The cooperative international neuromuscular research group Duchenne natural history study: Glucocorticoid treatment preserves clinically meaningful functional milestones and reduces rate of disease progression as measured by manual muscle testing and other commonly used clinical trial outcome measures

Muscle and Nerve

Volumn 48, Issue 1, 2013, Pages 55-67

  Henricson, Erik K ^a   Abresch, R Ted ^a   Cnaan, Avital ^b,c   Hu, Fengming ^b   Duong, Tina ^b   Arrieta, Adrienne ^b   Han, Jay ^a   Escolar, Diana M ^d   Florence, Julaine M ^e   Clemens, Paula R ^f   Hoffman, Eric P ^b,c   McDonald, Craig M ^a   Vishwanathan, V ^g,h   Chidambaranathan, S ^g,h   Biggar, W Douglas ⁱ   Mah, Jean K ^j   Tulinius, Mar ^k   Leshner, Robert ^b   Tesi Rocha, Carolina ^b   Kornberg, Andrew ^l   Ryan, Monique ^l   Nevo, Yoram ^m   Dubrovsky, Alberto ⁿ   Kuntz, Nancy ^o   Driscoll, Sherilyn ^o   Connolly, Anne ^e   Pestronk, Alan ^e   Teasley, Jean ^p   Bertorini, Tulio ^q   North, Kathryn ^r   Kolski, Hanna ^s   Carlo, Jose ^t   Gorni, Ksenija ^u,v   Lotze, Timothy ^w   Day, John ^x   Benditt, Josh ^x   Boitano, Louis ^x   Birnkrant, David ^x   Connuck, David ^x   Finder, Jonathan ^x   Hinton, Veronica ^x   Mathews, Katherine ^x   Moxley, Richard ^x   Sparks, Susan ^x   Gordon, Erynn ^x   Cregan, Michelle ^a   Goude, Erica ^a   Glick, Merete ^a   Johnson, Linda ^a   Joyce, Nanette ^a   Lipa, Bethany ^a   Nicorici, Alina ^a   Skalsky, Andrew ^a   Witt, Amanda ^a   Kumar, Suresh ^g,h   Eliasoph, Laila ⁱ   Hosaki, Elizabeth ⁱ   Gonzales, Angela ⁱ   Harris, Vivien ⁱ   Chiu, Angela ^j   Goia, Edit ^j   Thannhauser, Jennifer ^j   Walker, Lori ^j   Wright, Caitlin ^j   Yousefi, Mehrnaz ^j   Alhander, Ann Christine ^k   Berglund, Lisa ^k   Ekstrom, Ann Berit ^k   Kroksmark, Anna Karin ^k   Sterky, Ulrika ^k   Birkmeier, Marissa ^b   Kaminski, Sarah ^b   Carroll, Kate ^l   DeValle, Katy ^l   Kennedy, Rachel ^l   Villano, Dani ^l   Leve, Adina Bar ^m   Shurr, Itai ^m   Wisband, Elana ^m   Yaffe, Debbie ^m   Andreone, Luz ⁿ   Corderi, Jose ⁿ   Mesa, Lilia ⁿ   Levi, Lorena ⁿ   Coleman Wood, Krista ^o   Hoffman, Ann ^o   Korn Petersen, Wendy ^o   Selcen, Duygu ^o   Abdel Hamid, Hoda ^f   Bise, Christopher ^f   Craig, Ann ^f   Hughes, Sarah ^f   Nguyen, Casey ^f   Weimer, Jason ^f   Golumbak, Paul ^e   Lopate, Glenn ^e   Malane, Justin ^e   Malkus, Betsy ^e   Nozaki, Kenkicki ^e   Renna, Renee ^e   Schierbacker, Jeanine ^e   Seiner, Catherine ^e   Wulf, Charlie ^e   Blair, Susan ^p   Grillo, Barbara ^p   Jones, Karen ^p   Monasterio, Eugenio ^p   Clift, Judy ^q   Feliciano, Cassandra ^q   Igarashi, Masanori ^q   Young, Rachel ^q   Rose, Kristy ^r   Webster, Richard ^r   Wicks, Stephanie ^r   Chen, Lucia ^s   Kennedy, Cameron ^s   Deliz, Brenda ^t   Espada, Sheila ^t   Fuste, Pura ^t   Luciano, Carlos ^t   Capone, Luca ^u   Beneggi, Maria ^v   Morettini, Valentina ^v   Gupta, Anjali ^w   McNeil, Robert ^w   Erickson, Amy ^x   Margolis, Marcia ^x   Naughton, Cameron ^x   Parry, Gareth ^x   Walk, David ^x   Bartley, Naomi ^y   Canelos, Paola ^y   Casper, Robert ^y   Hache, Lauren ^y   Ahmed, Mohammad ^y   Zimmerman, Angela ^y   more..

