메뉴 건너뛰기




Volumn 891, Issue , 2012, Pages 1-7

The concept of prenatal gene therapy

Author keywords

Animal models; Ethical considerations; Fetal Medicine; Genetic disease; Prenatal (in utero, fetal) gene therapy; Prenatal disease; Prevention; Vectors

Indexed keywords

VIRUS VECTOR;

EID: 84934434571     PISSN: 10643745     EISSN: None     Source Type: Book Series    
DOI: 10.1007/978-1-61779-873-3_1     Document Type: Article
Times cited : (5)

References (37)
  • 1
    • 0347003513 scopus 로고    scopus 로고
    • The burden of genetic disease on inpatient care in a children's hospital
    • McCandless SE, Brunger JW, Cassidy SB (2004) The burden of genetic disease on inpatient care in a children's hospital. Am J Hum Genet 74:121-127
    • (2004) Am J Hum Genet , vol.74 , pp. 121-127
    • McCandless, S.E.1    Brunger, J.W.2    Cassidy, S.B.3
  • 3
    • 0034532718 scopus 로고    scopus 로고
    • Surgically correctable fetal disease
    • Harrison MR (2000) Surgically correctable fetal disease. Am J Surg 180:335-342
    • (2000) Am J Surg , vol.180 , pp. 335-342
    • Harrison, M.R.1
  • 4
    • 0023029609 scopus 로고
    • Gene transfer and expression in nonhuman primates using retroviral vectors
    • Anderson W, Kantoff P, Eglitis M et al (1986) Gene transfer and expression in nonhuman primates using retroviral vectors. Cold Spring Harb Symp Quant Biol 51(Pt 2):1073-1081
    • (1986) Cold Spring Harb Symp Quant Biol , vol.51 , Issue.PART. 2 , pp. 1073-1081
    • Anderson, W.1    Kantoff, P.2    Eglitis, M.3
  • 5
    • 0023516063 scopus 로고
    • Gene therapy: Efforts at developing large animal models for autologous bone marrow transplant and gene transfer with retroviral vectors
    • Eglitis M, Kantoff PW, McLachlin JR et al (1987) Gene therapy: efforts at developing large animal models for autologous bone marrow transplant and gene transfer with retroviral vectors. Ciba Found Symp 130:229-246
    • (1987) Ciba Found Symp , vol.130 , pp. 229-246
    • Eglitis, M.1    Kantoff, P.W.2    McLachlin, J.R.3
  • 6
    • 0024505011 scopus 로고
    • In utero gene transfer and expression: A sheep transplantation model
    • Kantoff PW, Flake AW, Eglitis MA, Scharf S et al (1989) In utero gene transfer and expression: a sheep transplantation model. Blood 73: 1066-1073
    • (1989) Blood , vol.73 , pp. 1066-1073
    • Kantoff, P.W.1    Flake, A.W.2    Eglitis, M.A.3    Scharf, S.4
  • 7
    • 0026500033 scopus 로고
    • In-utero transplantation of fetal liver stem cells into human fetuses
    • Touraine JL (1992) In-utero transplantation of fetal liver stem cells into human fetuses. Hum Reprod 7:44-48
    • (1992) Hum Reprod , vol.7 , pp. 44-48
    • Touraine, J.L.1
  • 8
    • 0025064567 scopus 로고
    • Hepatic gene transfer in animals using retroviruses containing the promoter from the gene for phosphoenolpyruvate carboxykinase
    • Hatzoglou M, Lamers W, Bosch F et al (1990) Hepatic gene transfer in animals using retroviruses containing the promoter from the gene for phosphoenolpyruvate carboxykinase. J Biol Chem 265:17285-17293
    • (1990) J Biol Chem , vol.265 , pp. 17285-17293
    • Hatzoglou, M.1    Lamers, W.2    Bosch, F.3
  • 9
    • 0029616586 scopus 로고
