-
1
-
-
84860310432
-
Retinal dystrophies and gene therapy
-
Sundaram V, Moore AT, Ali RR, Bainbridge JW. Retinal dystrophies and gene therapy. Eur J Pediatr 2012; 171(5): 757-765.
-
(2012)
Eur J Pediatr
, vol.171
, Issue.5
, pp. 757-765
-
-
Sundaram, V.1
Moore, A.T.2
Ali, R.R.3
Bainbridge, J.W.4
-
2
-
-
84941231941
-
-
RP Fighting Blindness
-
RP Fighting Blindness. Other Inherited Retinal Conditions. http://www.rpfightingblindness.org.uk/index.php?tln= aboutrp&pageid=66.
-
Other Inherited Retinal Conditions.
-
-
-
4
-
-
84896843397
-
A comparison of the causes of blindness certifications in England and Wales in working age adults (16-64 years 1999-2000 with 2009-2010
-
Liew G, Michaelides M, Bunce C. A comparison of the causes of blindness certifications in England and Wales in working age adults (16-64 years), 1999-2000 with 2009-2010. BMJ Open 2014; 4: e004015.
-
(2014)
BMJ Open
, vol.4
, pp. e004015
-
-
Liew, G.1
Michaelides, M.2
Bunce, C.3
-
5
-
-
0242380316
-
Severe visual impairment and blindness in children in the UK
-
British Childhood Visual Impairment Study Group.
-
Rahi JS, Cable N. British Childhood Visual Impairment Study Group. Severe visual impairment and blindness in children in the UK. Lancet 2003; 362: 1359-1365.
-
(2003)
Lancet
, vol.362
, pp. 1359-1365
-
-
Rahi, J.S.1
Cable, N.2
-
6
-
-
84941231942
-
Patient: Trusted medical information and support
-
Available at
-
Patient: trusted medical information and support. Hereditary retinal dystrophies. Available at http://www. patient.co.uk/doctor/Hereditary-Retinal-Dystrophies.htm.
-
Hereditary Retinal Dystrophies.
-
-
-
7
-
-
84904630562
-
The sight loss and vision priority setting partnership (slv-psp): Overview and results of the research prioritisation survey process
-
Rowe F, Wormald R, Cable R, Acton M, Bonstein K, Bowen M, et al. The Sight Loss and Vision Priority Setting Partnership (SLV-PSP): overview and results of the research prioritisation survey process. BMJ Open 2014; 4(7): e004905.
-
(2014)
BMJ Open
, vol.4
, Issue.7
, pp. e004905
-
-
Rowe, F.1
Wormald, R.2
Cable, R.3
Acton, M.4
Bonstein, K.5
Bowen, M.6
-
8
-
-
84964776775
-
-
EuroScan International Network. EuroScan International Network. Birmingham: Euroscan International Network. Available at
-
EuroScan International Network. EuroScan International Network. A toolkit for the identification and assessment of new and emerging technologies, 2014. Birmingham: Euroscan International Network. Available at http:// euroscan.org.uk/methods.
-
A Toolkit for the Identification and Assessment of New and Emerging Technologies, 2014
-
-
-
9
-
-
85007302654
-
AAV2 gene therapy readministration in three adults with congenital blindness
-
120ra15
-
Bennett J, Ashtari M, Wellman J, Marshall KA, Cyckowski LL, Chung DC, et al. AAV2 gene therapy readministration in three adults with congenital blindness. Sci Transl Med 2012; 4(120): 120ra15.
-
(2012)
Sci Transl Med
, vol.4
, pp. 120
-
-
Bennett, J.1
Ashtari, M.2
Wellman, J.3
Marshall, K.A.4
Cyckowski, L.L.5
Chung, D.C.6
-
10
-
-
84855611189
-
Gene therapy for leber congenital amaurosis caused by RPE65 mutations: Safety and efficacy in 15 children and adults followed up to 3 years
-
Jacobson SG, Cideciyan AV, Ratnakaram R, Heon E, Schwartz SB, Roman AJ, et al. Gene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years. Arch Ophthalmol 2012; 130(1): 9-24.
