Outcome of Early Juvenile Onset Metachromatic Leukodystrophy after Unrelated Cord Blood Transplantation

Journal of Child Neurology

Volumn 31, Issue 3, 2016, Pages 338-344

  Chen, Xuqin ^a   Gill, Deepak ^b   Shaw, Peter ^b   Ouvrier, Robert ^b   Troedson, Christopher ^b  

^a CHILDREN S HOSPITAL OF SOOCHOW UNIVERSITY   (China)

^b CHILDREN S HOSPITAL AT WESTMEAD   (Australia)

Author keywords

juvenile; metachromatic leukodystrophy; onset; outcome; umbilical cord blood transplantation

Indexed keywords

BUSULFAN; CYCLOPHOSPHAMIDE; CYCLOSPORIN; FLUDARABINE; METHYLPREDNISOLONE; THYMOCYTE ANTIBODY;

CASE REPORT; CHILD; CLINICAL EXAMINATION; CONTROLLED STUDY; CORD BLOOD STEM CELL TRANSPLANTATION; DYSPHAGIA; EPILEPSY; FAMILY HISTORY; FEMALE; FOLLOW UP; GRAFT VERSUS HOST REACTION; HUMAN; HYPERSALIVATION; INCONTINENCE; INTELLECTUAL IMPAIRMENT; MALE; MENTAL DEFICIENCY; METACHROMATIC LEUKODYSTROPHY; NEUROIMAGING; OUTCOME ASSESSMENT; PRIORITY JOURNAL; PROPHYLAXIS; QUADRIPLEGIA; REVIEW; SENSORIMOTOR NEUROPATHY; UNRELATED UMBILICAL CORD BLOOD TRANSPLANTATION; WECHSLER PRESCHOOL AND PRIMARY SCALE OF INTELLIGENCE; ALLOTRANSPLANTATION; GENETICS; LEUKODYSTROPHY, METACHROMATIC; PATHOLOGY; PATHOPHYSIOLOGY; PRESCHOOL CHILD; PROCEDURES; SIBLING; TREATMENT OUTCOME;

CHILD, PRESCHOOL; CORD BLOOD STEM CELL TRANSPLANTATION; FEMALE; FOLLOW-UP STUDIES; HUMANS; LEUKODYSTROPHY, METACHROMATIC; MALE; SIBLINGS; TRANSPLANTATION, HOMOLOGOUS; TREATMENT OUTCOME;

EID: 84957866529     PISSN: 08830738     EISSN: 17088283     Source Type: Journal    
DOI: 10.1177/0883073815595078     Document Type: Review

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