cell transplantation for sickle cell anaemia: the first 50 patients transplanted in Belgium. Bone Marrow Transplant 22 (1998), 1–6.
    • (1998) Bone Marrow Transplant , vol.22 , pp. 1-6
    • Vermylen, C.1    Cornu, G.2    Ferster, A.3    Brichard, B.4    Niane, J.5    Ferrant, A.6
  • 43
    • 84875254453 scopus 로고    scopus 로고
    • Stem cell transplantation after reduced-intensity conditioning for sickle cell disease
    • Matthes-Martin, S., Lawitschka, A., Fritsch, G., Lion, T., Grimm, B., Breuer, S., et al. Stem cell transplantation after reduced-intensity conditioning for sickle cell disease. Eur J Haematol 90 (2013), 308–312.
    • (2013) Eur J Haematol , vol.90 , pp. 308-312
    • Matthes-Martin, S.1    Lawitschka, A.2    Fritsch, G.3    Lion, T.4    Grimm, B.5    Breuer, S.6
  • 44
    • 33846438578 scopus 로고    scopus 로고
    • Effect of myeloablative bone marrow transplantation on growth in children with sickle cell anaemia: results of the multicenter study of haematopoietic cell transplantation for sickle cell anaemia
    • Eggleston, B., Patience, M., Edwards, S., Adamkiewicz, T., Buchanan, G.R., Davies, S.C., et al. Effect of myeloablative bone marrow transplantation on growth in children with sickle cell anaemia: results of the multicenter study of haematopoietic cell transplantation for sickle cell anaemia. Br J Haematol 136 (2007), 673–676.
    • (2007) Br J Haematol , vol.136 , pp. 673-676
    • Eggleston, B.1    Patience, M.2    Edwards, S.3    Adamkiewicz, T.4    Buchanan, G.R.5    Davies, S.C.6
  • 46
    • 84954230957 scopus 로고    scopus 로고
    • Successful matched sibling donor marrow transplantation following reduced intensity conditioning in children with hemoglobinopathies
    • King, A.A., Kamani, N., Bunin, N., Sahdev, I., Brochstein, J., Hayashi, R.J., et al. Successful matched sibling donor marrow transplantation following reduced intensity conditioning in children with hemoglobinopathies. Am J Hematol 90 (2015), 1093–1098.
    • (2015) Am J Hematol , vol.90 , pp. 1093-1098
    • King, A.A.1    Kamani, N.2    Bunin, N.3    Sahdev, I.4    Brochstein, J.5    Hayashi, R.J.6
  • 47
    • 71849118976 scopus 로고    scopus 로고
    • Allogeneic hematopoietic stem-cell transplantation for sickle cell disease
    • Hsieh, M.M., Kang, E.M., Fitzhugh, C.D., Link, B., Bolan, C.D., Kurlander, R., et al. Allogeneic hematopoietic stem-cell transplantation for sickle cell disease. N Engl J Med 361 (2009), 2309–2317.
    • (2009) N Engl J Med , vol.361 , pp. 2309-2317
    • Hsieh, M.M.1    Kang, E.M.2    Fitzhugh, C.D.3    Link, B.4    Bolan, C.D.5    Kurlander, R.6
  • 48
    • 34948830175 scopus 로고    scopus 로고
    • Long-term results of related myeloablative stem-cell transplantation to cure sickle cell disease
    • Bernaudin, F., Socie, G., Kuentz, M., Chevret, S., Duval, M., Bertrand, Y., et al. Long-term results of related myeloablative stem-cell transplantation to cure sickle cell disease. Blood 110 (2007), 2749–2756.
    • (2007) Blood , vol.110 , pp. 2749-2756
    • Bernaudin, F.1    Socie, G.2    Kuentz, M.3    Chevret, S.4    Duval, M.5    Bertrand, Y.6
  • 49
    • 0036045174 scopus 로고    scopus 로고
    • Nonmyeloablative bone marrow transplantation from partially HLA-mismatched related donors using posttransplantation cyclophosphamide
    • O'Donnell, P.V., Luznik, L., Jones, R.J., Vogelsang, G.B., Leffell, M.S., Phelps, M., et al. Nonmyeloablative bone marrow transplantation from partially HLA-mismatched related donors using posttransplantation cyclophosphamide. Biol Blood Marrow Transplant 8 (2002), 377–386.
    • (2002) Biol Blood Marrow Transplant , vol.8 , pp. 377-386
    • O'Donnell, P.V.1    Luznik, L.2    Jones, R.J.3    Vogelsang, G.B.4    Leffell, M.S.5    Phelps, M.6
  • 50
    • 84904566576 scopus 로고    scopus 로고
    • HLA match likelihoods for hematopoietic stem-cell grafts in the U.S. registry
    • Gragert, L., Eapen, M., Williams, E., Freeman, J., Spellman, S., Baitty, R., et al. HLA match likelihoods for hematopoietic stem-cell grafts in the U.S. registry. N Engl J Med 371 (2014), 339–348.
    • (2014) N Engl J Med , vol.371 , pp. 339-348
    • Gragert, L.1    Eapen, M.2    Williams, E.3    Freeman, J.4    Spellman, S.5    Baitty, R.6
  • 51
    • 85015019083 scopus 로고    scopus 로고
    • A trial of unrelated donor marrow transplantation for children with severe sickle cell disease
    • Shenoy, S., Eapen, M., Panepinto, J.A., Logan, B.R., Wu, J., Abraham, A., et al. A trial of unrelated donor marrow transplantation for children with severe sickle cell disease. Blood 128 (2016), 2561–2567.
