SCOPUS 정보 검색 플랫폼

Molecular Therapy

Volumn 23, Issue 12, 2015, Pages 1800-1801

Selecting the Best AAV Capsid for Human Studies

(1) Kay, Mark A a

a STANFORD UNIVERSITY SCHOOL OF MEDICINE (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; BLOOD CLOTTING FACTOR 9; CAPSID PROTEIN;

ADENO ASSOCIATED VIRUS; AMINO ACID SEQUENCE; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; GENETIC TRANSDUCTION; HEMOPHILIA B; HUMAN; LETTER; LIVER CELL; NONHUMAN; SEROTYPE; T LYMPHOCYTE; TRANSGENE; XENOTRANSPLANTATION; DEPENDOPARVOVIRUS; GENE VECTOR; GENETICS; VIRUS CAPSID;

CAPSID; CAPSID PROTEINS; DEPENDOVIRUS; GENETIC VECTORS; HUMANS;

EID: 84951289951 PISSN: 15250016 EISSN: 15250024 Source Type: Journal
DOI: 10.1038/mt.2015.206 Document Type: Letter

Times cited : (11)

References (7)

1
- 33644820684
- Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed on host immune response
- Manno, CS, Pierce, GF, Arruda, VR, Glader B, Ragni, M, Rasko, JJ et al. (2006). Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed on host immune response. Nat Medicine 12 (3): 342-347.
- (2006) Nat Medicine , vol.12 , Issue.3 , pp. 342-347
- Manno, C.S.¹ Pierce, G.F.² Arruda, V.R.³ Glader, B.⁴ Ragni, M.⁵ Rasko, J.J.⁶

2
- 84911383748
- Longterm safety and efficacy of factor IX gene therapy in hemophilia B
- Nathwani, AC, Reiss, UM, Tuddenham, EG, Rosales, C, Chowdary, P, McIntosh, J et al. (2014). Longterm safety and efficacy of factor IX gene therapy in hemophilia B. N Engl J Med 371: 1994-2004.
- (2014) N Engl J Med , vol.371 , pp. 1994-2004
- Nathwani, A.C.¹ Reiss, U.M.² Tuddenham, E.G.³ Rosales, C.⁴ Chowdary, P.⁵ McIntosh, J.⁶

3
- 84855161388
- Adenovirus-associated virus vector-mediated gene transfer in hemophilia B
- Nathwani, AC, Tuddenham, EG, Rangarajan, S, Rosales, C, McIntosh, J, Linch, DC et al. (2011). Adenovirus-associated virus vector-mediated gene transfer in hemophilia B. N Engl J Med 365: 2357-2365.
- (2011) N Engl J Med , vol.365 , pp. 2357-2365
- Nathwani, A.C.¹ Tuddenham, E.G.² Rangarajan, S.³ Rosales, C.⁴ McIntosh, J.⁵ Linch, D.C.⁶

4
- 84894242894
- Selection and evaluation of clinically relevant AAV variants in a xenograft liver model
- Lisowski, L, Dane, AP, Chu, K, Zhang, Y, Cunninghamm, SC, Wilson, EM et al. (2014). Selection and evaluation of clinically relevant AAV variants in a xenograft liver model. Nature 506: 382-386.
- (2014) Nature , vol.506 , pp. 382-386
- Lisowski, L.¹ Dane, A.P.² Chu, K.³ Zhang, Y.⁴ Cunninghamm, S.C.⁵ Wilson, E.M.⁶

5
- 84952636705
- Comparative study of liver gene transfer with AAV vectors based on natural and engineered AAV capsids
- Wang, L, Bell, P, Somanathan, S, Wang, Q, He, Z, Yu, H et al. (2015). Comparative study of liver gene transfer with AAV vectors based on natural and engineered AAV capsids. Mol Ther 23: 1877-1887.
- (2015) Mol Ther , vol.23 , pp. 1877-1887
- Wang, L.¹ Bell, P.² Somanathan, S.³ Wang, Q.⁴ He, Z.⁵ Yu, H.⁶

6
- 84935897836
- Development and rescue of human familial hypercholesterolaemia in a xenograft mouse model
- Bissig-Choisat, B, Wang, L, Legras, X, Saha, PK, Chen, L, Bell, P et al. (2015). Development and rescue of human familial hypercholesterolaemia in a xenograft mouse model. Nat Commun 6: 7339.
- (2015) Nat Commun , vol.6 , pp. 7339
- Bissig-Choisat, B.¹ Wang, L.² Legras, X.³ Saha, P.K.⁴ Chen, L.⁵ Bell, P.⁶

7
- 84952638250
- Efficient and targeted transduction of nonhuman primate liver with systemically delivered optimized AAV3B vectors
- Li, S, Ling, C, Zhong, L, Li, M, Su, Q, He, R et al. (2015). Efficient and targeted transduction of nonhuman primate liver with systemically delivered optimized AAV3B vectors. Mol Ther 23: 1867-1876
- (2015) Mol Ther , vol.23 , pp. 1867-1876
- Li, S.¹ Ling, C.² Zhong, L.³ Li, M.⁴ Su, Q.⁵ He, R.⁶

* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.