    • Persistent expression of genes transferred in the fetal rat liver via retroviruses
    • Hatzoglou M, Moorman A, Lamers W (1995) Persistent expression of genes transferred in the fetal rat liver via retroviruses. Somatic Cell Mol Biol 2:265-278
    • (1995) Somatic Cell Mol Biol , vol.2 , pp. 265-278
    • Hatzoglou, M.1    Moorman, A.2    Lamers, W.3
  • 10
    • 0028803618 scopus 로고
    • Intraamniotic administration of an adenovirus vector for gene transfer to fetal sheep and mouse tissue
    • Holzinger A, Trapnell BC, Weaver TE, Whitsett JA, Iwamoto HS (1995) Intraamniotic administration of an adenovirus vector for gene transfer to fetal sheep and mouse tissue. Pediatr Res 38:844-850
    • (1995) Pediatr Res , vol.38 , pp. 844-850
    • Holzinger, A.1    Trapnell, B.C.2    Weaver, T.E.3    Whitsett, J.A.4    Iwamoto, H.S.5
  • 11
    • 0029046114 scopus 로고
    • Adenoviral-mediated gene transfer to fetal pulmonary epithelia in vitro and in vivo
    • McCray PB, Armstrong K, Zabner J, Miller DW et al (1995) Adenoviral-mediated gene transfer to fetal pulmonary epithelia in vitro and in vivo. J Clin Invest 95:2620-2632
    • (1995) J Clin Invest , vol.95 , pp. 2620-2632
    • McCray, P.B.1    Armstrong, K.2    Zabner, J.3    Miller, D.W.4
  • 12
    • 0029115287 scopus 로고
    • Retrovirus-mediated gene transfer in lungs of living fetal sheep
    • Pitt BR, Schwarz MA, Pilewski JM et al (1995) Retrovirus-mediated gene transfer in lungs of living fetal sheep. Gene Ther 2:344-350
    • (1995) Gene Ther , vol.2 , pp. 344-350
    • Pitt, B.R.1    Schwarz, M.A.2    Pilewski, J.M.3
  • 13
    • 0028872747 scopus 로고
    • Gene transfer and expression in progeny after intravenous DNA injection into pregnant mice
    • Tsukamoto M, Ochiya T, Yoshida S et al (1995) Gene transfer and expression in progeny after intravenous DNA injection into pregnant mice. Nat Genet 9:243-248
    • (1995) Nat Genet , vol.9 , pp. 243-248
    • Tsukamoto, M.1    Ochiya, T.2    Yoshida, S.3
  • 14
    • 17744367655 scopus 로고    scopus 로고
    • In utero gene therapy: Current challenges and perspectives
    • Waddington SN, Kramer MG, Hernandez-Alcoceba R et al (2005) In utero gene therapy: current challenges and perspectives. Mol Ther 11:661-676
    • (2005) Mol Ther , vol.11 , pp. 661-676
    • Waddington, S.N.1    Kramer, M.G.2    Hernandez-Alcoceba, R.3
  • 17
    • 52049125232 scopus 로고    scopus 로고
    • Local delivery of VEGF adenovirus to the uterine artery increases vasorelaxation and uterine blood fl ow in the pregnant sheep
    • David AL, Torondel B, Zachary I et al (2008) Local delivery of VEGF adenovirus to the uterine artery increases vasorelaxation and uterine blood fl ow in the pregnant sheep. Gene Ther 15:1344-1350
    • (2008) Gene Ther , vol.15 , pp. 1344-1350
    • David, A.L.1    Torondel, B.2    Zachary, I.3
  • 18
    • 70350573626 scopus 로고    scopus 로고
    • Placental gene transfer: Transgene screening in mice for trophic effects on the placenta
    • Katz AB, Keswani SG, Habli M et al (2009) Placental gene transfer: transgene screening in mice for trophic effects on the placenta. Am J Obstet Gynecol 201(499):e491-e498
    • (2009) Am J Obstet Gynecol , vol.201 , Issue.499