    • (2016) Blood , vol.128 , pp. 2561-2567
    • Shenoy, S.1    Eapen, M.2    Panepinto, J.A.3    Logan, B.R.4    Wu, J.5    Abraham, A.6
  • 53
    • 84864005843 scopus 로고    scopus 로고
    • Unrelated donor cord blood transplantation for children with severe sickle cell disease: results of one cohort from the phase II study from the Blood and Marrow Transplant Clinical Trials Network (BMT CTN)
    • Kamani, N.R., Walters, M.C., Carter, S., Aquino, V., Brochstein, J.A., Chaudhury, S., et al. Unrelated donor cord blood transplantation for children with severe sickle cell disease: results of one cohort from the phase II study from the Blood and Marrow Transplant Clinical Trials Network (BMT CTN). Biol Blood Marrow Transplant 18 (2012), 1265–1272.
    • (2012) Biol Blood Marrow Transplant , vol.18 , pp. 1265-1272
    • Kamani, N.R.1    Walters, M.C.2    Carter, S.3    Aquino, V.4    Brochstein, J.A.5    Chaudhury, S.6
  • 54
    • 84869813639 scopus 로고    scopus 로고
    • HLA-haploidentical bone marrow transplantation with posttransplant cyclophosphamide expands the donor pool for patients with sickle cell disease
    • Bolaños-Meade, J., et al. HLA-haploidentical bone marrow transplantation with posttransplant cyclophosphamide expands the donor pool for patients with sickle cell disease. Blood 120 (2012), 4285–4291.
    • (2012) Blood , vol.120 , pp. 4285-4291
    • Bolaños-Meade, J.1
  • 55
    • 84876333389 scopus 로고    scopus 로고
    • Long-term outcome and evaluation of organ function in pediatric patients undergoing haploidentical and matched related hematopoietic cell transplantation for sickle cell disease
    • Dallas, M.H., Triplett, B., Shook, D.R., Hartford, C., Srinivasan, A., Laver, J., et al. Long-term outcome and evaluation of organ function in pediatric patients undergoing haploidentical and matched related hematopoietic cell transplantation for sickle cell disease. Biol Blood Marrow Transplant 19 (2013), 820–830.
    • (2013) Biol Blood Marrow Transplant , vol.19 , pp. 820-830
    • Dallas, M.H.1    Triplett, B.2    Shook, D.R.3    Hartford, C.4    Srinivasan, A.5    Laver, J.6
  • 56
    • 84924278004 scopus 로고    scopus 로고
    • Health-related quality of life after allogeneic hematopoietic stem cell transplantation for sickle cell disease
    • Bhatia, M., Kolva, E., Cimini, L., Jin, Z., Satwani, P., Savone, M., et al. Health-related quality of life after allogeneic hematopoietic stem cell transplantation for sickle cell disease. Biol Blood Marrow Transplant 21 (2015), 666–672.
    • (2015) Biol Blood Marrow Transplant , vol.21 , pp. 666-672
    • Bhatia, M.1    Kolva, E.2    Cimini, L.3    Jin, Z.4    Satwani, P.5    Savone, M.6
  • 57
    • 84904243199 scopus 로고    scopus 로고
    • Targeted Busulfan therapy with a steady-state concentration of 600–700 ng/mL in patients with sickle cell disease receiving HLA-identical sibling bone marrow transplant
    • Maheshwari, S., Kassim, A., Yeh, R.F., Domm, J., Calder, C., Evans, M., et al. Targeted Busulfan therapy with a steady-state concentration of 600–700 ng/mL in patients with sickle cell disease receiving HLA-identical sibling bone marrow transplant. Bone Marrow Transp 49 (2014), 366–369.
    • (2014) Bone Marrow Transp , vol.49 , pp. 366-369
    • Maheshwari, S.1    Kassim, A.2    Yeh, R.F.3    Domm, J.4    Calder, C.5    Evans, M.6
  • 59
    • 84912059866 scopus 로고    scopus 로고
    • Hematopoietic stem cell transplantation for patients with sickle cell disease: progress and future directions
    • Fitzhugh, C.D., Abraham, A.A., Tisdale, J.F., Hsieh, M.M., Hematopoietic stem cell transplantation for patients with sickle cell disease: progress and future directions. Hematol Oncol Clin North Am 28 (2014), 1171–1185.
    • (2014) Hematol Oncol Clin North Am , vol.28 , pp. 1171-1185
    • Fitzhugh, C.D.1    Abraham, A.A.2    Tisdale, J.F.3    Hsieh, M.M.4
  • 60
    • 84930432811 scopus 로고    scopus 로고
    • HLA-haploidentical blood or marrow transplantation with high-dose, posttransplantation cyclophosphamide
    • Fuchs, E.J., HLA-haploidentical blood or marrow transplantation with high-dose, posttransplantation cyclophosphamide. Bone Marrow Transplant 50:Suppl. 2 (2015), S31–6.
    • (2015) Bone Marrow Transplant , vol.50 , pp. S31-6
    • Fuchs, E.J.1
  • 61
    • 84899721999 scopus 로고    scopus 로고
    • Hematopoietic stem cell transplantation in thalassemia major and sickle cell disease: indications and management recommendations from an international expert panel
    • Angelucci, E., Matthew-Martin, S., Baronciani, D., Bernaudin, F., Bonanomi, S., Cappellini, M.D., et al. Hematopoietic stem cell transplantation in thalassemia major and sickle cell disease: indications and management recommendations from an international expert panel. Haematologica 99 (2014), 811–820.
    • (2014) Haematologica , vol.99 , pp. 811-820
    • Angelucci, E.1    Matthew-Martin, S.2    Baronciani, D.3    Bernaudin, F.4    Bonanomi, S.5    Cappellini, M.D.6


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.