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Volumn 16, Issue 5, 2017, Pages 573-578

A multiple reader scoring system for Nasal Potential Difference parameters

Author keywords

CFTR; Clinical trial outcomes; Nasal Potential Difference

Indexed keywords

AMILORIDE; CHLORIDE; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; ISOPRENALINE; SODIUM;

EID: 85018344290     PISSN: 15691993     EISSN: 18735010     Source Type: Journal    
DOI: 10.1016/j.jcf.2017.04.011     Document Type: Article
Times cited : (10)

References (28)
  • 1
    • 0019490443 scopus 로고
    • Measurements of nasal transepithelial electric potential differences in normal human subjects in vivo
    • Knowles, M.R., Carson, J.L., Collier, A.M., Gatzy, J.T., Boucher, R.C., Measurements of nasal transepithelial electric potential differences in normal human subjects in vivo. Am Rev Respir Dis 124:4 (1981), 484–490.
    • (1981) Am Rev Respir Dis , vol.124 , Issue.4 , pp. 484-490
    • Knowles, M.R.1    Carson, J.L.2    Collier, A.M.3    Gatzy, J.T.4    Boucher, R.C.5
  • 2
    • 0019985202 scopus 로고
    • Measurements of transepithelial electric potential differences in the trachea and bronchi of human subjects in vivo
    • Knowles, M.R., Buntin, W.H., Bromberg, P.A., Gatzy, J.T., Boucher, R.C., Measurements of transepithelial electric potential differences in the trachea and bronchi of human subjects in vivo. Am Rev Respir Dis 126:1 (1982), 108–112.
    • (1982) Am Rev Respir Dis , vol.126 , Issue.1 , pp. 108-112
    • Knowles, M.R.1    Buntin, W.H.2    Bromberg, P.A.3    Gatzy, J.T.4    Boucher, R.C.5
  • 4
    • 2442453783 scopus 로고    scopus 로고
    • Standardized procedure for measurement of nasal potential difference: an outcome measure in multicenter cystic fibrosis clinical trials
    • Standaert, T.A., Boitano, L., Emerson, J., Milgram, L.J., Konstan, M.W., Hunter, J., et al. Standardized procedure for measurement of nasal potential difference: an outcome measure in multicenter cystic fibrosis clinical trials. Pediatr Pulmonol 37:5 (2004), 385–392.
    • (2004) Pediatr Pulmonol , vol.37 , Issue.5 , pp. 385-392
    • Standaert, T.A.1    Boitano, L.2    Emerson, J.3    Milgram, L.J.4    Konstan, M.W.5    Hunter, J.6
  • 6
    • 0022973473 scopus 로고
    • + transport in cystic fibrosis respiratory epithelia. Abnormal basal rate and response to adenylate cyclase activation
    • + transport in cystic fibrosis respiratory epithelia. Abnormal basal rate and response to adenylate cyclase activation. J Clin Invest 78:5 (1986), 1245–1252.
    • (1986) J Clin Invest , vol.78 , Issue.5 , pp. 1245-1252
    • Boucher, R.C.1    Stutts, M.J.2    Knowles, M.R.3    Cantley, L.4    Gatzy, J.T.5
  • 7
    • 0022638101 scopus 로고
    • Increased nasal potential difference and amiloride sensitivity in neonates with cystic fibrosis
    • Gowen, C.W., Lawson, E.E., Gingras-Leatherman, J., Gatzy, J.T., Boucher, R.C., Knowles, M.R., Increased nasal potential difference and amiloride sensitivity in neonates with cystic fibrosis. J Pediatr 108:4 (1986), 517–521.
    • (1986) J Pediatr , vol.108 , Issue.4 , pp. 517-521
    • Gowen, C.W.1    Lawson, E.E.2    Gingras-Leatherman, J.3    Gatzy, J.T.4    Boucher, R.C.5    Knowles, M.R.6
  • 8
    • 0020610435 scopus 로고
    • Abnormal ion permeation through cystic fibrosis respiratory epithelium
    • Knowles, M.R., Stutts, M.J., Spock, A., Fischer, N., Gatzy, J.T., Boucher, R.C., Abnormal ion permeation through cystic fibrosis respiratory epithelium. Science 221:4615 (1983), 1067–1070.
    • (1983) Science , vol.221 , Issue.4615 , pp. 1067-1070
    • Knowles, M.R.1    Stutts, M.J.2    Spock, A.3    Fischer, N.4    Gatzy, J.T.5    Boucher, R.C.6
