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Volumn 11, Issue 1, 2016, Pages

The availability and affordability of orphan drugs for rare diseases in China

Author keywords

Affordability; Availability; China; Orphan drug; Price; Rare disease

Indexed keywords

HOMOHARRINGTONINE; ORPHAN DRUG;

EID: 85007414204     PISSN: None     EISSN: 17501172     Source Type: Journal    
DOI: 10.1186/s13023-016-0392-4     Document Type: Article
Times cited : (61)

References (40)
  • 1
    • 84873079257 scopus 로고    scopus 로고
    • Orphan drugs: The regulatory environment
    • Franco P. Orphan drugs: the regulatory environment. Drug Discov Today. 2013;18(3-4):163-72.
    • (2013) Drug Discov Today , vol.18 , Issue.3-4 , pp. 163-172
    • Franco, P.1
  • 2
    • 79960002064 scopus 로고    scopus 로고
    • Accelerating access to treatments for rare diseases
    • Dunoyer M. Accelerating access to treatments for rare diseases. Nat Rev Drug Discov. 2011;10(7):475-6.
    • (2011) Nat Rev Drug Discov. , vol.10 , Issue.7 , pp. 475-476
    • Dunoyer, M.1
  • 3
    • 44849143056 scopus 로고    scopus 로고
    • Why rare diseases are an important medical and social issue
    • Schieppati A, Henter JI, Daina E, Aperia A. Why rare diseases are an important medical and social issue. Lancet. 2008;371(9629):2039-41.
    • (2008) Lancet , vol.371 , Issue.9629 , pp. 2039-2041
    • Schieppati, A.1    Henter, J.I.2    Daina, E.3    Aperia, A.4
  • 5
    • 84876743099 scopus 로고    scopus 로고
    • Orphan drugs, orphan diseases. The first decade of orphan drug legislation in the EU
    • Joppi R, Bertele V, Garattini S. Orphan drugs, orphan diseases. The first decade of orphan drug legislation in the EU. Eur J Clin Pharmacol. 2013;69(4):1009-24.
    • (2013) Eur J Clin Pharmacol. , vol.69 , Issue.4 , pp. 1009-1024
    • Joppi, R.1    Bertele, V.2    Garattini, S.3
  • 8
    • 84945919084 scopus 로고    scopus 로고
    • Current progress in the management of rare diseases and orphan drugs in China
    • Gong S, Jin S. Current progress in the management of rare diseases and orphan drugs in China. Intractable Rare Dis Res. 2012;1(2):45-52.
    • (2012) Intractable Rare Dis Res. , vol.1 , Issue.2 , pp. 45-52
    • Gong, S.1    Jin, S.2
  • 10
    • 58149522302 scopus 로고    scopus 로고
    • Medicine prices, availability, and affordability in 36 developing and middle-income countries: A secondary analysis
    • Cameron A, Ewen M, Ross-Degnan D, Ball D, Laing R. Medicine prices, availability, and affordability in 36 developing and middle-income countries: a secondary analysis. Lancet. 2009;373(9659):240-9.
    • (2009) Lancet , vol.373 , Issue.9659 , pp. 240-249
    • Cameron, A.1    Ewen, M.2    Ross-Degnan, D.3    Ball, D.4    Laing, R.5
  • 11
    • 77954736394 scopus 로고    scopus 로고
    • Prices, availability and affordability of essential medicines in rural areas of Hubei Province, China
    • Yang H, Dib HH, Zhu M, Qi G, Zhang X. Prices, availability and affordability of essential medicines in rural areas of Hubei Province, China. Health Policy Plan. 2010;25(3):219-29.
    • (2010) Health Policy Plan , vol.25 , Issue.3 , pp. 219-229
    • Yang, H.1    Dib, H.H.2    Zhu, M.3    Qi, G.4    Zhang, X.5
  • 12
    • 84925490315 scopus 로고    scopus 로고
    • Medicine prices, availability, and affordability in the Shaanxi Province in China: Implications for the future
    • Jiang M, Zhou Z, Wu L, et al. Medicine prices, availability, and affordability in the Shaanxi Province in China: implications for the future. Int J Clin Pharm. 2015;37(1):12-7.
    • (2015) Int J Clin Pharm. , vol.37 , Issue.1 , pp. 12-17
    • Jiang, M.1    Zhou, Z.2    Wu, L.3
  • 13
    • 85007490066 scopus 로고    scopus 로고
    • Accessed 17 December 2015
    • World Health Organization. Description of essential medicines. 2015. http://apps.who.int/medicinedocs/en/d/Js4875e/5.2.html. Accessed 17 December 2015.
    • (2015) Description of Essential Medicines
  • 14
    • 84938384222 scopus 로고    scopus 로고
    • An appeal to the global health community for a tripartite innovation: An "Essential diagnostics list," "Health in all policies," and "See-through 21(st) century science and ethics"
