-
1
-
-
84862339238
-
Rare diseases, orphan drugs, and their regulation in Asia: current status and future perspectives
-
Feb
-
P.Song, J.Gao, Y.Inagaki, et al. Rare diseases, orphan drugs, and their regulation in Asia: current status and future perspectives. Intractable Rare Dis Res. 2012 Feb;1(1):3–9.•• Review article includes discussion on orphan drugs research and development issues in Japan.
-
(2012)
Intractable Rare Dis Res
, vol.1
, Issue.1
, pp. 3-9
-
-
Song, P.1
Gao, J.2
Inagaki, Y.3
-
2
-
-
44849143056
-
Why rare diseases are an important medical and social issue
-
Jun
-
A.Schieppati, J.I.Henter, E.Daina, et al. Why rare diseases are an important medical and social issue. Lancet. 2008 Jun 14;371(9629):2039–2041.
-
(2008)
Lancet
, vol.371
, Issue.9629
, pp. 2039-2041
-
-
Schieppati, A.1
Henter, J.I.2
Daina, E.3
-
3
-
-
84862324757
-
Hopes for intractable and rare diseases research
-
Feb
-
W.Tang Hopes for intractable and rare diseases research. Intractable Rare Dis Res. 2013 Feb;2(1):1–2.
-
(2013)
Intractable Rare Dis Res
, vol.2
, Issue.1
, pp. 1-2
-
-
Tang, W.1
-
4
-
-
79959559590
-
-
Available from:, Dec
-
Rare Diseases Europe. About rare disease. 2009 [cited 2015 Dec10]. Available from: http://www.eurordis.org/about-rare-diseases.
-
(2009)
About rare disease
-
-
-
5
-
-
84941876142
-
Current situation and prospects of newborn screening and treatment for Phenylketonuria in China – compared with the current situation in the United States, UK and Japan
-
Nov
-
L.Mei, P.Song, N.Kokudo, et al. Current situation and prospects of newborn screening and treatment for Phenylketonuria in China – compared with the current situation in the United States, UK and Japan. Intractable Rare Dis Res. 2013 Nov;2(4):106–114.
-
(2013)
Intractable Rare Dis Res
, vol.2
, Issue.4
, pp. 106-114
-
-
Mei, L.1
Song, P.2
Kokudo, N.3
-
6
-
-
84975184862
-
Newborn screening and related policy against Phenylketonuria in China
-
Aug
-
L.Mei, P.Song, L.Xu. Newborn screening and related policy against Phenylketonuria in China. Intractable Rare Dis Res. 2013 Aug;2(3):72–76.
-
(2013)
Intractable Rare Dis Res
, vol.2
, Issue.3
, pp. 72-76
-
-
Mei, L.1
Song, P.2
Xu, L.3
-
7
-
-
85007144943
-
The ice bucket challenge: the public sector should get ready to promptly promote the sustained development of a system of medical care for and research into rare diseases
-
Aug
-
P.Song. The ice bucket challenge: the public sector should get ready to promptly promote the sustained development of a system of medical care for and research into rare diseases. Intractable Rare Dis Res. 2014 Aug;3(3):94–96.
-
(2014)
Intractable Rare Dis Res
, vol.3
, Issue.3
, pp. 94-96
-
-
Song, P.1
-
8
-
-
84862310230
-
Intractable and rare diseases research in Asia
-
Apr
-
P.Song, J.Gao, Y.Inagaki, et al. Intractable and rare diseases research in Asia. Biosci Trends. 2012 Apr;6(2):48–51.
-
(2012)
Biosci Trends
, vol.6
, Issue.2
, pp. 48-51
-
-
Song, P.1
Gao, J.2
Inagaki, Y.3
-
9
-
-
84975196029
-
Revision of measures to combat intractable diseases in Japan: three pillars will play an even greater role in the future
-
Feb
-
P.Song, N.Kokudo. Revision of measures to combat intractable diseases in Japan: three pillars will play an even greater role in the future. Intractable Rare Dis Res. 2013 Feb;2(1):33–34.• Article describing the revision of measures to combat rare diseases in Japan.