  • 9
    • 0025874599 scopus 로고
    • Activation by extracellular nucleotides of chloride secretion in the airway epithelia of patients with cystic fibrosis
    • Knowles, M.R., Clarke, L.L., Boucher, R.C., Activation by extracellular nucleotides of chloride secretion in the airway epithelia of patients with cystic fibrosis. N Engl J Med 325:8 (1991), 533–538.
    • (1991) N Engl J Med , vol.325 , Issue.8 , pp. 533-538
    • Knowles, M.R.1    Clarke, L.L.2    Boucher, R.C.3
  • 10
    • 78549279173 scopus 로고    scopus 로고
    • Effect of VX-770 in persons with cystic fibrosis and the G551D-CFTR mutation
    • Accurso, F.J., Rowe, S.M., Clancy, J.P., Boyle, M.P., Dunitz, J.M., Durie, P.R., et al. Effect of VX-770 in persons with cystic fibrosis and the G551D-CFTR mutation. N Engl J Med 363:21 (2010), 1991–2003.
    • (2010) N Engl J Med , vol.363 , Issue.21 , pp. 1991-2003
    • Accurso, F.J.1    Rowe, S.M.2    Clancy, J.P.3    Boyle, M.P.4    Dunitz, J.M.5    Durie, P.R.6
  • 11
    • 84855202429 scopus 로고    scopus 로고
    • Results of a phase IIa study of VX-809, an investigational CFTR corrector compound, in subjects with cystic fibrosis homozygous for the F508del-CFTR mutation
    • Clancy, J.P., Rowe, S.M., Accurso, F.J., Aitken, M.L., Amin, R.S., Ashlock, M.A., et al. Results of a phase IIa study of VX-809, an investigational CFTR corrector compound, in subjects with cystic fibrosis homozygous for the F508del-CFTR mutation. Thorax 67:1 (2012), 12–18.
    • (2012) Thorax , vol.67 , Issue.1 , pp. 12-18
    • Clancy, J.P.1    Rowe, S.M.2    Accurso, F.J.3    Aitken, M.L.4    Amin, R.S.5    Ashlock, M.A.6
  • 12
    • 34347224756 scopus 로고    scopus 로고
    • No detectable improvements in cystic fibrosis transmembrane conductance regulator by nasal aminoglycosides in patients with cystic fibrosis with stop mutations
    • Clancy, J.P., Rowe, S.M., Bebok, Z., Aitken, M.L., Gibson, R., Zeitlin, P., et al. No detectable improvements in cystic fibrosis transmembrane conductance regulator by nasal aminoglycosides in patients with cystic fibrosis with stop mutations. Am J Respir Cell Mol Biol 37:1 (2007), 57–66.
    • (2007) Am J Respir Cell Mol Biol , vol.37 , Issue.1 , pp. 57-66
    • Clancy, J.P.1    Rowe, S.M.2    Bebok, Z.3    Aitken, M.L.4    Gibson, R.5    Zeitlin, P.6
  • 13
    • 79960187095 scopus 로고    scopus 로고
    • Chronic ataluren (PTC124) treatment of nonsense mutation cystic fibrosis
    • Wilschanski, M., Miller, L.L., Shoseyov, D., Blau, H., Rivlin, J., Aviram, M., et al. Chronic ataluren (PTC124) treatment of nonsense mutation cystic fibrosis. Eur Respir J 38:1 (2011), 59–69.
    • (2011) Eur Respir J , vol.38 , Issue.1 , pp. 59-69
    • Wilschanski, M.1    Miller, L.L.2    Shoseyov, D.3    Blau, H.4    Rivlin, J.5    Aviram, M.6
  • 14
    • 0028113998 scopus 로고
    • Gene therapy for cystic fibrosis using E1-deleted adenovirus: a phase I trial in the nasal cavity. The University of North Carolina at Chapel Hill
    • Boucher, R.C., Knowles, M.R., Johnson, L.G., Olsen, J.C., Pickles, R., Wilson, J.M., et al. Gene therapy for cystic fibrosis using E1-deleted adenovirus: a phase I trial in the nasal cavity. The University of North Carolina at Chapel Hill. Hum Gene Ther 5:5 (1994), 615–639.
    • (1994) Hum Gene Ther , vol.5 , Issue.5 , pp. 615-639
    • Boucher, R.C.1    Knowles, M.R.2    Johnson, L.G.3    Olsen, J.C.4    Pickles, R.5    Wilson, J.M.6
  • 15
    • 0029100239 scopus 로고
    • A controlled study of adenoviral-vector-mediated gene transfer in the nasal epithelium of patients with cystic fibrosis