    • Dove ES, Barlas IO, Birch K, et al. An Appeal to the Global Health Community for a Tripartite Innovation: An "Essential Diagnostics List," "Health in All Policies," and "See-Through 21(st) Century Science and Ethics". Omics. 2015;19(8):435-42.
    • (2015) Omics , vol.19 , Issue.8 , pp. 435-442
    • Dove, E.S.1    Barlas, I.O.2    Birch, K.3
  • 15
    • 78650240029 scopus 로고    scopus 로고
    • Availability of and access to orphan drugs: An international comparison of pharmaceutical treatments for pulmonary arterial hypertension, fabry disease, hereditary angioedema and chronic myeloid leukaemia
    • Blankart CR, Stargardt T, Schreyogg J. Availability of and access to orphan drugs: an international comparison of pharmaceutical treatments for pulmonary arterial hypertension, Fabry disease, hereditary angioedema and chronic myeloid leukaemia. Pharmacoeconomics. 2011;29(1):63-82.
    • (2011) Pharmacoeconomics , vol.29 , Issue.1 , pp. 63-82
    • Blankart, C.R.1    Stargardt, T.2    Schreyogg, J.3
  • 16
    • 84872660761 scopus 로고    scopus 로고
    • Accessed 31 July 2013
    • U.S. Foo. and Drug Administration. Search Orphan Drug Designations and Approvals. 2013. http//www.accessdata.fda.gov/scripts/opdlisting/oopd/index.cfm. Accessed 31 July 2013
    • (2013) Search Orphan Drug Designations and Approvals
  • 17
    • 0008348082 scopus 로고    scopus 로고
    • Accessed 17 July 2013
    • European Medicines Agency. European public assessment reports: Orphan medicines. 2013. http://www.ema.europa.eu/ema/index.jsp?curl=pages%2Fmedicines%2Flanding%2Fepar-search.jsp&mid=WC0b01ac058001d125&searchTab=searchByAuthType&alreadyLoaded=true&isNewQuery=true&status=Authorised&status=Withdrawn&status=Suspended&status=Refused&keyword=Enter+keywords&searchType=name&taxonomyPath=&treeNumber=&searchGenericType=orphan. Accessed 17 July 2013
    • (2013) European Public Assessment Reports: Orphan Medicines
  • 18
    • 85007423773 scopus 로고    scopus 로고
    • Accessed 27 March 2014
    • Ministry of Health, Labour and Welfare of Japan. List of products designated as orphan drugs for diseases 2014. 2014. http://www.mhlw.go.jp/english/policy/health-medical/pharmaceuticals/orphan-drug.html. Accessed 27 March 2014.
    • (2014) List of Products Designated as Orphan Drugs for Diseases 2014
  • 19
    • 85007426431 scopus 로고    scopus 로고
    • Accessed 28 December 2013
    • Food and Drug Administration of China. Data Search. 2013. http://app1.sfda.gov.cn/datasearch/face3/dir.html. Accessed 28 December 2013.
    • (2013) Data Search
  • 20
    • 84879306396 scopus 로고    scopus 로고
    • Accessed 2 May 2013
    • World Health Organization. ATC/DDD Index 2013. 2013. http://www.whoccno/atc-ddd-index/ Accessed 2 May 2013.
    • (2013) ATC/DDD Index 2013
  • 21
    • 77954243603 scopus 로고    scopus 로고
    • Emergence of orphan drugs in the United States: A quantitative assessment of the first 25 years
    • Braun MM, Farag-El-Massah S, Xu K, Cote TR. Emergence of orphan drugs in the United States: a quantitative assessment of the first 25 years. Nat Rev Drug Discov. 2010;9(7):519-22.
    • (2010) Nat Rev Drug Discov. , vol.9 , Issue.7 , pp. 519-522
    • Braun, M.M.1    Farag-El-Massah, S.2    Xu, K.3    Cote, T.R.4
  • 22
    • 84880643025 scopus 로고    scopus 로고
    • Accessed 2 December 2013
    • U.S. Foo. and Drug Administration. What Are Generic Drugs? 2009. http://www.fda.gov/Drugs/ResourcesForYou/Consumers/BuyingUsingMedicineSafely/UnderstandingGenericDrugs/ucm144456.htm. Accessed 2 December 2013
    • (2009) What are Generic Drugs?
  • 24
    • 84872896308 scopus 로고    scopus 로고
    • Accessed 30 May 2013
    • National Bureau of Statistics of China. Income of Urban and Rural Residents in 2011. 2012. http://www.stats.gov.cn/english/NewsEvents/201201/t20120130-26566.html. Accessed 30 May 2013.
    • (2012) Income of Urban and Rural Residents in 2011
  • 25
    • 85007491932 scopus 로고    scopus 로고
    • Accessed 30 November 2013
    • Ministry of Human Resources and Social Security of the People's Republic of China. Drug lists of National Basic Medical Insurance. 2009. http://www.gov.cn/gzdt/2009-11/30/content-1476934.htm. Accessed 30 November 2013
    • (2009) Drug Lists of National Basic Medical Insurance
  • 26
    • 84859326107 scopus 로고    scopus 로고