-
(2012)
Arch Ophthalmol
, vol.130
, Issue.1
, pp. 9-24
-
-
Jacobson, S.G.1
Cideciyan, A.V.2
Ratnakaram, R.3
Heon, E.4
Schwartz, S.B.5
Roman, A.J.6
-
11
-
-
44249120315
-
Effect of gene therapy on visual function in Leber's congenital amaurosis
-
Bainbridge JW, Smith AJ, Barker SS, Robbie S, Henderson R, Balaggan K, et al. Effect of gene therapy on visual function in Leber's congenital amaurosis. N Engl J Med 2008; 358(21): 2231-2239.
-
(2008)
N Engl J Med
, vol.358
, Issue.21
, pp. 2231-2239
-
-
Bainbridge, J.W.1
Smith, A.J.2
Barker, S.S.3
Robbie, S.4
Henderson, R.5
Balaggan, K.6
-
12
-
-
84875138677
-
Gene therapy for retinal disease
-
McClements M, Maclaren RE. Gene therapy for retinal disease. Transl Res 2013; 161(4): 241-254.
-
(2013)
Transl Res
, vol.161
, Issue.4
, pp. 241-254
-
-
McClements, M.1
MacLaren, R.E.2
-
14
-
-
84887357405
-
Using human induced pluripotent stem cells to treat retinal disease
-
Borooah S, Phillips MJ, Bilican B, Wright AF, Wilmut I, Chandran S, et al. Using human induced pluripotent stem cells to treat retinal disease. Prog Retin Eye Res 2013; 37: 163-181.
-
(2013)
Prog Retin Eye Res
, vol.37
, pp. 163-181
-
-
Borooah, S.1
Phillips, M.J.2
Bilican, B.3
Wright, A.F.4
Wilmut, I.5
Chandran, S.6
-
15
-
-
79955024448
-
Stem cell-based therapeutic applications in retinal degenerative diseases
-
Huang Y, Enzmann V, Ildstad ST. Stem cell-based therapeutic applications in retinal degenerative diseases. Stem Cell Rev 2011; 7(2): 434-445.
-
(2011)
Stem Cell Rev
, vol.7
, Issue.2
, pp. 434-445
-
-
Huang, Y.1
Enzmann, V.2
Ildstad, S.T.3
-
16
-
-
84923096065
-
Personalized therapeutic strategies for patients with retinitis pigmentosa
-
Zheng A, Li Y, Tsang SH. Personalized therapeutic strategies for patients with retinitis pigmentosa. Expert Opin Biol Ther 2015; 15: 391-402.
-
(2015)
Expert Opin Biol Ther
, vol.15
, pp. 391-402
-
-
Zheng, A.1
Li, Y.2
Tsang, S.H.3
-
18
-
-
84941231945
-
-
Available at Accessed January
-
Neurotech. NT-501 CNTF Renexus. Available at http://www.neurotechusa.com/cntfrenexus.html. Accessed January 2015.
-
(2015)
Neurotech. NT-501 CNTF Renexus.
-
-
-
19
-
-
84908101924
-
CNGB3-Achromatopsia clinical trial with CNTF: Diminished rod pathway responses with no evidence of improvement in cone function
-
Zein WM, Jeffrey BG, Wiley HE, Turriff AE, Tumminia SJ, Tao W, et al. CNGB3-Achromatopsia clinical trial with CNTF: diminished rod pathway responses with no evidence of improvement in cone function. Invest Ophthalmol Vis Sci 2014; 55(10): 6301-6308.
-
(2014)
Invest Ophthalmol Vis Sci
, vol.55
, Issue.10
, pp. 6301-6308
-
-
Zein, W.M.1
Jeffrey, B.G.2
Wiley, H.E.3
Turriff, A.E.4
Tumminia, S.J.5
Tao, W.6
-
20
-
-
84880571547
-
Randomized trial of ciliary neurotrophic factor delivered by encapsulated cell intraocular implants for retinitis pigmentosa
-
e1 Ciliary Neurotrophic Factor Retinitis Pigmentosa Study Group.
-
Birch DG, Weleber RG, Duncan JL, Jaffe GJ, Tao W. Ciliary Neurotrophic Factor Retinitis Pigmentosa Study Group. Randomized trial of ciliary neurotrophic factor delivered by encapsulated cell intraocular implants for retinitis pigmentosa. Am J Ophthalmol 2013; 156(2): 283-292.e1.
-
(2013)
Am J Ophthalmol
, vol.156
, Issue.2
, pp. 283-292
-
-
Birch, D.G.1
Weleber, R.G.2
Duncan, J.L.3
Jaffe, G.J.4
Tao, W.5
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