    • Knowles, M.R., Hohneker, K.W., Zhou, Z., Olsen, J.C., Noah, T.L., Hu, P.C., et al. A controlled study of adenoviral-vector-mediated gene transfer in the nasal epithelium of patients with cystic fibrosis. N Engl J Med 333:13 (1995), 823–831.
    • (1995) N Engl J Med , vol.333 , Issue.13 , pp. 823-831
    • Knowles, M.R.1    Hohneker, K.W.2    Zhou, Z.3    Olsen, J.C.4    Noah, T.L.5    Hu, P.C.6
  • 16
    • 0033660570 scopus 로고    scopus 로고
    • Safety and biological efficacy of a lipid-CFTR complex for gene transfer in the nasal epithelium of adult patients with cystic fibrosis
    • Noone, P.G., Hohneker, K.W., Zhou, Z., Johnson, L.G., Foy, C., Gipson, C., et al. Safety and biological efficacy of a lipid-CFTR complex for gene transfer in the nasal epithelium of adult patients with cystic fibrosis. Mol Ther 1:1 (2000), 105–114.
    • (2000) Mol Ther , vol.1 , Issue.1 , pp. 105-114
    • Noone, P.G.1    Hohneker, K.W.2    Zhou, Z.3    Johnson, L.G.4    Foy, C.5    Gipson, C.6
  • 17
    • 84949035059 scopus 로고    scopus 로고
    • A phase I/IIa safety and efficacy study of nebulized liposome-mediated gene therapy for cystic fibrosis supports a multidose trial
    • Alton, E.W., Boyd, A.C., Porteous, D.J., Davies, G., Davies, J.C., Griesenbach, U., et al. A phase I/IIa safety and efficacy study of nebulized liposome-mediated gene therapy for cystic fibrosis supports a multidose trial. Am J Respir Crit Care Med 192:11 (2015), 1389–1392.
    • (2015) Am J Respir Crit Care Med , vol.192 , Issue.11 , pp. 1389-1392
    • Alton, E.W.1    Boyd, A.C.2    Porteous, D.J.3    Davies, G.4    Davies, J.C.5    Griesenbach, U.6
  • 18
    • 84941179388 scopus 로고    scopus 로고
    • Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial
    • Alton, E.W., Armstrong, D.K., Ashby, D., Bayfield, K.J., Bilton, D., Bloomfield, E.V., et al. Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial. Lancet Respir Med 3:9 (2015), 684–691.
    • (2015) Lancet Respir Med , vol.3 , Issue.9 , pp. 684-691
    • Alton, E.W.1    Armstrong, D.K.2    Ashby, D.3    Bayfield, K.J.4    Bilton, D.5    Bloomfield, E.V.6
  • 19
    • 0026002078 scopus 로고
    • Aerosolized amiloride as treatment of cystic fibrosis lung disease: a pilot study
    • [discussion 29-32]
    • Knowles, M.R., Church, N.L., Waltner, W.E., Yankaskas, J.R., Gilligan, P., King, M., et al. Aerosolized amiloride as treatment of cystic fibrosis lung disease: a pilot study. Adv Exp Med Biol 290 (1991), 119–128 [discussion 29-32].
    • (1991) Adv Exp Med Biol , vol.290 , pp. 119-128
    • Knowles, M.R.1    Church, N.L.2    Waltner, W.E.3    Yankaskas, J.R.4    Gilligan, P.5    King, M.6
  • 20
    • 0025236867 scopus 로고
    • A pilot study of aerosolized amiloride for the treatment of lung disease in cystic fibrosis
    • Knowles, M.R., Church, N.L., Waltner, W.E., Yankaskas, J.R., Gilligan, P., King, M., et al. A pilot study of aerosolized amiloride for the treatment of lung disease in cystic fibrosis. N Engl J Med 322:17 (1990), 1189–1194.
    • (1990) N Engl J Med , vol.322 , Issue.17 , pp. 1189-1194
    • Knowles, M.R.1    Church, N.L.2    Waltner, W.E.3    Yankaskas, J.R.4    Gilligan, P.5    King, M.6
  • 21
    • 0031862236 scopus 로고    scopus 로고
    • Effects of topically delivered benzamil and amiloride on nasal potential difference in cystic fibrosis
    • Hofmann, T., Stutts, M.J., Ziersch, A., Ruckes, C., Weber, W.M., Knowles, M.R., et al. Effects of topically delivered benzamil and amiloride on nasal potential difference in cystic fibrosis. Am J Respir Crit Care Med 157:6 Pt 1 (1998), 1844–1849.
    • (1998) Am J Respir Crit Care Med , vol.157 , Issue.6 , pp. 1844-1849