-
(2013)
Intractable Rare Dis Res
, vol.2
, Issue.1
, pp. 33-34
-
-
Song, P.1
Kokudo, N.2
-
10
-
-
84866780366
-
New opportunity for orphan drug development in Japan: early exploratory clinical trial bases promote drug translation from basic studies to clinical application
-
May
-
P.Song, J.Gao, N.Kokudo, et al. New opportunity for orphan drug development in Japan: early exploratory clinical trial bases promote drug translation from basic studies to clinical application. Intractable Rare Dis Res. 2012 May;1(2):95–97.•• Article describing the early exploratory clinical trial bases to promote drug translation from basic studies to clinical application in Japan.
-
(2012)
Intractable Rare Dis Res
, vol.1
, Issue.2
, pp. 95-97
-
-
Song, P.1
Gao, J.2
Kokudo, N.3
-
11
-
-
84896724127
-
Necessity of cooperation with government on publication of scientific research results for intractable diseases
-
May
-
Y.Inagaki, P.Song. Necessity of cooperation with government on publication of scientific research results for intractable diseases. Intractable Rare Dis Res. 2013 May;2(2):69–71.• Article emphasizes the importance of government-funded special biomedical research programs to combat rare diseases and orphan drugs.
-
(2013)
Intractable Rare Dis Res
, vol.2
, Issue.2
, pp. 69-71
-
-
Inagaki, Y.1
Song, P.2
-
12
-
-
84862324757
-
Intractable & rare diseases research
-
Feb
-
W.Tang, M.Makuuchi. Intractable & rare diseases research. Intractable Rare Dis Res. 2012 Feb;1(1):1–2.•• Article emphasizes the importance of research programs to combat rare diseases and orphan drugs.
-
(2012)
Intractable Rare Dis Res
, vol.1
, Issue.1
, pp. 1-2
-
-
Tang, W.1
Makuuchi, M.2
-
14
-
-
84975183373
-
-
Japan Intractable Diseases Information Center. Strategies against intractable disease since 2015 [Internet]. 2015 [cited 2016 Jan 3]. Available from: http://www.nanbyou.or.jp/entry/4141.
-
-
-
-
15
-
-
84975177223
-
-
Japan Intractable Diseases Information Center. Number of patient enrolled specified disease treatment research program [Internet]. 2015 [cited 2016 Jan 5]. Available from: http://www.nanbyou.or.jp/entry/1356.
-
(2015)
-
-
-
19
-
-
84880585067
-
Perspectives on human clinical trials of therapies using iPS cells in Japan: reaching the forefront of stem-cell therapies
-
Jun
-
P.Song, Y.Inagaki, Y.Sugawara, et al. Perspectives on human clinical trials of therapies using iPS cells in Japan: reaching the forefront of stem-cell therapies. Biosci Trends. 2013 Jun;7(3):157–158.
-
(2013)
Biosci Trends
, vol.7
, Issue.3
, pp. 157-158
-
-
Song, P.1
Inagaki, Y.2
Sugawara, Y.3
-
20
-
-
84975177227
-
-
The MHLW Grants System. The research against intractable liver diseases [Internet]. 2013 [cited 2016 Jan 5]. Available from: http://mhlw-grants.niph.go.jp/niph/search/NIDD00do?resrchNum=201231041A
-
(2013)
The research against intractable liver diseases
-
-
-
21
-
-
84975183383
-
-
Japan Intractable Diseases Information Center. The guideline for diagnosis and treatment [Internet]. 2015 [cited 2016 Jan 6]. Available from: http://www.nanbyou.or.jp/entry/504#01.
-
(2015)
The guideline for diagnosis and treatment
-
-
-
22
-
-
84975175041
-
-
Japan Intractable Diseases Information Center. The center hospital for treatment of rare diseases [Internet]. 2014 [cited 2016 Jan 7]. Available from: http://www.nanbyou.or.jp/entry/1439.
