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Volumn 371, Issue 9629, 2008, Pages 2039-2041

Why rare diseases are an important medical and social issue

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA 1 ANTITRYPSIN DEFICIENCY; AUTISM; BRUGADA SYNDROME; CONGENITAL DIAPHRAGM HERNIA; DYSTONIA; ERYTHROPOIETIC PROTOPORPHYRIA; ESOPHAGUS ATRESIA; FALLOT TETRALOGY; GREAT VESSELS TRANSPOSITION; GUILLAIN BARRE SYNDROME; HUMAN; JUVENILE RHEUMATOID ARTHRITIS; MARFAN SYNDROME; MEDICAL SOCIETY; MELANOMA; MULTIPLE MYELOMA; NARCOLEPSY; NEUROFIBROMATOSIS; NONHODGKIN LYMPHOMA; POLYCYTHEMIA VERA; PREVALENCE; PRIORITY JOURNAL; PUBLIC HEALTH; RARE DISEASE; RETINITIS PIGMENTOSA; REVIEW; SCLERODERMA; WORLD HEALTH ORGANIZATION;

EID: 44849143056     PISSN: 01406736     EISSN: None     Source Type: Journal    
DOI: 10.1016/S0140-6736(08)60872-7     Document Type: Review
Times cited : (449)

References (14)
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    • A journey of hope: lessons learned from studies on rare diseases and orphan drugs
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    • Dionisi-Vici, C.1    Rizzo, C.2    Burlina, A.3
  • 13
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    • Overview of current Centres of Reference on rare diseases in the EU (accessed July, 2006).
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    • Adopting orphan drugs: two dozen years of treating rare diseases
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    • Haffner, M.1


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.