메뉴 건너뛰기




Volumn 38, Issue 9, 2016, Pages 785-791

Long-term outcomes of steroid therapy for Duchenne muscular dystrophy in Japan

Author keywords

Ambulation; Corticosteroid treatment; Height; Mixed model; Respiratory function; Side effect

Indexed keywords

PREDNISOLONE; CORTICOSTEROID; MUSCLE RELAXANT AGENT;

EID: 84963985259     PISSN: 03877604     EISSN: 18727131     Source Type: Journal    
DOI: 10.1016/j.braindev.2016.04.001     Document Type: Article
Times cited : (16)

References (29)
  • 1
    • 0026734187 scopus 로고
    • The membrane hypothesis of Duchenne muscular dystrophy: quest for functional evidence
    • [1] Hutter, O.F., The membrane hypothesis of Duchenne muscular dystrophy: quest for functional evidence. J Inherit Metab Dis 15 (1992), 565–577.
    • (1992) J Inherit Metab Dis , vol.15 , pp. 565-577
    • Hutter, O.F.1
  • 3
    • 0016287539 scopus 로고
    • Prednisone in Duchenne muscular dystrophy
    • [3] Drachman, D.B., Toyka, K.V., Myer, E., Prednisone in Duchenne muscular dystrophy. Lancet 2 (1974), 1409–1412.
    • (1974) Lancet , vol.2 , pp. 1409-1412
    • Drachman, D.B.1    Toyka, K.V.2    Myer, E.3
  • 4
    • 3843121117 scopus 로고    scopus 로고
    • Glucocorticoid corticosteroids for Duchenne muscular dystrophy
    • CD003725
    • [4] Manzur, A.Y., Kuntzer, T., Pike, M., Swan, A., Glucocorticoid corticosteroids for Duchenne muscular dystrophy. Cochrane Database Syst Rev, 1, 2008, CD003725.
    • (2008) Cochrane Database Syst Rev , vol.1
    • Manzur, A.Y.1    Kuntzer, T.2    Pike, M.3    Swan, A.4
  • 6
    • 0024332294 scopus 로고
    • Randomized, double-blind six-month trial of prednisone in Duchenne's muscular dystrophy
    • [6] Mendell, J.R., Moxley, R.T., Griggs, R.C., Brooke, M.H., Fenichel, G.M., Miller, J.P., et al. Randomized, double-blind six-month trial of prednisone in Duchenne's muscular dystrophy. N Engl J Med 320 (1989), 1592–1597.
    • (1989) N Engl J Med , vol.320 , pp. 1592-1597
    • Mendell, J.R.1    Moxley, R.T.2    Griggs, R.C.3    Brooke, M.H.4    Fenichel, G.M.5    Miller, J.P.6
  • 7
    • 0025860096 scopus 로고
    • A comparison of daily and alternate-day prednisone therapy in the treatment of Duchenne muscular dystrophy
    • [7] Fenichel, G.M., Mendell, J.R., Moxley, R.T. 3rd, Griggs, R.C., Brooke, M.H., Miller, J.P., et al. A comparison of daily and alternate-day prednisone therapy in the treatment of Duchenne muscular dystrophy. Arch Neurol 48 (1991), 575–579.
    • (1991) Arch Neurol , vol.48 , pp. 575-579
    • Fenichel, G.M.1    Mendell, J.R.2    Moxley, R.T.3    Griggs, R.C.4    Brooke, M.H.5    Miller, J.P.6
  • 8
    • 33750620045 scopus 로고    scopus 로고
    • Prednisolone in Duchenne muscular dystrophy with imminent loss of ambulation
    • [8] Pradhan, S., Ghosh, D., Srivastava, N.K., Kumar, A., Mittal, B., Pandey, C.M., et al. Prednisolone in Duchenne muscular dystrophy with imminent loss of ambulation. J Neurol 253 (2006), 1309–1316.
    • (2006) J Neurol , vol.253 , pp. 1309-1316
    • Pradhan, S.1    Ghosh, D.2    Srivastava, N.K.3    Kumar, A.4    Mittal, B.5    Pandey, C.M.6
  • 9
    • 0036893708 scopus 로고    scopus 로고