    • Katz, A.B.1    Keswani, S.G.2    Habli, M.3
  • 19
    • 0742269636 scopus 로고    scopus 로고
    • Fetal membranes act as a barrier for adenoviruses: Gene transfer into exocoelomic cavity of rat fetuses does not affect cells in the fetus
    • Laurema A, Vanamo K, Heikkila A et al (2004) Fetal membranes act as a barrier for adenoviruses: gene transfer into exocoelomic cavity of rat fetuses does not affect cells in the fetus. Am J Obstet Gynecol 190:264-267
    • (2004) Am J Obstet Gynecol , vol.190 , pp. 264-267
    • Laurema, A.1    Vanamo, K.2    Heikkila, A.3
  • 20
    • 84941944716 scopus 로고    scopus 로고
    • Comparative in vivo approaches for selective adenovirus-mediated gene delivery to the placenta
    • Xing A, Boileau P, Cauzac M et al (2000) Comparative in vivo approaches for selective adenovirus-mediated gene delivery to the placenta. Hum Gene Ther 11:167-177
    • (2000) Hum Gene Ther , vol.11 , pp. 167-177
    • Xing, A.1    Boileau, P.2    Cauzac, M.3
  • 22
    • 33751068475 scopus 로고    scopus 로고
    • Transient local overexpression of human vascular endothelial growth factor (VEGF) in mouse feto-maternal interface during mid-term pregnancy lowers systemic maternal blood pressure
    • Koyama S, Kimura T, Ogita K et al (2006) Transient local overexpression of human vascular endothelial growth factor (VEGF) in mouse feto-maternal interface during mid-term pregnancy lowers systemic maternal blood pressure. Horm Metab Res 38:619-624
    • (2006) Horm Metab Res , vol.38 , pp. 619-624
    • Koyama, S.1    Kimura, T.2    Ogita, K.3
  • 23
    • 31344439716 scopus 로고    scopus 로고
    • Over-expression of heme oxygenase-1 by adenoviral gene transfer improves pregnancy outcome in a murine model of abortion
    • Zenclussen ML, Anegon I, Bertoja AZ et al (2006) Over-expression of heme oxygenase-1 by adenoviral gene transfer improves pregnancy outcome in a murine model of abortion. J Reprod Immunol 69:35-52
    • (2006) J Reprod Immunol , vol.69 , pp. 35-52
    • Zenclussen, M.L.1    Anegon, I.2    Bertoja, A.Z.3
  • 25
    • 0033121139 scopus 로고    scopus 로고
    • Prenatal gene therapy: Can the technical hurdles be overcome?
    • Senut M, Gage FH (1999) Prenatal gene therapy: can the technical hurdles be overcome? Mol Med Today 5:152-156
    • (1999) Mol Med Today , vol.5 , pp. 152-156
    • Senut, M.1    Gage, F.H.2
  • 27
    • 27944470542 scopus 로고    scopus 로고
    • Gene therapy progress and prospects: Fetal gene therapy-fi rst proofs of concept-some adverse effects
    • Coutelle C, Themis M, Waddington SN et al (2005) Gene therapy progress and prospects: fetal gene therapy-fi rst proofs of concept-some adverse effects. Gene Ther 12:1601-1607
    • (2005) Gene Ther , vol.12 , pp. 1601-1607
    • Coutelle, C.1    Themis, M.2    Waddington, S.N.3
  • 28
    • 29544439253 scopus 로고    scopus 로고
    • Fetal therapy for single gene disorders
    • O'Brien B, Bianchi DW (2005) Fetal therapy for single gene disorders. Clin Obstet Gynecol 48:885-896
    • (2005) Clin Obstet Gynecol , vol.48 , pp. 885-896
    • O'brien, B.1    Bianchi, D.W.2
  • 29
    • 67649093971 scopus 로고    scopus 로고
    • Prenatal stem cell transplantation and gene therapy
