Use of polylactide-co-glycolide-nanoparticles for lysosomal delivery of a therapeutic enzyme in glycogenosis type II fibroblasts

Journal of Nanoscience and Nanotechnology

Volumn 15, Issue 4, 2015, Pages 2657-2666

  Tancini, Brunella ^a   Tosi, Giovanni ^b   Bortot, Barbara ^c   Dolcetta, Diego ^d   Magini, Alessandro ^a   De Martino, Eleonora ^c   Urbanelli, Lorena ^a   Ruozi, Barbara ^b   Forni, Flavio ^b   Emiliani, Carla ^a   Vandelli, Maria A ^b   Severini, Giovanni Maria ^c  

^a UNIVERSITY OF PERUGIA   (Italy)

^b UNIVERSITY OF MODENA AND REGGIO EMILIA   (Italy)

^c INSTITUTE FOR MATERNAL AND CHILD HEALTH IRCCS BURLO GAROFOLO   (Italy)

^d BIRD Foundation   (Italy)

Author keywords

Acid alpha glucosidase; Drug delivery.; Myozyme ; Nanoparticles; PLGA; Pompe disease

Indexed keywords

CELL CULTURE; COPOLYMERS; DIGITAL STORAGE; DRUG DELIVERY; EMULSIFICATION; FIBROBLASTS; GALLIUM ALLOYS; NANOPARTICLES; PARTICLE SIZE; PATIENT TREATMENT;

ALPHA GLUCOSIDASE; BIOCHEMICAL ACTIVITY; DOUBLE EMULSION-SOLVENT EVAPORATION; ENZYME REPLACEMENT THERAPY; MYOZYME; PLGA; POLY LACTIDE-CO-GLYCOLIDE; POMPE DISEASE;

ENZYMES;

ALPHA GLUCOSIDASE; GAA PROTEIN, HUMAN; LACTIC ACID; NANOPARTICLE; POLYGLYCOLIC ACID; POLYLACTIC ACID-POLYGLYCOLIC ACID COPOLYMER; RNA; RNA, RECOMBINANT;

CELL CULTURE; CHEMISTRY; DRUG DELIVERY SYSTEM; FIBROBLAST; GLYCOGEN STORAGE DISEASE TYPE 2; HUMAN; LYSOSOME; METABOLISM;

ALPHA-GLUCOSIDASES; CELLS, CULTURED; DRUG DELIVERY SYSTEMS; FIBROBLASTS; GLYCOGEN STORAGE DISEASE TYPE II; HUMANS; LACTIC ACID; LYSOSOMES; NANOPARTICLES; POLYGLYCOLIC ACID; RNA;

EID: 84920746970     PISSN: 15334880     EISSN: 15334899     Source Type: Journal    
DOI: 10.1166/jnn.2015.9251     Document Type: Article

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