^a UNIVERSITY OF CALIFORNIA   (United States)

^b CHILDREN'S NATIONAL MEDICAL CENTER   (United States)

^c GEORGE WASHINGTON UNIVERSITY   (United States)

^d KENNEDY KRIEGER INSTITUTE   (United States)

^e WASHINGTON UNIVERSITY SCHOOL OF MEDICINE   (United States)

^f UNIVERSITY OF PITTSBURGH SCHOOL OF MEDICINE   (United States)

^g Sundaram Medical Foundation   (India)

^h Apollo Children s Hospital   (India)

ⁱ HOLLAND BLOORVIEW KIDS REHABILITATION HOSPITAL   (Canada)

^j ALBERTA CHILDREN'S HOSPITAL   (Canada)

^k QUEEN SILVIA CHILDREN'S HOSPITAL   (Sweden)

^l ROYAL CHILDREN'S HOSPITAL   (Australia)

^m HADASSAH HEBREW UNIVERSITY MEDICAL CENTER   (Israel)

ⁿ HOSPITAL UNIVERSITARIO FUNDACIÓN FAVALORO   (Argentina)

^o MAYO CLINIC   (United States)

^p Children s Hospital of Virginia   (United States)

^q UNIVERSITY OF TENNESSEE HEALTH SCIENCE CENTER   (United States)

^r CHILDREN S HOSPITAL AT WESTMEAD   (Australia)

^s UNIVERSITY OF ALBERTA   (Canada)

^t UNIVERSITY OF PUERTO RICO SCHOOL OF MEDICINE   (Puerto Rico)

^u UNIVERSITY OF PAVIA   (Italy)

^v OSPEDALE NIGUARDA CA GRANDA   (Italy)

^w TEXAS CHILDREN S HOSPITAL   (United States)

^x UNIVERSITY OF MINNESOTA   (United States)

^y The CINRG Coordinating Center   (United States)

more..

Author keywords

Adolescent; Adult; Child preschool; Follow up studies; Health status; Humans; Locomotion; Male; Muscle strength physiology; Muscular dystrophies classification; Muscular dystrophies Duchenne physiopathology; Muscular dystrophies therapy; Phenotype; Quality of life psychology; Respiratory function tests

Indexed keywords

GLUCOCORTICOID;

ADOLESCENT; ADULT; ARM; ARTICLE; CHILD; CORTICOSTEROID THERAPY; DIAGNOSTIC TEST; DISEASE COURSE; DUCHENNE MUSCULAR DYSTROPHY; FAMILY HISTORY; FUNCTIONAL STATUS; HEALTH STATUS; HUMAN; LUNG FUNCTION TEST; MAJOR CLINICAL STUDY; MALE; MANUAL MUSCLE TEST; MEDICAL HISTORY; MOBILIZATION; MUSCLE STRENGTH; PRESCHOOL CHILD; PRIORITY JOURNAL; RANGE OF MOTION; SCHOOL CHILD;

EID: 84879551615     PISSN: 0148639X     EISSN: 10974598     Source Type: Journal    
DOI: 10.1002/mus.23808     Document Type: Article

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