Emerging and future therapies for hemophilia

Journal of Blood Medicine

Volumn 6, Issue , 2015, Pages 245-255

  Carr, Marcus E ^a,b   Tortella, Bartholomew J ^b,c  

^a ROBERT WOOD JOHNSON MEDICAL SCHOOL   (United States)

^b PFIZER INC   (United States)

^c DREXEL UNIVERSITY COLLEGE OF MEDICINE   (United States)

Author keywords

Anti tissue factor pathway inhibitor antibodies; Clotting factor analogs; Extended half life clotting factors; Gene therapy; Nonfactor replacement therapy

Indexed keywords

ALBUMIN; BISPECIFIC ANTIBODY; BLOOD CLOTTING FACTOR 8; BLOOD CLOTTING FACTOR 9; BLOOD CLOTTING FACTOR CONCENTRATE; CONCIZUMAB; HYBRID PROTEIN; LENTIVIRUS VECTOR; MACROGOL; PARVOVIRUS VECTOR; POLYSIALIC ACID; RECOMBINANT BLOOD CLOTTING FACTOR 7A FC; RECOMBINANT BLOOD CLOTTING FACTOR 8; RECOMBINANT BLOOD CLOTTING FACTOR 9; RECOMBINANT PROTEIN; SERUM ALBUMIN; TISSUE FACTOR PATHWAY INHIBITOR; UNCLASSIFIED DRUG;

BLEEDING; CHEMICAL MODIFICATION; CIRCUMCISION; CONTROLLED CLINICAL TRIAL (TOPIC); DISEASE TRANSMISSION; DONOR SELECTION; DRUG HALF LIFE; DRUG SAFETY; GENE MUTATION; GENE SEQUENCE; GENE THERAPY; HEMOPHILIA; HETEROZYGOTE; HUMAN; MOLECULAR CLONING; MULTICENTER STUDY (TOPIC); PHASE 1 CLINICAL TRIAL (TOPIC); PHASE 2 CLINICAL TRIAL (TOPIC); PHASE 3 CLINICAL TRIAL (TOPIC); RANDOMIZED CONTROLLED TRIAL (TOPIC); REVIEW; VIRUS INACTIVATION; X CHROMOSOME; X CHROMOSOME INACTIVATION;

EID: 85006216296     PISSN: None     EISSN: 11792736     Source Type: Journal    
DOI: 10.2147/JBM.S42669     Document Type: Review

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