    • Santore MT, Roybal JL, Flake AW (2009) Prenatal stem cell transplantation and gene therapy. Clin Perinatol 36:451-471, x. i.
    • (2009) Clin Perinatol , vol.36 , pp. 451-471
    • Santore, M.T.1    Roybal, J.L.2    Flake, A.W.3
  • 30
    • 17744396281 scopus 로고    scopus 로고
    • The current status and future direction of fetal gene therapy
    • David A, Themis M, Waddington S et al (2003) The current status and future direction of fetal gene therapy. Gene Ther Mol Biol 7:181-209
    • (2003) Gene Ther Mol Biol , vol.7 , pp. 181-209
    • David, A.1    Themis, M.2    Waddington, S.3
  • 31
    • 0032821708 scopus 로고    scopus 로고
    • Prospects for in utero human gene therapy
    • Zanjani ED, Anderson WF (1999) Prospects for in utero human gene therapy. Science 285:2084-2088
    • (1999) Science , vol.285 , pp. 2084-2088
    • Zanjani, E.D.1    Anderson, W.F.2
  • 32
    • 0034180256 scopus 로고    scopus 로고
    • Prenatal gene transfer: Scienti fi c medical and ethical issues
    • RAC
    • RAC (2000) Prenatal gene transfer: scienti fi c medical and ethical issues. A report of the Recombinant DNA Advisory Committee. Hum Gene Ther 11:1211-1229
    • (2000) A Report of the Recombinant DNA Advisory Committee. Hum Gene Ther , vol.11 , pp. 1211-1229
  • 33
    • 0032475806 scopus 로고    scopus 로고
    • RAC confronts in utero gene therapy proposal
    • Couzin J (1998) RAC confronts in utero gene therapy proposal. Science 282:27
    • (1998) Science , vol.282 , pp. 27
    • Couzin, J.1
  • 34
    • 0037448352 scopus 로고    scopus 로고
    • A serious adverse event after successful gene therapy for X-linked severe combined immunode fi ciency
    • Hacein-Bey-Abina S, von Kalle C, Schmidt M et al (2003) A serious adverse event after successful gene therapy for X-linked severe combined immunode fi ciency. N Engl J Med 348:255-256
    • (2003) N Engl J Med , vol.348 , pp. 255-256
    • Hacein-Bey-Abina, S.1    Von Kalle, C.2    Schmidt, M.3
  • 35
    • 0142089747 scopus 로고    scopus 로고
    • Fatal systemic in fl ammatory response syndrome in a ornithine transcarbamylase de fi cient patient following adenoviral gene transfer
    • Raper SE, Chirmule N, Lee FS et al (2003) Fatal systemic in fl ammatory response syndrome in a ornithine transcarbamylase de fi cient patient following adenoviral gene transfer. Mol Genet Metab 80:148-158
    • (2003) Mol Genet Metab , vol.80 , pp. 148-158
    • Raper, S.E.1    Chirmule, N.2    Lee, F.S.3
  • 36
    • 0037134031 scopus 로고    scopus 로고
    • Murine leukemia induced by retroviral gene marking
    • Li Z, Dullmann J, Schiedlmeier B et al (2002) Murine leukemia induced by retroviral gene marking. Science 296:497
    • (2002) Science , vol.296 , pp. 497
    • Li, Z.1    Dullmann, J.2    Schiedlmeier, B.3
  • 37
    • 23844507993 scopus 로고    scopus 로고
    • Oncogenesis following delivery of a non-primate lentiviral gene therapy vector to fetal mice
    • Themis M, Waddington SN, Schmidt M et al (2005) Oncogenesis following delivery of a non-primate lentiviral gene therapy vector to fetal mice. Mol Ther 12:763-771
    • (2005) Mol Ther , vol.12 , pp. 763-771
    • Themis, M.1    Waddington, S.N.2    Schmidt, M.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.