    • High dose weekly oral prednisone improves strength in boys with Duchenne muscular dystrophy
    • [9] Connolly, A.M., Schierbecker, J., Renna, R., Florence, J., High dose weekly oral prednisone improves strength in boys with Duchenne muscular dystrophy. Neuromuscul Disord 12 (2002), 917–925.
    • (2002) Neuromuscul Disord , vol.12 , pp. 917-925
    • Connolly, A.M.1    Schierbecker, J.2    Renna, R.3    Florence, J.4
  • 10
    • 80051500586 scopus 로고    scopus 로고
    • Randomized, blinded trial of weekend vs daily prednisone in Duchenne muscular dystrophy
    • [10] Escolar, D.M., Hache, L.P., Clemens, P.R., Cnaan, A., McDonald, C.M., Viswanathan, V., et al. Randomized, blinded trial of weekend vs daily prednisone in Duchenne muscular dystrophy. Neurology 77 (2011), 444–452.
    • (2011) Neurology , vol.77 , pp. 444-452
    • Escolar, D.M.1    Hache, L.P.2    Clemens, P.R.3    Cnaan, A.4    McDonald, C.M.5    Viswanathan, V.6
  • 11
    • 33646478253 scopus 로고    scopus 로고
    • Long-term benefits of deflazacort treatment for boys with Duchenne muscular dystrophy in their second decade
    • [11] Biggar, W.D., Harris, V.A., Eliasoph, L., Alman, B., Long-term benefits of deflazacort treatment for boys with Duchenne muscular dystrophy in their second decade. Neuromuscul Disord 16 (2006), 249–255.
    • (2006) Neuromuscul Disord , vol.16 , pp. 249-255
    • Biggar, W.D.1    Harris, V.A.2    Eliasoph, L.3    Alman, B.4
  • 12
    • 34248201124 scopus 로고    scopus 로고
    • Orthopedic outcomes of long-term daily corticosteroid treatment in Duchenne muscular dystrophy
    • [12] King, W.M., Ruttencutter, R., Nagaraja, H.N., Matkovic, V., Landoll, J., Hoyle, C., et al. Orthopedic outcomes of long-term daily corticosteroid treatment in Duchenne muscular dystrophy. Neurology 68 (2007), 1607–1613.
    • (2007) Neurology , vol.68 , pp. 1607-1613
    • King, W.M.1    Ruttencutter, R.2    Nagaraja, H.N.3    Matkovic, V.4    Landoll, J.5    Hoyle, C.6
  • 13
    • 84877594408 scopus 로고    scopus 로고
    • Long-term benefits and adverse effects of intermittent versus daily glucocorticoids in boys with Duchenne muscular dystrophy
    • [13] Ricotti, V., Ridout, D.A., Scott, E., Quinlivan, R., Robb, S.A., Manzur, A.Y., et al. Long-term benefits and adverse effects of intermittent versus daily glucocorticoids in boys with Duchenne muscular dystrophy. J Neurol Neurosurg Psychiatry 84 (2013), 698–705.
    • (2013) J Neurol Neurosurg Psychiatry , vol.84 , pp. 698-705
    • Ricotti, V.1    Ridout, D.A.2    Scott, E.3    Quinlivan, R.4    Robb, S.A.5    Manzur, A.Y.6
  • 14
    • 19944427852 scopus 로고    scopus 로고
    • Practice parameter: corticosteroid treatment of Duchenne dystrophy: report of the Quality Standards Subcommittee of the American Academy of Neurology and the Practice Committee of the Child Neurology Society
    • [14] Moxley, R.T. 3rd, Ashwal, S., Pandya, S., Connolly, A., Florence, J., Mathews, K., et al. Practice parameter: corticosteroid treatment of Duchenne dystrophy: report of the Quality Standards Subcommittee of the American Academy of Neurology and the Practice Committee of the Child Neurology Society. Neurology 11:64 (2005), 13–20.