    • Hofmann, T.1    Stutts, M.J.2    Ziersch, A.3    Ruckes, C.4    Weber, W.M.5    Knowles, M.R.6
  • 22
    • 84880067253 scopus 로고    scopus 로고
    • Reduced sodium transport with nasal administration of the prostasin inhibitor camostat in subjects with cystic fibrosis
    • Rowe, S.M., Reeves, G., Hathorne, H., Solomon, G.M., Abbi, S., Renard, D., et al. Reduced sodium transport with nasal administration of the prostasin inhibitor camostat in subjects with cystic fibrosis. Chest 144:1 (2013), 200–207.
    • (2013) Chest , vol.144 , Issue.1 , pp. 200-207
    • Rowe, S.M.1    Reeves, G.2    Hathorne, H.3    Solomon, G.M.4    Abbi, S.5    Renard, D.6
  • 23
    • 84880774140 scopus 로고    scopus 로고
    • Optimizing nasal potential difference analysis for CFTR modulator development: assessment of ivacaftor in CF subjects with the G551D-CFTR mutation
    • Rowe, S.M., Liu, B., Hill, A., Hathorne, H., Cohen, M., Beamer, J.R., et al. Optimizing nasal potential difference analysis for CFTR modulator development: assessment of ivacaftor in CF subjects with the G551D-CFTR mutation. PLoS One, 8(7), 2013, e66955.
    • (2013) PLoS One , vol.8 , Issue.7
    • Rowe, S.M.1    Liu, B.2    Hill, A.3    Hathorne, H.4    Cohen, M.5    Beamer, J.R.6
  • 24
    • 77957827856 scopus 로고    scopus 로고
    • An international randomized multicenter comparison of nasal potential difference techniques
    • Solomon, G.M., Konstan, M.W., Wilschanski, M., Billings, J., Sermet-Gaudelus, I., Accurso, F., et al. An international randomized multicenter comparison of nasal potential difference techniques. Chest 138:4 (2010), 919–928.
    • (2010) Chest , vol.138 , Issue.4 , pp. 919-928
    • Solomon, G.M.1    Konstan, M.W.2    Wilschanski, M.3    Billings, J.4    Sermet-Gaudelus, I.5    Accurso, F.6
  • 25
    • 80052340084 scopus 로고    scopus 로고
    • Nasal potential difference measurements to assess CFTR ion channel activity
    • Rowe, S.M., Clancy, J.P., Wilschanski, M., Nasal potential difference measurements to assess CFTR ion channel activity. Methods Mol Biol 741 (2011), 69–86.
    • (2011) Methods Mol Biol , vol.741 , pp. 69-86
    • Rowe, S.M.1    Clancy, J.P.2    Wilschanski, M.3
  • 26
    • 47049115524 scopus 로고    scopus 로고
    • Guidelines for diagnosis of cystic fibrosis in newborns through older adults: Cystic Fibrosis Foundation consensus report
    • Farrell, P.M., Rosenstein, B.J., White, T.B., Accurso, F.J., Castellani, C., Cutting, G.R., et al. Guidelines for diagnosis of cystic fibrosis in newborns through older adults: Cystic Fibrosis Foundation consensus report. J Pediatr 153:2 (2008), S4–S14.
    • (2008) J Pediatr , vol.153 , Issue.2 , pp. S4-S14
    • Farrell, P.M.1    Rosenstein, B.J.2    White, T.B.3    Accurso, F.J.4    Castellani, C.5    Cutting, G.R.6
  • 27
    • 0017360990 scopus 로고
    • The measurement of observer agreement for categorical data
    • Landis, J.R., Koch, G.G., The measurement of observer agreement for categorical data. Biometrics 33:1 (1977), 159–174.
    • (1977) Biometrics , vol.33 , Issue.1 , pp. 159-174
    • Landis, J.R.1    Koch, G.G.2
  • 28
    • 84890429584 scopus 로고    scopus 로고
    • Nasal potential difference measurements in diagnosis of cystic fibrosis: an international survey
    • Naehrlich, L., Ballmann, M., Davies, J., Derichs, N., Gonska, T., Hjelte, L., et al. Nasal potential difference measurements in diagnosis of cystic fibrosis: an international survey. J Cyst Fibros 13:1 (2014), 24–28.
    • (2014) J Cyst Fibros , vol.13 , Issue.1 , pp. 24-28
    • Naehrlich, L.1    Ballmann, M.2    Davies, J.3    Derichs, N.4    Gonska, T.5    Hjelte, L.6


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