    • Rare diseases and orphan drugs
    • Melnikova I. Rare diseases and orphan drugs. Nat Rev Drug Discov. 2012; 11(4):267-8.
    • (2012) Nat Rev Drug Discov. , vol.11 , Issue.4 , pp. 267-268
    • Melnikova, I.1
  • 27
    • 78751571157 scopus 로고    scopus 로고
    • Emerging issues in public health: A perspective on China's healthcare system
    • Ling RE, Liu F, Lu XQ, Wang W. Emerging issues in public health: a perspective on China's healthcare system. Public Health. 2011;125(1):9-14.
    • (2011) Public Health , vol.125 , Issue.1 , pp. 9-14
    • Ling, R.E.1    Liu, F.2    Lu, X.Q.3    Wang, W.4
  • 28
    • 84891930582 scopus 로고    scopus 로고
    • The ecology of medical care in Beijing
    • Shao S, Zhao F, Wang J, et al. The ecology of medical care in Beijing. PLoS ONE. 2013;8(12):e82446.
    • (2013) PLoS ONE , vol.8 , Issue.12
    • Shao, S.1    Zhao, F.2    Wang, J.3
  • 29
    • 84992421885 scopus 로고    scopus 로고
    • Management strategy for raising the accessibility to orphan drugs in China
    • Gong SW, Zhang L, Jin S, Li LL. Management strategy for raising the accessibility to orphan drugs in China. Chin J Hospital Admin. 2010;26(2):126-30.
    • (2010) Chin J Hospital Admin. , vol.26 , Issue.2 , pp. 126-130
    • Gong, S.W.1    Zhang, L.2    Jin, S.3    Li, L.L.4
  • 30
    • 77954244068 scopus 로고    scopus 로고
    • China: Public health genomics
    • Zheng S, Song M, Wu L, et al. China: public health genomics. Public Health Genom. 2010;13(5):269-75.
    • (2010) Public Health Genom. , vol.13 , Issue.5 , pp. 269-275
    • Zheng, S.1    Song, M.2    Wu, L.3
  • 31
    • 84986133005 scopus 로고    scopus 로고
    • Orphan drugs: Pricing, reimbursement and patient access
    • Barak A, Shankar NJ. Orphan drugs: pricing, reimbursement and patient access. Int J Pharmaceut Healthcare Market. 2011;5(4):299-317
    • (2011) Int J Pharmaceut Healthcare Market , vol.5 , Issue.4 , pp. 299-317
    • Barak, A.1    Shankar, N.J.2
  • 32
    • 84856487084 scopus 로고    scopus 로고
    • Access to orphan drugs in Europe: Current and future issues
    • Michel M, Toumi M. Access to orphan drugs in Europe: current and future issues. Expert Rev Pharmacoecon Outcomes Res. 2012;12(1):23-9.
    • (2012) Expert Rev Pharmacoecon Outcomes Res. , vol.12 , Issue.1 , pp. 23-29
    • Michel, M.1    Toumi, M.2
  • 35
    • 84866564048 scopus 로고    scopus 로고
    • Paying for the orphan drug system: Break or bend? Is it time for a new evaluation system for payers in Europe to take account of new rare disease treatments?
    • Hughes-Wilson W, Palma A, Schuurman A, Simoens S. Paying for the Orphan Drug System: break or bend? Is it time for a new evaluation system for payers in Europe to take account of new rare disease treatments? Orphanet J Rare Dis. 2012;7:74.
    • (2012) Orphanet J Rare Dis. , vol.7 , pp. 74
    • Hughes-Wilson, W.1    Palma, A.2    Schuurman, A.3    Simoens, S.4
  • 36
    • 27744461277 scopus 로고    scopus 로고
    • Drugs for exceptionally rare diseases: Do they deserve special status for funding?
    • Hughes DA, Tunnage B, Yeo ST. Drugs for exceptionally rare diseases: do they deserve special status for funding? QJM. 2005;98(11):829-36.
    • (2005) QJM , vol.98 , Issue.11 , pp. 829-836
    • Hughes, D.A.1    Tunnage, B.2    Yeo, S.T.3
  • 38
    • 85007490051 scopus 로고    scopus 로고
    • Orphan drugs Part 1 - Patient care to the individual level
    • Pierce D. Orphan Drugs Part 1 - Patient Care to the Individual Level. Oncol Issues. 2010;25(6):44.
    • (2010) Oncol Issues , vol.25 , Issue.6 , pp. 44
    • Pierce, D.1
  • 39
    • 85007423741 scopus 로고    scopus 로고
    • Accessed 17 July 2014
    • The LPL Deficiency Association. Patient Assistance Programs. 2014. http://lplda.org/lpld-patients-and-caregivers/resources/patient-assistance/. Accessed 17 July 2014
    • (2014) Patient Assistance Programs
  • 40
    • 84940645721 scopus 로고    scopus 로고
    • Accessed 19 July 2014
    • Food and Drug Administration of China. 2013 China Drug Review Annual Report. 2014. http://www.cde.org.cn/news.do?method=viewInfoCommon&id=313280. Accessed 19 July 2014
    • (2014) 2013 China Drug Review Annual Report


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