    • (2005) Neurology , vol.11 , Issue.64 , pp. 13-20
    • Moxley, R.T.1    Ashwal, S.2    Pandya, S.3    Connolly, A.4    Florence, J.5    Mathews, K.6
  • 15
    • 84957598991 scopus 로고    scopus 로고
    • Practice guideline update summary: corticosteroid treatment of Duchenne muscular dystrophy: report of the Guideline Development Subcommittee of the American Academy of Neurology
    • [15] Gloss, D., Moxley, R.T. 3rd, Ashwal, S., Oskoui, M., Practice guideline update summary: corticosteroid treatment of Duchenne muscular dystrophy: report of the Guideline Development Subcommittee of the American Academy of Neurology. Neurology 86 (2016), 465–472.
    • (2016) Neurology , vol.86 , pp. 465-472
    • Gloss, D.1    Moxley, R.T.2    Ashwal, S.3    Oskoui, M.4
  • 16
    • 9544220511 scopus 로고
    • Flow-volume curve in healthy and asthmatic children in the non-attack stage (in Japanese)
    • [16] Nishima, S., Flow-volume curve in healthy and asthmatic children in the non-attack stage (in Japanese). Rinsho to Kenkyu 54 (1977), 525–530.
    • (1977) Rinsho to Kenkyu , vol.54 , pp. 525-530
    • Nishima, S.1
  • 18
    • 0030670430 scopus 로고    scopus 로고
    • Using the general linear mixed model to analyse unbalanced repeated measures and longitudinal data
    • [18] Cnaan, A., Laird, N.M., Slasor, P., Using the general linear mixed model to analyse unbalanced repeated measures and longitudinal data. Stat Med 16 (1997), 2349–2380.
    • (1997) Stat Med , vol.16 , pp. 2349-2380
    • Cnaan, A.1    Laird, N.M.2    Slasor, P.3
  • 19
    • 84879551364 scopus 로고    scopus 로고
    • Corticosteroids in Duchenne muscular dystrophy: major variations in practice
    • [19] Griggs, R.C., Herr, B.E., Reha, A., Elfring, G., Atkinson, L., Cwik, V., et al. Corticosteroids in Duchenne muscular dystrophy: major variations in practice. Muscle Nerve 48 (2013), 27–31.
    • (2013) Muscle Nerve , vol.48 , pp. 27-31
    • Griggs, R.C.1    Herr, B.E.2    Reha, A.3    Elfring, G.4    Atkinson, L.5    Cwik, V.6
  • 21
    • 77956322846 scopus 로고    scopus 로고
    • Change in natural history of Duchenne muscular dystrophy with long-term corticosteroid treatment: implications for management
    • [21] Moxley, R.T. 3rd, Pandya, S., Ciafaloni, E., Fox, D.J., Campbell, K., Change in natural history of Duchenne muscular dystrophy with long-term corticosteroid treatment: implications for management. J Child Neurol 25 (2010), 1116–1129.
    • (2010) J Child Neurol , vol.25 , pp. 1116-1129
    • Moxley, R.T.1    Pandya, S.2    Ciafaloni, E.3    Fox, D.J.4    Campbell, K.5
  • 22
    • 84879551615 scopus 로고    scopus 로고
    • The cooperative international neuromuscular research group Duchenne natural history study: glucocorticoid treatment preserves clinically meaningful functional milestones and reduces rate of disease progression as measured by manual muscle testing and other commonly used clinical trial outcome measures