-
(2014)
The center hospital for treatment of rare diseases
-
-
-
25
-
-
84975207641
-
Global movement for diagnosis and treatment of rare/intractable diseases
-
(in Japanese)
-
T.Kodama, N.Tomita. Global movement for diagnosis and treatment of rare/intractable diseases. J Natl Inst Public Health. 2011;60:105–111. (in Japanese).
-
(2011)
J Natl Inst Public Health
, vol.60
, pp. 105-111
-
-
Kodama, T.1
Tomita, N.2
-
26
-
-
0038416960
-
Characteristics of a medical care program for specific diseases in Japan in an era of changing cost-sharing
-
Jun
-
H.Nakatani, T.Kondo. Characteristics of a medical care program for specific diseases in Japan in an era of changing cost-sharing. Health Policy. 2003 Jun;64(3):377–389.
-
(2003)
Health Policy
, vol.64
, Issue.3
, pp. 377-389
-
-
Nakatani, H.1
Kondo, T.2
-
27
-
-
51249119642
-
35 years of Japanese policy on rare diseases
-
Sep
-
S.Hayashi, T.Umeda. 35 years of Japanese policy on rare diseases. Lancet. 2008 Sep 13;372(9642):889–890.
-
(2008)
Lancet
, vol.372
, Issue.9642
, pp. 889-890
-
-
Hayashi, S.1
Umeda, T.2
-
28
-
-
84873079257
-
Orphan drugs: the regulatory environment
-
Feb
-
P.Franco. Orphan drugs: the regulatory environment. Drug Discov Today. 2013 Feb;18(3–4):163–172.• Article describing the orphan drugs designation in Japan, the USA, and the EU.
-
(2013)
Drug Discov Today
, vol.18
, Issue.3-4
, pp. 163-172
-
-
Franco, P.1
-
29
-
-
78649700786
-
Rare diseases, orphan drugs and their regulation: questions and misconceptions
-
Dec
-
E.Tambuyzer. Rare diseases, orphan drugs and their regulation: questions and misconceptions. Nat Rev Drug Discov. 2010 Dec;9(12):921–929.
-
(2010)
Nat Rev Drug Discov
, vol.9
, Issue.12
, pp. 921-929
-
-
Tambuyzer, E.1
-
30
-
-
80053379101
-
Estimating the budget impact of orphan medicines in Europe: 2010–2020
-
C.Schey, T.Milanova, A.Hutchings. Estimating the budget impact of orphan medicines in Europe: 2010–2020. Orphanet J Rare Dis. 2011;6:62.
-
(2011)
Orphanet J Rare Dis
, vol.6
, pp. 62
-
-
Schey, C.1
Milanova, T.2
Hutchings, A.3
-
31
-
-
84975179418
-
-
Pharmaceuticals and Medical Devices Agency. The business report in 2010 [Internet]. 2010 [cited 2015 Dec 15]. Available from: https://www.pmda.go.jp/english/about-pmda/annual-reports/0001.html
-
(2010)
-
-
-
32
-
-
52049090617
-
Personal imports of drugs to Japan in 2005 – an analysis of import certificates
-
Oct
-
K.Tsuji, K.Tsutani. Personal imports of drugs to Japan in 2005 – an analysis of import certificates. J Clin Pharm Ther. 2008 Oct;33(5):545–552.
-
(2008)
J Clin Pharm Ther
, vol.33
, Issue.5
, pp. 545-552
-
-
Tsuji, K.1
Tsutani, K.2
-
33
-
-
84975186673
-
-
Keio University Hospital Clinical and translation Research Center [Internet]. 2014 [cited 2015 Dec 27]. Available from: http://www.hosp.keio.ac.jp/ctr/about/outline.html
-
(2014)
-
-
-
34
-
-
84940513745
-
Accelerating regulatory science initiatives for the development of drugs for Alzheimer’s disease in Japan
-
Aug
-
T.Moritoyo. Accelerating regulatory science initiatives for the development of drugs for Alzheimer’s disease in Japan. Clin Ther. 2015 Aug;37(8):1622–1626.
-
(2015)
Clin Ther
, vol.37
, Issue.8
, pp. 1622-1626
-
-
Moritoyo, T.1
|