    • [22] Henricson, E.K., Abresch, R.T., Cnaan, A., Hu, F., Duong, T., Arrieta, A., et al. The cooperative international neuromuscular research group Duchenne natural history study: glucocorticoid treatment preserves clinically meaningful functional milestones and reduces rate of disease progression as measured by manual muscle testing and other commonly used clinical trial outcome measures. Muscle Nerve 48 (2013), 55–67.
    • (2013) Muscle Nerve , vol.48 , pp. 55-67
    • Henricson, E.K.1    Abresch, R.T.2    Cnaan, A.3    Hu, F.4    Duong, T.5    Arrieta, A.6
  • 24
    • 84883535995 scopus 로고    scopus 로고
    • Sniff nasal inspiratory pressure in the longitudinal assessment of young Duchenne muscular dystrophy children
    • [24] Nève, V., Cuisset, J.M., Edmé, J.L., Carpentier, A., Howsam, M., Leclerc, O., et al. Sniff nasal inspiratory pressure in the longitudinal assessment of young Duchenne muscular dystrophy children. Eur Respir J 42 (2013), 671–680.
    • (2013) Eur Respir J , vol.42 , pp. 671-680
    • Nève, V.1    Cuisset, J.M.2    Edmé, J.L.3    Carpentier, A.4    Howsam, M.5    Leclerc, O.6
  • 25
    • 0033812726 scopus 로고    scopus 로고
    • A multicenter, double-blind, randomized trial of deflazacort versus prednisone in Duchenne muscular dystrophy
    • [25] Bonifati, M.D., Ruzza, G., Bonometto, P., Berardinelli, A., Gorni, K., Orcesi, S., et al. A multicenter, double-blind, randomized trial of deflazacort versus prednisone in Duchenne muscular dystrophy. Muscle Nerve 23 (2000), 1344–1347.
    • (2000) Muscle Nerve , vol.23 , pp. 1344-1347
    • Bonifati, M.D.1    Ruzza, G.2    Bonometto, P.3    Berardinelli, A.4    Gorni, K.5    Orcesi, S.6
  • 26
    • 0029011230 scopus 로고
    • Low-dose prednisolone treatment in Duchenne and Becker muscular dystrophy
    • [26] Backman, E., Henriksson, K.G., Low-dose prednisolone treatment in Duchenne and Becker muscular dystrophy. Neuromuscul Disord 5 (1995), 233–241.
    • (1995) Neuromuscul Disord , vol.5 , pp. 233-241
    • Backman, E.1    Henriksson, K.G.2
  • 28
    • 84876285027 scopus 로고    scopus 로고
    • Characteristics of Japanese Duchenne and Becker muscular dystrophy patients in a novel Japanese national registry of muscular dystrophy (Remedy)
    • [28] Nakamura, H., Kimura, E., Mori-Yoshimura, M., Komaki, H., Matsuda, Y., Goto, K., et al. Characteristics of Japanese Duchenne and Becker muscular dystrophy patients in a novel Japanese national registry of muscular dystrophy (Remedy). Orphanet J Rare Dis, 8, 2013, 60.
    • (2013) Orphanet J Rare Dis , vol.8 , pp. 60
    • Nakamura, H.1    Kimura, E.2    Mori-Yoshimura, M.3    Komaki, H.4    Matsuda, Y.5    Goto, K.6
  • 29
    • 84890638565 scopus 로고    scopus 로고
    • Prednisolone improves walking in Japanese Duchenne muscular dystrophy patients
    • [29] Takeuchi, F., Yonemoto, N., Nakamura, H., Shimizu, R., Komaki, H., Mori-Yoshimura, M., et al. Prednisolone improves walking in Japanese Duchenne muscular dystrophy patients. J Neurol 260 (2013), 3023–3029.
    • (2013) J Neurol , vol.260 , pp. 3023-3029
    • Takeuchi, F.1    Yonemoto, N.2    Nakamura, H.3    Shimizu, R.4    Komaki, H.5    Mori-Yoshimura, M.6


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.